109145 ⎘
Structure or type of the nucleic acid; Type of nucleic acid interfering N.A.
PLASMA piRNA COMBINATION FOR EARLY DIAGNOSIS OF GASTRIC CANCER AND APPLICATION THEREOF
#302APPLICATION OF ZINC FINGER PROTEIN 217 GENE IN PREPARING MEDICINES FOR TREATING OSTEOPOROSIS
#303RNAI CONSTRUCTS FOR INHIBITING PNPLA3 EXPRESSION AND METHODS OF USE THEREOF
#304PALMITOYLATION OF THE ALTERNATIVE AMINO TERMINUS OF THE BTK-C ISOFORM CONTROLS SUBCELLULAR DISTRIBUTION AND SIGNALING
#305NUCLEIC ACID, PHARMACEUTICAL COMPOSITION AND SIRNA CONJUGATE CONTAINING THE NUCLEIC ACID, PREPARATION METHOD THEREFOR, AND USE THEREOF
#306METHOD OF TREATING A MAMMAL WITH DIABETES ASSOCIATED KIDNEY DISEASE USING LOCAL ADMINISTRATION OF STEM CELLS WITH TRANSIENTLY REDUCED p53
#307COMPOSITIONS AND METHODS FOR TREATING HEPATITIS B VIRUS (HBV) INFECTION AND HBV-ASSOCIATED DISEASES
#308INHIBITION OF FOLLISTATIN
#309INHIBITORS OF EXPRESSION AND/OR FUNCTION
#310METHODS FOR TREATING NEUROINFLAMMATION
#311METHODS AND COMPOSITIONS FOR TREATING FIBROSIS
#312METHODS OF DELIVERING THERAPEUTIC AGENTS, AND LIPID COMPOSITIONS
#313METHODS AND COMPOSITIONS FOR MODULATING FIBRINOGEN
#314COMPOSITIONS AND THERAPEUTIC AGENTS FOR MODULATING INFLAMMATORY RESPONSES ON BOTH TUMOR AND IMMUNE CELLS
#315PRODUCTS AND COMPOSITIONS
#316INTERFERING RNA FOR INHIBITING PCSK9 GENE EXPRESSION AND USE THEREOF
#317TREATMENT OF MST1 RELATED DISEASES AND DISORDERS
#318MUCIN-5B (MUC5B) TARGETED SIRNA AND ANTISENSE OLIGONUCLEOTIDES AND METHODS OF USE THEREOF
#319CONJUGATES FOR TISSUE-SPECIFIC OLIGONUCLEOTIDE DELIVERY
#320NUCLEIC ACID FOR TRANSFECTION
#321PRODUCTS AND COMPOSITIONS
#322RNAI CONSTRUCTS FOR INHIBITING SCAP EXPRESSION AND METHODS OF USE THEREOF
#323ANTISENSE OLIGONUCLEOTIDE FOR TREATING MELANOMA
#324COMPOSITIONS FOR TREATING SYNGAP-1 RELATED NEURODEVELOPMENTAL DISORDERS
#325Facile Assembly of Soft Nanoarchitectures and Co-Loading of Hydrophilic and Hydrophobic Molecules via Flash Nanoprecipitation
#326SYSTEMIC DELIVERY OF MYOSTATIN SHORT INTERFERING NUCLEIC ACIDS (SINA) CONJUGATED TO A LIPOPHILIC MOIETY
#327GELATIN AND LIPIDOID GENETIC DELIVERY PARTICLE
#328COMPOSITIONS OF LIPID NANOPARTICLES FOR PLASMID DNA DELIVERY TO THE LIVER AND METHODS FOR PREPARING THE SAME
#329PHARMACEUTICAL COMPOSITION FOR TREATING OR PREVENTING MALIGNANT BREAST CANCER
#330INHIBITORS OF EXPRESSION AND/OR FUNCTION
#33117BETA-HYDROXYSTEROID DEHYDROGENASE TYPE 13 (HSD17B13) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#332TREATMENT OF CARDIOVASCULAR DISEASE
#333DOUBLE-STRANDED RNA MOLECULE AND PHARMACEUTICAL USE THEREOF
#334SINGLE-STRANDED LOOP OLIGONUCLEOTIDES
#335miRNA-BASED COMPOSITIONS AND METHODS OF USE THEREOF
#336HUMAN ANTIBODIES TO THE GLUCAGON RECEPTOR
#337AMINOOXY CLICK CHEMISTRY (AOCC): A VERSATILE CONJUGATION APPROACH
#338METHOD OF SYNTHESIS OF AN IONIZABLE CATIONIC LIPID
#339NOVEL LIPIDS BASED ON OLIGO-y-GLUTAMIC ACID DERIVATIVES AND LIPID NANOPARTICLES CONTAINING THE SAME, AND USES THEREOF
#340COMPOSITIONS AND METHODS FOR TREATING HEPATITIS D VIRUS (HDV) INFECTION AND ASSOCIATED DISEASES
#341METHODS AND COMPOSITIONS RELATING TO TREATMENT OF CNS DISEASES
#342ONE-STEP CONSTRUCTION OF ALLOGENIC CAR-NK CELLS WITH INCREASED ANTI-TUMOR CYTOTOXICITY AND RESISTANCE TO HOST CELL REJECTION
#343REGULATION OF TYPE I IFN SIGNALING BY TARGETING A DECOY RECEPTOR
#344SYNTHETIC TRANSFER RNA WITH MODIFIED NUCLEOTIDES
#345COMPOSITIONS AND METHODS FOR INHIBITING CYTOCHROME P450 FAMILY 7 SUBFAMILY A MEMBER 1 (CYP7A1) EXPRESSION
#346OLIGONUCLEOTIDE-BASED DELIVERY VEHICLE FOR OLIGONUCLEOTIDES AGENTS AND METHODS OF USE THEREOF
#347CERTAIN DUX4 INHIBITORS AND METHODS OF USE THEREOF
#348COMPOSITION AND METHOD FOR INHIBITING EXPRESSION OF PROTEIN LPA(APO(A))
#349METHODS AND COMPOSITIONS FOR INHIBITING MISMATCH REPAIR
#350MUC5AC-TARGETED ANTISENSE OLIGONUCLEOTIDES AND RELATED METHODS FOR MODULATING MUCIN EXPRESSION
#351MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#352NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF
#353IMMUNOSTIMULATORY NANOPARTICLE
#354COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS
#355ISOLATION OF ANTI-INFLAMMATORY NEUTROPHIL OR MONOCYTE SUBSET AND USE IN TREATING CARDIOVASCULAR DISEASES
#356COMPOSITIONS AND METHODS OF MODULATING XANTHINE DEHYDROGENASE
#357USE OF ANTISENSE OLIGONUCLEOTIDE IN PREPARATION OF DRUG FOR TREATING DISEASE CAUSED BY ABNORMAL THYROID
#358EPICARDIAL CELL REGENERATION PROMOTER AND METHOD FOR PROMOTING EPICARDIAL CELL REGENERATION
#359VARIANT RNAi
#360STAT3 TARGETING OLIGONUCLEOTIDES AND USES THEREOF
#361SUGAR-CONJUGATED LIPID NANOPARTICLES FOR TARGETED DELIVERY OF SIRNA TO HEPATOCYTES
#362Compositions and Methods for RNA Editing
#363COMPOSITIONS AND METHODS FOR TREATING RETINAL DISEASES
#364Oligonucleotide Terminal Phosphate Derivatives and Method of Use
#365ACTIN-BINDING LIM PROTEIN 3 (ABLIM3) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#366RNA COMPOSITIONS AND THERAPEUTIC METHODS THEREOF
#367TREATMENT OF CARDIOVASCULAR DISEASE
#368COMPOSITIONS FOR TREATING AND/OR PREVENTING CELL OR TISSUE NECROSIS SPECIFICALLY TARGETING CATHEPSIN C AND/OR CELA1 AND/OR CELA3A AND/OR STRUCTURALLY RELATED ENZYMES THERETO
#369FN3 DOMAIN-siRNA CONJUGATES AND USES THEREOF
#370CATIONIC LIPIDS CONTAINING SILICON
#371OLIGONUCLEOTIDES FOR PRNP MODULATION
#372METHODS AND COMPOSITIONS FOR TREATING A PROPROTEIN CONVERTASE SUBTILISIN KEXIN (PCSK9) GENE-ASSOCIATED DISORDER
#373Allele-Specific Silencing of Transforming Growth Factor Beta Induced Gene with R124H Mutation Using Short Interfering RNA
#374LPA inhibitors and uses thereof
#375CO-DELIVERY OF INHIBITORY NUCLEIC ACIDS AND GENOME EDITORS FOR TUMOR THERAPY
#376BICYCLIC PEPTIDE LIGANDS SPECIFIC FOR TRANSFERRIN RECEPTOR 1 (TfR1)
#377SERUM AMYLOID P COMPONENT (APCS) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#378TOPICAL PATCH COMPOSITION FOR TARGETED SIRNA NANOPLEX DELIVERY AND GENE THERAPIES AND METHOD OF MAKING AND USE THEREOF
#379COMPOSITION FOR PREVENTING OR TREATING CANCER, CONTAINING LIPID NANOPARTICLES
#380NOVEL FISH TOTIVIRUS
#381Methods for Suppression of Gene Silencing in Plants
#382BIS-RNAI COMPOUNDS FOR CNS DELIVERY
#383ANTI-CANCER AGENTS
#384CIRCRNAS FOR GENE SILENCING
#385ORGANIC COMPOSITIONS TO TREAT BETA-CATENIN-RELATED DISEASES
#386MSI2 AS A THERAPEUTIC TARGET FOR THE TREATMENT OF MYOTONIC DYSTROPHY
#387CATIONIC SULFONAMIDE AMINO LIPIDS AND AMPHIPHILIC ZWITTERIONIC AMINO LIPIDS
#388LIPID NANOPARTICLES COMPRISING MANNOSE OR USES THEREOF
#389Olfactory Delivery Scaffolds Using Antisense Oligonucleotides and Methods for Making and Using Same
#390METHODS FOR THE IDENTIFICATION AND TREATMENT OF SEVERE FORMS OF COVID-19
#391PHARMACEUTICAL COMBINATIONS FOR TREATMENT OF HBV
#392NUCLEIC ACID-POLYPEPTIDE NANO-PHARMACEUTICAL COMPOSTION FOR TREATING AND PREVENTING HUMAN PAPILLOMA VIRUS INFECTION
#393RNAI AGENTS TARGETING CIDEB AND RELATED METHODS
#394COMPOSITIONS AND METHODS FOR MODULATING APOC3 EXPRESSION
#395METHOD OF TREATING, AMELIORATING AND/OR PREVENTING POLYCYSTIC KIDNEY DISEASE
#396COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH siRNAS TARGETING TBX3
#397COMPOSITIONS AND METHODS OF MODULATING RNA AND PROTEIN INTERACTIONS
#398NANO-IN-MICRO ENCAPSULATED siRNA DRY POWDER, METHOD FOR PRODUCING THE SAME AND USE OF A POWDER FORMULATION
#399COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH SIRNAS TARGETING SMYD2
#400MUSK-TARGETING OLIGONUCLEOTIDES
#401KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#402TREATMENT OF H3.3-MUTANT BRAIN CANCER WITH PNKP INHIBITORS
#403COMPOSITION AND METHOD FOR INHIBITING EXPRESSION OF PROTEIN LPA(APO(A))
#404SIGNAL ACTIVATABLE NUCLEIC ACID COMPLEXES
#405NON-HALLUCINOGENIC PSYCHEDELIC FUNGI
#406MARKERS SELECTIVELY DEREGULATED IN TUMOR-INFILTRATING REGULATORY T CELLS
#407METHODS AND COMPOSITIONS FOR TREATING ATHEROSCLEROSIS
#408SIRNA OR SALT THEREOF AND MEDICAMENT FOR INHIBITING EXPRESSION OF TMPRSS6 GENE, AND USE THEREOF
#409POLYNUCLEIC ACID MOLECULES FOR INHIBITING EXPRESSION OF FXI, PHARMACEUTICAL COMPOSITIONS, AND USES THEREOF
#410XANTHINE DEHYDROGENASE (XDH) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#411DOUBLE-STRANDED RNA MOLECULE FOR ADMINISTRATION TO THE EYE
#412MODIFIED OLIGONUCLEOTIDES
#413MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#414SARM1 RNAi AGENTS
#415ANTIMICROBIAL PEPTIDE DERIVATIVE AND USE THEREOF
#416LIPID NANOPARTICLES, NUCLEIC ACIDS, AND METHODS OF USE
#417piRNA-BASED CONSTRUCTS FOR REGULATING GENE EXPRESSION AND METHODS OF USE THEREOF
#418COMPOSITIONS AND METHODS FOR TREATMENT OF PRION DISEASES
#419PNPLA3-TARGETING SHORT INTERFERING RNA (SIRNA) MOLECULES AND USES THEREOF
#420UNIVERSAL NON-TARGETING SIRNA COMPOSITIONS AND METHODS OF USE THEREOF
#421COMPOSITIONS AND METHODS FOR INHIBITING STAG1 EXPRESSION AND USES THEREOF
#422Targeting Ligands For Therapeutic Compounds
#423CAR-EXPRESSING CELLS AGAINST MULTIPLE TUMOR ANTIGENS AND USES THEREOF
#424GLYCAN CONJUGATE COMPOSITIONS AND METHODS
#425METHOD OF DELIVERY OF DNA OR RNA CARGO USING UNSHIELDED LIPID NANOPARTICLES AND COMPOSITIONS THEREOF
#426POLY-GA PROTEINS IN ALZHEIMER’S DISEASE
#427Methods Of Treating Decreased Bone Mineral Density With Cluster Of Differentiation 109 (CD109) Inhibitors
#428MULTI-TARGETED SINGLE ENTITY CONJUGATES
#429COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH SIRNAS TARGETING CIDEB
#430METHODS FOR IMPROVING ADENO-ASSOCIATED VIRUS (AAV) DELIVERY
#431Methods and Compositions for Inhibiting the Growth and/or proliferation of MYC-Driven Tumor Cells
#432METHODS AND SYSTEMS FOR IDENTIFYING AND VALIDATING A GENE COMBINATION ASSOCIATED WITH A TRAIT AND USES THEREOF
#433Use of Trinucleotide Repeat RNAs To Treat Cancer
#434PRODUCTS AND METHODS FOR INHIBITION OF EXPRESSION OF DYNAMIN-1 VARIANTS
#435Nucleic acids for inhibiting expression of MASP-2 in a cell
#436Methods For The Treatment Of ANGPTL3-Related Diseases And Disorders
#437DELIVERY OF HYDROPHOBIC ACTIVE AGENT PARTICLES
#438METHODS AND COMPOSITIONS FOR NON-MYELOABLATIVE BONE MARROW RECONSTITUTION
#439COMPOUNDS TO INHIBIT YTHDF2, T HELPER CELLS LACKING EXPRESSION OF YTHDF2, AND METHODS TO TREAT CANCER
#440COMPOSITIONS AND METHODS FOR TREATMENT OF SEPSIS-RELATED DISORDERS
#441COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH SIRNAS TARGETING GPAM
#442Process to Inhibit or Eliminate Eosinophilic Diseases of the Airway and Related Conditions
#443COMBINATION OF A GREMLIN-1 ANTAGONIST WITH AN INHIBITOR OF RAS-RAF-MEK-ERK SIGNALLING
#444COMPOSITIONS AND METHODS FOR ORGAN SPECIFIC DELIVERY OF NUCLEIC ACIDS
#445PREPARATION AND ANTI-TUMOR APPLICATION OF GENE THERAPY VECTOR INTERFERING CKLF-LIKE MARVEL TRANSMEMBRANE DOMAIN-CONTAINING PROTEIN 6 (CMTM6) EXPRESSION
#446LIPID CONJUGATES FOR THE DELIVERY OF THERAPEUTIC AGENTS TO CNS TISSUE
#447ANTISENSE NUCLEIC ACID CAPABLE OF INHIBITING BIOSYNTHESIS OF CHONDROITIN SULFATE
#448METHOD FOR CONSTRUCTING GENE NETWORK THROUGH SINGLE-CELL TRANSCRIPTOME AND METHOD FOR DISCOVERING KEY GENE IN DIFFERENTIATION USING SAME
#449MODIFIED DOUBLE-STRANDED OLIGONUCLEOTIDE MOLECULE, MODIFIED DOUBLE-STRANDED OLIGONUCLEOTIDE CONJUGATE, AND USE THEREOF
#450Nucleic acid regulation of ApoE
#451OLIGONUCLEOTIDES WITH 2'-DEOXY-2'-F-2'-C-METHYL NUCLEOTIDES
#452IMMUNE CELLS WITH COMBINATION GENE PERTURBATIONS
#453TRANS-VACCENIC ACID (TVA) AND DERIVATIVES THEREOF IN T CELL-BASED CANCER THERAPIES
#454IMMUNE CELLS HAVING CO-EXPRESSED TGFBR SHRNAS
#455COMPOSITIONS AND METHODS FOR TREATMENT OF DOMINANT RETINITIS PIGMENTOSA
#456ANTI-HELICASE THERAPY FOR TREATMENT OF REPEAT EXPANSION DISEASE
#457COMPOSITION FOR PREVENTION OR TREATMENT OF CANCER COMPRISING DDX54 INHIBITOR AND CANCER IMMUNOTHERAPY AGENT
#458RNAi Agents for Inhibiting Expression of Complement Factor B (CFB), Pharmaceutical Compositions Thereof, and Methods of Use
#459BRANCHED TRIPLE LIPID-MODIFIED NUCLEIC ACID COMPOUNDS
#460TREATING METASTATIC CANCER AND MODEL SYSTEMS FOR METASTATIC DISEASE
#461BICYCLIC HETEROCYCLES AND THEIR LIGANDS FOR TARGETED DELIVERY OF THERAPEUTIC AGENTS
#462NOVEL APPROACH FOR TREATMENT OF CANCER USING IMMUNOMODULATION
#463RNAi Agents for Inhibiting Expression of Activin Receptor-Like Kinase 7 (ALK7), Compositions Thereof, and Methods of Use
#464RNAI CONSTRUCTS FOR INHIBITING PNPLA3 EXPRESSION AND METHODS OF USE THEREOF
#465AMPHIREGULIN GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTING AND TREATING FIBROSIS-RELATED DISEASES AND RESPIRATORY DISEASES, COMPRISING SAME
#466Use of Non-Coding Nucleic Acid for Crop Improvement and Protection Against Microbes
#467ASYMMETRIC RNA MOLECULES
#468MODIFIED RNA AGENTS WITH REDUCED OFF-TARGET EFFECT
#469METHODS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS
#470POLYNUCLEOTIDE AGENTS TARGETING COMPLEMENT COMPONENT C5 AND METHODS OF USE THEREOF
#471COMPOSITION FOR PREVENTING OR TREATING MYOCARDITIS, COMPRISING VLA-4 INHIBITOR
#472CRY PROTEIN CRYSTALS AND METHODS OF USE
#473LIPID NANOPARTICLES
#474COMPOSITIONS AND METHODS FOR MODULATING NaV1.8
#475MODIFIED RNA AGENTS WITH REDUCED OFF-TARGET EFFECT
#476Treatment Of Liver Disease With Mitochondrial Glycerol-3-Phosphate Acyltransferase (GPAM) Inhibitors
#477PHARMACEUTICAL COMPOSITION FOR TREATMENT OR PREVENTION OF FIBROTIC DISEASE
#478LNCRNA TRANSCRIPTS IN MELANOMAGENESIS
#479GALNAC COMPOSITIONS FOR IMPROVING SIRNA BIOAVAILABILITY
#480COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION OF ALPHA-1 ANTITRYPSIN
#481COMPOSITIONS AND METHODS FOR THE TREATMENT OF ANGIOPOIETIN LIKE 7 (ANGPTL7) RELATED DISEASES
#482RNAi Agents of Modulating PLP1
#483SIRNA TARGETING ANGIOTENSINOGEN AND PHARMACEUTICAL USE OF SIRNA
#484LIPID NANOPARTICLES USED TO TRANSPORT NUCLEIC ACIDS INTO LYMPHATIC ENDOTHELIUM CELLS
#485COMPOSITIONS AND METHODS FOR IMPROVING PERSISTENCE OF CELLS FOR ADOPTIVE TRANSFER
#486METHODS AND COMPOSITIONS FOR TREATING TNNT2 RELATED CARDIOMYOPATHY WITH A VIRAL VECTOR
#487COMPOSITIONS AND METHODS OF TREATING MUSCLE ATROPHY AND MYOTONIC DYSTROPHY
#488PHOSPHORODIAMIDATE MORPHOLINO OLIGOMER CONJUGATES
#489IMMUNOTHERAPEUTIC CONSTRUCTS AND METHODS OF THEIR USE
#490GENE-REGULATING COMPOSITIONS AND METHODS FOR IMPROVED IMMUNOTHERAPY
#491METHODS OF TREATING CHOLANGIOCARCINOMA
#492LIPID PARTICLE, COMPOSITION CONTAINING LIPID PARTICLE, KIT CONTAINING LIPID PARTICLE, AND ACTIVE AGENT DELIVERY METHOD USING LIPID PARTICLE
#493COMPOSITIONS AND METHODS FOR MANAGEMENT OF WHITEFLY
#494METHODS OF DESIGNING CONDITIONAL-ACTIVATABLE SMALL INTERFERING RNA SENSORS
#495METHODS FOR IDENTIFYING THERAPEUTIC AGENTS
#496siRNA SUPPRESSING EXPRESSION OF TRANSFERRIN RECEPTOR 2
#497CHEMICALLY MODIFIED OLIGONUCLEOTIDE HAVING RNAi ACTIVITY
#498COMPOUNDS AND METHODS FOR REDUCING IFNAR1 EXPRESSION
#499KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#500TREATMENT AND DIAGNOSIS OF INFLAMMATORY DISORDERS
#501Methods Of Treating Liver Diseases With Phosphodiesterase 3B (PDE3B) Inhibitors
#502SARM1 RNA INTERFERENCE AGENTS
#503NONCOVALENTLY BRANCHED OLIGONUCLEOTIDE COMPOSITIONS
#504POLYNUCLEIC ACID MOLECULES TARGETING APOC3 AND USES THEREOF
#505POLYNUCLEIC ACID MOLECULES FOR INHIBITING EXPRESSION OF LP(A), PHARMACEUTICAL COMPOSITIONS, AND USES THEREOF
#506FULLY STABILIZED ASYMMETRIC SIRNA
#507HIGH MOBILITY GROUP BOX-1 (HMGB1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#508LIPOPHILIC OLIGONUCLEOTIDE CONJUGATES
#509SIGNAL ACTIVATABLE NUCLEIC ACID CONSTRUCTS WITH WOBBLE BASE PAIRINGS
#510CONDITIONALLY ACTIVATABLE NUCLEIC ACID COMPLEXES
#511ENHANCING ESTROGEN RECEPTOR ALPHA IN OSTEOARTHRITIS
#512MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#513BLOCK COPOLYMERS
#514Treatment Methods for Fibrosis Targeting SMOC2
#515PYK2 INHIBITION MODULATES IMMUNE CELL FUNCTION
#516TARGETING NEUROPILIN 2 (NRP2) IN LETHAL PROSTATE CANCER
#517USE OF CDK16 AS TARGET IN PREPARATION OF MEDICINE FOR TREATING TRIPLE-NEGATIVE BREAST CANCER
#518RNAI AGENT TARGETING MARC1 GENE, AND USE THEREOF
#519USE OF DINUCLEOTIDE REPEAT RNAS TO TREAT CANCER
#520TARGETED COMPOSITIONS
#521ATXN2 RNA INTERFERENCE AGENTS
#522SYSTEMS
#523IL-6 INHIBITOR AS TREATMENT FOR NEPHROPATHY
#524MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#525G ALPHA Q/11 INHIBITORS FOR USE AS AN ANALGESIC
#526TARGETING PTCHD1 AND NEURONAL CHOLESTEROL TO ENHANCE SAFETY OF OPIOID ANALGESICS
#527HIF-1 ACTIVATORS AND USES THEREOF
#528COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE SIGNAL REGULATORY PROTEIN ALPHA (SIRPa) GENE
#529COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE PCSK9 GENE
#530APPLICATION OF MECHANICAL-FORCE SENSITIVE MACROPHAGE SUBSET IN PANCREATIC CANCER DIAGNOSIS OR PROGNOSIS EVALUATION
#531Microtubule Associated Protein Tau (MAPT) iRNA Agent Compositions and Methods of Use Thereof
#532METHODS OF PREPARING HIGH CONCENTRATION LIQUID DRUG SUBSTANCES
#533NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF
#534GENE THERAPEUTICS FOR TREATING BONE DISORDERS
#535MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#536INHIBIN SUBUNIT BETA E INHIBITOR AND METHODS OF USE THEREOF
#537ULTRASOUND RESPONSIVE LIPID NANOPARTICLE CARRYING GENES AND CELL MEMBRANE, ITS PREPARATION METHOD AND APPLICATION
#538SIRNA SPECIFICALLY BINDING TO M2 MACROPHAGE CD206 AND APPLICATION THEREOF
#539METHOD FOR TREATING TUBULAR AGGREGATE MYOPATHY AND STORMORKEN SYNDROME
#540Promotion of Cardiomyocyte Proliferation and Regenerative Treatment of the Heart by Inhibition of microRNA-128
#541Brush polymer-oligonucleotide conjugates for the treatment of muscular dystrophy
#542COMPOSITIONS AND METHODS FOR IMPROVING STRAND BIASED
#543Therapeutic Inhibition of LPA Expression
#544CATIONIC LIPIDS FOR NUCLEIC ACID DELIVERY AND PREPARATION THEREOF
#545METHOD FOR IMPROVING AUDITORY PERCEPTION USING A VIPR1 INHIBITOR
#546DESIGN AND DEVELOPMENT OF A NOVEL MESSENGER RNA THERAPEUTIC TO TREAT ATHEROSCLEROSIS
#547BRAIN TUMOR MODEL
#548RNAI CONSTRUCTS FOR INHIBITING PNPLA3 EXPRESSION AND METHODS OF USE THEREOF
#549Products and Methods for Treatment of Amyotrophic Lateral Sclerosis
#550LINKAGE MODIFIED OLIGOMERIC COMPOUNDS AND USES THEREOF
#551GENETICALLY-MODIFIED IMMUNE CELLS COMPRISING A MICRORNA-ADAPTED SHRNA (SHRNAMIR)
#552MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#553METHOD FOR PREPARING LIPOSOMES
#554Methods and Compositions for RNA-Directed Target DNA Modification and For RNA-Directed Modulation of Transcription
#555Compositions and Methods for Enhancing AAV Therapy and Decreasing Tropism of AAV to the Liver
#556COMPOSITIONS AND METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS (ALS)
#557COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF PREKALLIKREIN (PKK) PROTEIN
#558OLIGONUCLEOTIDES WITH ETHYLENE GLYCOL MODIFICATION
#559EGFL6 SPECIFIC MONOCLONAL ANTIBODIES AND METHODS OF THEIR USE
#560TREATMENT OF SMOKING WITH CHOLINERGIC RECEPTOR NICOTINIC BETA 3 SUBUNIT (CHRNB3) INHIBITORS
#561ANTI-PTEN RNA INTERFERENCE OLIGONUCLEOTIDES AND USES THEREOF
#562ANTISENSE OLIGONUCLEOTIDES TARGETING ADENOSINE KINASE
#563COMPOSITIONS AND METHODS COMPRISING ENGINEERED SHORT NUCLEAR RNA (SNRNA)
#564iRNA Compositions and Methods for Silencing ANGPTL4
#565NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF COMPLEMENT FACTOR B (CFB) IN A CELL
#566USE OF ETV3 OR ETV6 INHIBITORS FOR BLOCKING THE DIFFERENTIATION OF MONOCYTES INTO DENDRITIC CELLS
#567NUCLEIC ACID MODIFIED BIOLOGICAL CELL WITH EXPANSION-DEPENDENT GENE EXPRESSION
#568COMPOSITIONS FOR EDITING MECP2 TRANSCRIPTS AND METHODS THEREOF
#569Treatment Of Myeloid Cell Dysfunction With Membrane Spanning 4-Domains A6A (MS4A6A) Inhibitors
#570COMPOSITION FOR PREVENTING OR TREATING CANCER COMPRISING MSH2 OR MSH6 INHIBITOR AS ACTIVE INGREDIENT
#571NANOPARTICLE VECTOR FOR RNA SELF-DELIVERY, AND PREPARATION METHOD THEREFOR AND USE THEREOF
#572Treatment Of Osteoarthritis With Procollagen Galactosyl Transferase 2 (COLGALT2) Inhibitors
#573Treatment Of Macular Degeneration With Complement Factor D (CFD) Inhibitors
#574siRNA based on RNA sequence of SARS-CoV-2 and use thereof
#575Treatment Of Liver Disease Or Metabolic Disorder With Folliculin Interacting Protein 1 (FNIP1) Inhibitors And/Or Folliculin (FLCN) Inhibitors
#576EPO RECEPTOR AGONISTS AND ANTAGONISTS
#577EPO RECEPTOR AGONISTS AND ANTAGONISTS
#578CD71 BINDING FIBRONECTIN TYPE III DOMAINS
#579COMPOSITIONS AND METHODS FOR TREATING CANCERS
#580ASSESSMENT AND TREATMENT OF CHRONIC HEPATITIS B
#581MODULATION OF TGF BETA SIGNALING IN GENETICALLY-MODIFIED EUKARYOTIC CELLS
#582ANISAMIDE-CONTAINING LIPIDS AND COMPOSITIONS AND METHODS OF USE THEREOF
#583Methods and Compositions for RNA-Directed Target DNA Modification and for RNA-Directed Modulation of Transcription
#584DEPLETION OF FNDC5 REDUCES CANCER INDUCED MUSCLE LOSS/CACHEXIA
#585Modulation of TJPI Expression to Treat Liver Diseases
#586COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#587THERAPEUTIC SUPPRESSOR TRNA TO TREAT GENETIC DISEASES
#588ANTIVIRAL HAIRPIN CONSTRUCTS AND METHODS OF USE THEREOF
#589HIV PRE-IMMUNIZATION AND IMMUNOTHERAPY
#590METHODS OF PRODUCING CELLS RESISTANT TO HIV INFECTION
#591LIPID NANOPARTICLES
#592Treatment Of Uveitis With Endoplasmic Reticulum Aminopeptidase 1 (ERAP1) Inhibitors
#593MODULATORY POLYNUCLEOTIDES
#594MODULATION OF SUV39H1 EXPRESSION BY RNAS
#595METHOD FOR THE DIAGNOSIS, PROGNOSIS AND TREATMENT OF CANCER METASTASIS
#596COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION OF LPA
#597LIPID NANOPARTICLE (LNP) COMPOSITIONS FOR BRAIN-SELECTIVE CARGO DELIVERY, AND METHODS OF USE THEREOF
#598THERAPY FOR POLYCYSTIC KIDNEY DISEASE
#599METHOD OF DELIVERY OF DNA OR RNA CARGO USING UNSHIELDED LIPID NANOPARTICLES AND COMPOSITIONS THEREOF
#600HIGH MOLECULAR WEIGHT MODIFIED RNA COMPOSITIONS