109047 ⎘
Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof General methods applicable to biologically active non-coding nucleic acids
GENE CORRECTION FOR X-CGD IN HEMATOPOIETIC STEM AND PROGENITOR CELLS
#902CD70+ SOLID TUMOR THERAPY USING GENETICALLY ENGINEERED T CELLS TARGETING CD70
#903DONOR T-CELLS WITH KILL SWITCH
#904STERILE ORGANISMS, METHODS OF MAKING, AND METHODS OF USE THEREOF
#905A HIGH-THROUGHPUT SCREENING METHOD TO DISCOVER OPTIMAL GRNA PAIRS FOR CRISPR-MEDIATED EXON DELETION
#906INSECTICIDAL PROTEINS FROM PLANTS AND METHODS FOR THEIR USE
#907Defining source of bits in trigger frame for disregard bits and releasing redundant beamformed bit
#908BOOSTING HOMOLOGY DIRECTED REPAIR IN PLANTS
#909SHORT INTERFERING NUCLEIC ACID (siNA) COMPOSITIONS
#910OLIGONUCLEOTIDES
#911NUCLEOBASE EDITORS COMPRISING NUCLEIC ACID PROGRAMMABLE DNA BINDING PROTEINS
#912BASE EDITING ENZYMES
#913Compounds and compositions including phosphorothioated oligodeoxynucleotide, and methods of use thereof
#914TRANS-SPLICING SYSTEM FOR TISSUE-SPECIFIC REPLACEMENT OF RNA SEQUENCES
#915METHODS FOR USING GUIDE RNAS WITH CHEMICAL MODIFICATIONS
#916METHODS AND COMPOSITIONS FOR PRIME EDITING NUCLEOTIDE SEQUENCES
#917METHODS AND COMPOSITIONS FOR PRIME EDITING NUCLEOTIDE SEQUENCES
#918Methods and compositions for prime editing nucleotide sequences
#919NOVEL RNA-GUIDED DNA NUCLEASES AND USES THEREOF
#920ELECTROPORATION, DEVELOPMENTALLY-ACTIVATED CELLS, PLURIPOTENT-LIKE CELLS, CELL REPROGRAMMING AND REGENERATIVE MEDICINE
#921TEMPLATE GUIDE RNA MOLECULES
#922DISCONTINUOUS OLIGONUCLEOTIDE LIGANDS
#923CRISPR-CAS EFFECTOR POLYPEPTIDES AND METHODS OF USE THEREOF
#924CAS9 PROTEINS WITH ENHANCED SPECIFICITY AND USES THEREOF
#925VESICLES COMPRISING A PTEN INHIBITOR AND USES OF SAME
#926Targeting ligands for tau pathology
#927TRANSGENE EXPRESSION SYSTEM
#928Polynucleotides containing a morpholino linker
#929GENETIC TOOLS FOR RECOMBINING TRANSGENES AT THE SAME LOCUS
#930CRISPR-CAS EFFECTOR POLYPEPTIDES AND METHODS OF USE THEREOF
#931COMPOSITIONS FOR USE IN TREATING AUTOSOMAL DOMINANT BEST1-RELATED RETINOPATHIES
#932RNA AND DNA BASE EDITING VIA ENGINEERED ADAR
#933Oligonucleotides comprising modified nucleosides
#934MODULAR PLATFORM FOR TARGETED THERAPEUTICS
#935ARC-BASED CAPSIDS AND USES THEREOF
#936COMPOSITIONS AND METHODS FOR THE DELIVERY OF NUCLEIC ACIDS
#937COMPOSITIONS FOR GENOME EDITING AND METHODS OF USE THEREOF
#938Methods of Modulating Expression of Target Nucleic Acid Sequences in A Cell
#939COMPOSITIONS AND METHODS OF IMPROVING SPECIFICITY IN GENOMIC ENGINEERING USING RNA-GUIDED ENDONUCLEASES
#940LOADING OF EXTRACELLULAR VESICLES THROUGH IMPARTING OF MECHANICAL SHEAR
#941Oligonucleotides for inducing paternal UBE3A expression
#942METHODS AND COMPOSITIONS FOR INTEGRATION OF A DNA CONSTRUCT
#943GENE THERAPEUTICS FOR FIBRODYSPLASIA OSSIFICANS PROGRESSIVA
#944PREPARATION METHOD FOR MUTANT CELLS WITH DELETION OF TARGET GENES
#945METHODS AND COMPOSITIONS OF BIOLOGICALLY ACTIVE AGENTS
#946Tuning cascade assay kinetics via molecular design
#947MAGNETIC INORGANIC IRON-BASED NANOPARTICLES
#948KRAB FUSION REPRESSORS AND METHODS AND COMPOSITIONS FOR REPRESSING GENE EXPRESSION
#949CRISPR-Cas effector polypeptides and methods of use thereof
#950MUSCLE-TARGETING COMPLEXES AND USES THEREOF
#951Treatment delivery system and method
#952Oligomeric Compounds Comprising Bicyclic Nucleotides and Uses Thereof
#953Single-stranded RNA-editing oligonucleotides
#954Systems, methods, and compositions for site-specific genetic engineering using programmable addition via site-specific targeting elements (paste)
#955ORTHOGONALLY LINKED MULTIMERIC OLIGONUCLEOTIDES
#956Genetically-modified immune cells comprising a microRNA-adapted shRNA (shRNAmiR)
#957DISCOVERY AND ENGINEERING OF INTEGRASES FOR HIGH-EFFICIENCY GENE INTEGRATION
#958COMPOSITIONS OF DNA MOLECULES, METHODS OF MAKING THEREFOR, AND METHODS OF USE THEREOF
#959MODIFICATION OF BLOOD TYPE ANTIGENS
#960USE OF CIRCUTRN IN PREPARATION OF DRUG FOR TREATING HEART FAILURE, RECOMBINANT VECTOR, AND DRUG FOR TREATING HEART FAILURE
#961CIRCULAR miRNA SPONGES
#962IMPROVED RNA EDITING METHOD
#963Compositions and methods for targeting, editing, or modifying genes
#964CANNABIS WITH ALTERED CANNABINOID CONTENT
#965REMOVABLE PLANT TRANSGENIC LOCI WITH COGNATE GUIDE RNA RECOGNITION SITES
#966Aptamers That Bind Thiamine Analogs and Derivatives
#967Type II CRISPR/Cas9 genome editing system and the application thereof
#968CRISPR EDITING TO EMBED NUCLEIC ACID LANDING PADS INTO GENOMES OF LIVE CELLS
#969Genetically engineered T cells with Regnase-1 and/or TGFBRII disruption have improved functionality and persistence
#970PATHOGEN RESISTANCE IN PLANTS
#971Compositions and methods for TTR gene editing and treating ATTR amyloidosis
#972Compositions and methods for inhibiting expression of transthyretin
#973Lipid formulations for delivery of therapeutic agents
#974NOVEL TYPE I-C CRISPR-CAS SYSTEM FROM CLOSTRIDIA
#975HIV PRE-IMMUNIZATION AND IMMUNOTHERAPY
#976Compositions and methods for targeting, editing, or modifying genes
#977NUCLEIC ACID-CONTAINING LIPID PARTICLES AND RELATED METHODS
#978ARGONAUTE PROTEIN FROM EUKARYOTES AND APPLICATION THEREOF
#979METHODS AND COMPOSITIONS FOR RNA-DIRECTED TARGET DNA MODIFICATION AND FOR RNA-DIRECTED MODULATION OF TRANSCRIPTION
#980CLASS II, TYPE V CRISPR SYSTEMS
#981CLINICALLY APPLICABLE CHARACTERIZATION OF GENETIC VARIANTS BY GENOME EDITING
#982COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS TO CELLS
#983Extracellular Vesicles Engineered to Be Loaded with Distinct RNA Cargo for Improved Therapeutic Efficacy
#984PRECISE INTRODUCTION OF DNA OR MUTATIONS INTO THE GENOME OF WHEAT
#985METHODS AND MODIFICATIONS THAT PRODUCE ssRNAi COMPOUNDS WITH ENHANCED ACTIVITY, POTENCY AND DURATION OF EFFECT
#986REGULATION OF GENE EXPRESSION VIA APTAMER-MEDIATED CONTROL OF SELF-CLEAVING RIBOZYMES
#987DNA-ENCODED FUNCTIONALIZED APTAMERS
#988Methods and compositions for simultaneous editing of both strands of a target double-stranded nucleotide sequence
#989METHODS AND COMPOSITIONS FOR RNA-DIRECTED TARGET DNA MODIFICATION AND FOR RNA DIRECTED MODULATION OF TRANSCRIPTION
#990DIFFERENTIAL KNOCKOUT OF A HETEROZYGOUS ALLELE OF SAMD9L
#991CRISPR DNA targeting enzymes and systems
#992Mutations in Cas9 discovered by broad scanning mutagenesis demonstrate enhancement of DNA cleavage activity
#993IMMUNOMODULATORY POLYNUCLEOTIDES AND USES THEREOF
#994EFFECTOR PROTEINS AND METHODS OF USE
#995LIPID NANOPARTICLE FORMULATIONS FOR CRISPR/CAS COMPONENTS
#996MULTI-CONJUGATES COMPRISING MULTIPLE LIGANDS
#997SYNTHESIS OF 3'N NUCLEOSIDES THROUGH OXIME INTERMEDIATES AND RELATED COMPOUNDS
#998PRECISE DELETION OF CHROMOSOMAL SEQUENCES IN VIVO AND TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS USING ENGINEERED NUCLEASES
#999CRISPR HYBRID DNA/RNA POLYNUCLEOTIDES AND METHODS OF USE
#1000Tuning cascade assay kinetics via molecular design
#1001TAT-INDUCED CRISPR/ENDONUCLEASE-BASED GENE EDITING
#1002IMPROVED HIGH-THROUGHPUT COMBINATORIAL GENETIC MODIFICATION SYSTEM AND OPTIMIZED CAS9 ENZYME VARIANTS
#1003COMPOSITIONS COMPRISING A CAS12I2 POLYPEPTIDE AND USES THEREOF
#1004RECOMBINANT POLYPEPTIDES FOR MEMBRANE FUSION AND USES THEREOF
#1005Modified double-stranded RNA agents
#1006ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES
#1007Reducing intron retention
#1008Particle delivery systems
#1009EXOSOME DELIVERY OF CANCER THERAPEUTICS
#1010Compositions and Methods for Genome Editing
#1011MODIFIED GUIDE RNAS FOR NEISSERIA MENINGITIDIS CAS9
#1012METHODS FOR MODIFICATION OF TARGET NUCLEIC ACIDS
#1013CURE ALL FOR NUCLEIC ACID-GUIDED CELL EDITING IN E. COLI
#1014METHODS AND COMPOSITIONS FOR RNA-GUIDED TREATMENT OF HIV INFECTION
#1015Compositions and methods for promoting gene editing of CXCR4 gene
#1016A PLANT FERTILITY-ASSOCIATED PROTEIN AND ITS APPLICATION THEREOF
#1017METHODS AND COMPOSITIONS FOR INCREASING RESISTANCE TO EAR ROT AND STEM ROT DISEASE IN MAIZE
#1018Integrated silicon platform for electronic biosensors
#1019ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY
#1020DESIGN OF TWO-PART GUIDE RNAS FOR CRISPRa APPLICATIONS
#1021COMPOSITIONS AND METHODS FOR THE TARGETING OF PCSK9
#1022MODIFIED CRISPR RNA AND MODIFIED SINGLE CRISPR RNA AND USES THEREOF
#1023METHODS AND COMPOSITIONS FOR APTAMER-DRIVEN SURFACE FORMULATION OF SELF-FORMING POLYNUCLEOTIDE NANOPARTICLES
#1024COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION
#1025PEPTIDE NUCLEIC ACID CONJUGATES
#1026NUCLEIC ACID COMPLEX AND PHARMACEUTICAL COMPOSITION CONTAINING SAME
#1027ANTISENSE NUCLEIC ACIDS
#1028DESIGN METHOD FOR OPTIMIZED RIG-I LIGANDS
#1029Nucleic Acid Carriers And Therapeutic Methods Of Use
#1030Systems, methods, and compositions for site-specific genetic engineering using programmable addition via site-specific targeting elements (paste)
#1031ANTISENSE OLIGONUCLEOTIDES FOR USE IN THE TREATMENT OF USHER SYNDROME
#1032GLYPICAN-3-SPECIFIC MODIFIED APTAMER AND USE THEREOF
#1033RNAi Agents for Inhibiting Expression of Xanthine Dehydrogenase (XDH), Pharmaceutical Compositions Thereof, and Methods of Use
#1034Oligomeric Compounds Comprising Bicyclic Nucleotides and Uses Thereof
#1035Compositions and methods for TTR gene editing and treating ATTR amyloidosis
#1036Compositions and methods for improved gene editing
#1037Selective Antisense Compounds and Uses Thereof
#1038NUCLEASE-MEDIATED MODULATION OF GENE EXPRESSION
#1039MODULATING STRESS RESPONSES BY A NOVEL CHROMATIN-ASSOCIATED GUIDE RNA DERIVED FROM TRANSFER RNA
#1040MODIFIED DOUBLE-STRANDED RNA AGENTS
#1041Nucleic acid and other compositions and methods for the modulation of cell membranes
#1042EDIBLE PLANT-DERIVED MICROVESICLE COMPOSITIONS FOR DELIVERY OF miRNA AND METHODS FOR TREATMENT OF CANCER
#1043METHODS FOR MODIFICATION OF TARGET NUCLEIC ACIDS
#1044CONDITIONAL-siRNAS AND USES THEREOF IN TREATING CARDIAC HYPERTROPHY
#1045Inhibition of unintended mutations in gene editing
#1046Compositions and methods for delivery of nucleic acids to cells
#1047CHEMICALLY MODIFIED OLIGONUCLEOTIDES WITH IMPROVED SYSTEMIC DELIVERY
#1048SYSTEMS AND METHODS FOR EVALUATING CAS9-INDEPENDENT OFF-TARGET EDITING OF NUCLEIC ACIDS
#1049Compositions and methods for delivery of nucleic acids to cells
#1050ENHANCED PLACENTAL STEM CELLS AND USES THEREOF
#1051COMPOSITIONS COMPRISING BACTERIALLY DERIVED MINICELLS AND METHODS OF USING THE SAME
#1052EXPORTED RNA REPORTERS FOR LIVE-CELL MEASUREMENT
#1053THREE-COMPONENT CRISPR/CAS COMPLEX SYSTEM AND USES THEREOF
#1054REPROGRAMMING THE METABOLOME TO DELAY ONSET OR TREAT NEURODEGENERATION
#1055Multi-conjugate of siRNA and preparing method thereof
#1056PRECISE TEMPLATE-FREE CORRECTION OF BRCA1 MUTATION IN HUMAN CELLS VIA GENOME EDITING
#1057Effector proteins and methods of use
#1058TRANSPOSON SYSTEMS FOR GENOME EDITING
#1059METHODS TO CHARACTERIZE ENZYMES FOR GENOME ENGINEERING
#1060TARGETED AND LOCALIZED IN VIVO DELIVERY OF OLIGONUCLEOTIDES
#1061ANTISENSE MOLECULES AND METHODS FOR TREATING PATHOLOGIES
#1062Methods for ameliorating infusion reactions
#1063DOUBLE-STRANDED NUCLEIC ACID MOLECULES AND METHOD FOR REMOVING GLASS ADAPTOR IN DNA LIBRARY BY MEANS OF SAME
#1064CRISPR DNA targeting enzymes and systems
#1065NOVEL PRECURSOR MIRNA AND APPLICATION THEREOF IN TUMOR TREATMENT
#1066Engineered class 2 type V CRISPR systems
#1067TREATMENT OF LIVER INJURY
#1068IMPROVED METHODS FOR MODIFICATION OF TARGET NUCLEIC ACIDS
#1069Polynucleotide compositions and methods for gene expression regulations
#1070COMPOSITIONS AND METHODS OF IMPROVING SPECIFICITY IN GENOMIC ENGINEERING USING RNA-GUIDED ENDONUCLEASES
#1071NUCLEIC ACID COMPLEXES FOR SCREENING BARCODED COMPOUNDS
#1072ALKYLATED NUCLEOSIDES, AND COMPOSITIONS AND METHODS THEREOF FOR NUCLEIC ACID DELIVERY
#1073Compositions and methods for delivery of nucleic acids to cells
#1074METHOD FOR DETECTING TARGET NUCLEIC ACID, METHOD FOR DETECTING NUCLEIC ACID-BINDING MOLECULE, AND METHOD FOR EVALUATING NUCLEIC ACID-BINDING ABILITY
#1075Compositions and methods for organ specific delivery of nucleic acids
#1076Recombinant Adeno-Associated Virus Delivery of Exon 2-Targeted U7SNRNA Polynucleotide Constructs
#1077METHODS FOR MODIFICATION OF TARGET NUCLEIC ACIDS
#1078CAS9 VARIANTS HAVING NON-CANONICAL PAM SPECIFICITIES AND USES THEREOF
#1079Engineered CRISPR-Cas9 nucleases with Altered PAM Specificity
#1080COMPOSITIONS AND METHODS FOR NON-TOXIC CONDITIONING
#1081RNAi agents for inhibiting expression of xanthine dehydrogenase (XDH), pharmaceutical compositions thereof, and methods of use
#1082POLY(Beta-AMINO ESTER) NANOPARTICLES FOR THE NON-VIRAL DELIVERY OF PLASMID DNA FOR GENE EDITING AND RETINAL GENE THERAPY
#1083OLIGONUCLEOTIDES COMPRISING A PHOSPHORODITHIOATE INTERNUCLEOSIDE LINKAGE
#1084CRISPR/CAS-RELATED METHODS, COMPOSITIONS AND COMPONENTS
#1085Adeno-Associated Virus Vector Delivery of Microrna-29 to Treat Muscular Dystrophy
#1086DUAL SUPRAMOLECULAR NANOPARTICLE VECTORS ENABLE CRISPR/CAS9-MEDIATED KNOCKIN OF RETINOSCHISIN 1 GENE-A POTENTIAL NON-VIRAL THERAPEUTIC SOLUTIONS FOR X-LINKED JUVENILE RETINOSCHISIS
#1087PREPARATION METHOD AND APPLICATION OF SINGLE EMULSIFIER AND DOUBLE EMULSION BASED ON DNA TRIANGULAR ORIGAMI TECHNOLOGY
#1088METHODS OF SYNTHESIZING RNA MOLECULES
#1089NUCLEIC ACID COMPOSITIONS
#1090Nuclease Resistant Polynucleotides and Uses Thereof
#1091LIBRARY OF BARCODED EXTRACELLULAR VESICLES
#1092METHOD OF TRANSACTIVATING A HOMOLOGOUS GENE OF A GENE OF INTEREST AND AN IN VITRO METHOD OF DIAGNOSING A DISEASE
#1093PROTEINS CONTAINING MULTIPLE, DIFFERENT UNNATURAL AMINO ACIDS AND METHODS OF MAKING AND USING SUCH PROTEINS
#1094COMPOSITIONS AND METHODS FOR TARGETED DELIVERY OF CRISPR-CAS EFFECTOR POLYPEPTIDES AND TRANSGENES
#1095LIGHT-INDUCIBLE CRISPR/CAS9 SYSTEM FOR GENOME EDITING
#1096MODIFIED iRNA AGENTS
#1097SYSTEM AND METHOD FOR COMBATING INFECTIONS DUE TO PATHOGENS BELONGING TO PHYLUM PROTEOBACTERIA
#1098TRANSKINGDOM PLATFORM FOR THERAPEUTIC NUCLEIC ACID DELIVERY
#1099CRISPR-RELATED METHODS AND COMPOSITIONS WITH GOVERNING gRNAS
#1100Targeted CRISPR Delivery Platforms
#1101Modified double-stranded RNA agents
#1102MODIFIED OLIGONUCLEOTIDES
#1103RNA-GUIDED CAS NUCLEASES AND USES THEREOF IN DIAGNOSTICS AND THERAPY
#1104Compositions and methods for organ specific delivery of nucleic acids
#1105Multiplex RNA-Guided Genome Engineering
#1106SYSTEM AND METHOD FOR COMBATING MYCOBACTERIUM TUBERCULOSIS INFECTIONS
#1107A METHOD TO PREPARE PERSONALIZED TARGET-IRRELEVANT GUIDE RNA POOL FOR CRISPR
#1108Crispr enzymes and systems
#1109COMPOSITIONS AND METHODS FOR HOMOLOGY-DIRECTED RECOMBINATION
#1110RNA NANOPARTICLE FOR LIVER CANCER TREATMENT
#1111COMPOSITIONS AND METHODS FOR LOADING EXTRACELLULAR VESICLES WITH CHEMICAL AND BIOLOGICAL AGENTS/MOLECULES
#1112Gene Panels for Molecular Subtype and Survival Risk Assessment of Lung Adenocarcinoma and Diagnostic Products and Applications Thereof
#1113CRISPR enabled multiplexed genome engineering
#1114EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
#1115MicroRNA-33 inhibitors and use thereof in the treatment of pulmonary fibrosis
#1116NOVEL CRISPR ENZYMES AND SYSTEMS
#1117Base editing enzymes
#1118ADMINISTRATION OF SPHERICAL NUCLEIC ACIDS FOR OPHTHALMOLOGICAL USES
#1119Oligonucleotide-ligand conjugates and process for their preparation
#1120METHOD FOR IDENTIFYING M1 GENERATION PLANT MUTANTS RESULTING FROM PHYSICAL AND CHEMICAL MUTAGENESIS AND FOR ACQUIRING MUTANT, IDENTIFICATION OF GENOTYPING PRIMER FOR ORYZA SATIVA MUTATION, MUTANT GENE, AND USE THEREOF
#1121COMPOSITIONS AND METHODS FOR IMPROVED GENE EDITING
#1122CRISPR-MEDIATED CAPTURE OF NUCLEIC ACIDS
#1123Method for the production of a catalytically active DNA molecule having improved activity and its use in a method of treating asthma
#1124STEREOSELECTIVE PH RESPONSIVE PEPTIDE DENDRIMERS FOR NUCLEIC ACID TRANSFECTION
#1125Compositions for identification of membrane targets for enhancement of T cell activity against cancer
#1126Genetically engineered cells
#1127Methods for creating bilayers for use with nanopore sensors
#1128SiRNA, medical compositions, and methods for treating type ii diabetes using the same
#1129Long Noncoding RNA Implicated in Cardiovascular Disease and Use Thereof
#1130COMPOSITIONS AND METHODS FOR IN VIVO GENE EDITING
#1131GENE VECTOR
#1132Crispr DNA targeting enzymes and systems
#1133Split CPF1 Protein
#1134Use of aptamers in proteomics
#1135METHODS FOR GENOMIC INTEGRATION
#1136CRISPR EPIGENETIC THERAPEUTICS FOR PAIN MANAGEMENT
#1137METHODS FOR DIAGNOSING THE EFFECTIVENESS OF ANTI-TUMOR TREATMENT
#1138CAS 9 RETROVIRAL INTEGRASE AND CAS 9 RECOMBINASE SYSTEMS FOR TARGETED INCORPORATION OF A DNA SEQUENCE INTO A GENOME OF A CELL OR ORGANISM
#1139COMPOSITIONS, SYSTEMS AND METHODS FOR CELL THERAPY
#1140AUGMENTED sgRNAS AND METHODS FOR THEIR USE TO ENHANCE SOMATIC AND GERMLINE PLANT GENOME ENGINEERING
#1141Safe harbor loci
#1142Extended dicer substrate agents and methods for the specific inhibition of gene expression
#1143Methods and Compositions for Selecting siRNA of Improved Functionality
#1144BASE EDITORS WITH DIVERSIFIED TARGETING SCOPE
#1145METHODS AND COMPOSITIONS FOR RNA-GUIDED TREATMENT OF HIV INFECTION
#1146METHOD AND SYSTEM FOR IDENTIFICATION OF CANDIDATE TARGET SITES FOR COMBATING PATHOGENS
#1147ASSAYS AND METHODS FOR DETERMINING ACTIVITY OF A THERAPEUTIC AGENT IN A SUBJECT
#1148METHODS AND REAGENTS FOR NUCLEIC ACID AMPLIFICATION AND/OR DETECTION
#1149Treatment Of Liver Disease With Ring Finger Protein 213 (RNF213) Inhibitors
#1150PROCESS OF DELIVERING SMALL RNAS TO SPERM
#1151LIBRARY CONSTRUCTION METHOD FOR DETECTING ENDOMETRIAL CANCER-RELATED GENE MUTATIONS BASED ON HIGH-THROUGHPUT SEQUENCING
#1152METHOD FOR STABILIZING INTRACELLULAR RNA
#1153PROCESS FOR FORMULATING AN ANIONIC AGENT
#1154NDUFS2 SUBUNIT KNOCKOUT HUMAN CELL LINE
#1155COMPOSITIONS AND METHODS FOR IMPROVING POD SHATTER TOLERANCE IN CANOLA
#1156POD SHATTER TOLERANCE IN BRASSICA PLANTS
#1157COMPOSITIONS AND METHODS FOR DELIVERY OF NUCLEIC ACIDS
#1158CRISPR-ASSOCIATED MU TRANSPOSASE SYSTEMS
#1159A METHOD FOR DEVELOPMENTALLY ACTIVATING A CELL
#1160Strategy to increase anti-viral, anti-microbial, and anti-fungal defense
#1161Class II, type V CRISPR systems
#1162GENE EDITING USING A MODIFIED CLOSED-ENDED DNA (CEDNA)
#1163NUCLEIC ACID-CONTAINING LIPID PARTICLES AND RELATED METHODS
#1164Defined multi-conjugates oligonucleotides
#1165Methods to detect motor neuron disease comprising micro-RNAs
#1166Chemically Ligated RNAs for CRISPR/Cas9-lgRNA Complexes as Antiviral Therapeutic Agents
#11672'-METHOXY SUBSTITUTED OLIGOMERIC COMPOUNDS AND COMPOSITIONS FOR USE IN GENE MODULATIONS
#1168Targeting ligands for tau pathology
#1169NOVEL CRISPR DNA TARGETING ENZYMES AND SYSTEMS
#1170LONG NON-CODING RNA IN CANCER
#1171COMPOUNDS AND METHODS USEFUL FOR MODULATING GENE SPLICING
#1172OLIGONUCLEOTIDE THERAPY FOR STARGARDT DISEASE
#1173RNA INTERFERENCE MEDIATED INHIBITION OF GENE EXPRESSION USING CHEMICALLY MODIFIED SHORT INTERFERING NUCLEIC ACID (SINA)
#1174COMPOSITIONS AND METHODS FOR MODULATING TTR EXPRESSION
#1175Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
#1176CRISPR MULTI-TARGET DETECTION METHOD AND TEST KIT THEREFOR
#1177Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
#1178Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
#1179Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription
#1180Platform for T lymphocyte genome engineering and in vivo high-throughput screening thereof
#1181CONTROL OF MAMMALIAN GENE DOSAGE USING CRISPR
#1182Systems and Methods for Designing RNA Nanostructures and Uses Thereof
#1183REVERSIR™ compounds
#1184RECOMBINANT AD35 VECTORS AND RELATED GENE THERAPY IMPROVEMENTS
#1185ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES
#1186AAV DELIVERY OF NUCLEOBASE EDITORS
#1187NANOVESICLES AND ITS USE FOR NUCLEIC ACID DELIVERY
#1188ANGIOTENSIN II TYPE 1 RECEPTOR TARGETED OLIGONUCLEOTIDES AND USES THEREOF
#1189OPTIMIZED GENETIC TOOL FOR MODIFYING BACTERIA
#1190Modulators of IRF4 expression
#1191Conjugation of lipophilic albumin-binding moiety to RNA for improved carrier-free in vivo pharmacokinetics and gene silencing
#1192NUCLEIC ACID COMPOSITIONS AND METHODS OF MULTI-EXON SKIPPING
#1193PROTECTIVE ELEMENTS FOR NUCLEIC ACID SYNTHETIC BIOLOGY
#1194NOVEL CRISPR-CAS SYSTEMS AND USES THEREOF
#1195Method to engineer transplantable human tissues
#1196EXOSOME COMPRISING STABILIZED RNA THERAPEUTICS
#1197Compositions and methods for organ specific delivery of nucleic acids
#1198LINKED TARGET CAPTURE
#1199RECOMBINANT MICROORGANISM HAVING HIGH ABILITY TO PRODUCE LUTEIN AND METHOD FOR PRODUCING LUTEIN USING THE SAME
#1200Peptide-Modified Hybrid Recombinant Adeno-Associated Virus Serotype Between AAV9 and AAVrh74 with Reduced Liver Tropism and Increased Muscle Transduction