ClassID:

109145

C12N2310/14 - page 2 - CPC Classification

Classification description:

Structure or type of the nucleic acid; Type of nucleic acid interfering N.A.

Recent Application in this class:
#301
20250322953
2025-10-16

PLASMA piRNA COMBINATION FOR EARLY DIAGNOSIS OF GASTRIC CANCER AND APPLICATION THEREOF

#302
20250320507
2025-10-16

APPLICATION OF ZINC FINGER PROTEIN 217 GENE IN PREPARING MEDICINES FOR TREATING OSTEOPOROSIS

#303
20250320502
2025-10-16

RNAI CONSTRUCTS FOR INHIBITING PNPLA3 EXPRESSION AND METHODS OF USE THEREOF

#304
20250320501
2025-10-16

PALMITOYLATION OF THE ALTERNATIVE AMINO TERMINUS OF THE BTK-C ISOFORM CONTROLS SUBCELLULAR DISTRIBUTION AND SIGNALING

#305
20250320500
2025-10-16

NUCLEIC ACID, PHARMACEUTICAL COMPOSITION AND SIRNA CONJUGATE CONTAINING THE NUCLEIC ACID, PREPARATION METHOD THEREFOR, AND USE THEREOF

#306
20250320499
2025-10-16

METHOD OF TREATING A MAMMAL WITH DIABETES ASSOCIATED KIDNEY DISEASE USING LOCAL ADMINISTRATION OF STEM CELLS WITH TRANSIENTLY REDUCED p53

#307
20250320497
2025-10-16

COMPOSITIONS AND METHODS FOR TREATING HEPATITIS B VIRUS (HBV) INFECTION AND HBV-ASSOCIATED DISEASES

#308
20250320495
2025-10-16

INHIBITION OF FOLLISTATIN

#309
20250320494
2025-10-16

INHIBITORS OF EXPRESSION AND/OR FUNCTION

#310
20250319139
2025-10-16

METHODS FOR TREATING NEUROINFLAMMATION

#311
20250319117
2025-10-16

METHODS AND COMPOSITIONS FOR TREATING FIBROSIS

#312
20250319037
2025-10-16

METHODS OF DELIVERING THERAPEUTIC AGENTS, AND LIPID COMPOSITIONS

#313
20250319023
2025-10-16

METHODS AND COMPOSITIONS FOR MODULATING FIBRINOGEN

#314
20250313900
2025-10-09

COMPOSITIONS AND THERAPEUTIC AGENTS FOR MODULATING INFLAMMATORY RESPONSES ON BOTH TUMOR AND IMMUNE CELLS

#315
20250313846
2025-10-09

PRODUCTS AND COMPOSITIONS

#316
20250313844
2025-10-09

INTERFERING RNA FOR INHIBITING PCSK9 GENE EXPRESSION AND USE THEREOF

#317
20250313841
2025-10-09

TREATMENT OF MST1 RELATED DISEASES AND DISORDERS

#318
20250313840
2025-10-09

MUCIN-5B (MUC5B) TARGETED SIRNA AND ANTISENSE OLIGONUCLEOTIDES AND METHODS OF USE THEREOF

#319
20250313839
2025-10-09

CONJUGATES FOR TISSUE-SPECIFIC OLIGONUCLEOTIDE DELIVERY

#320
20250313838
2025-10-09

NUCLEIC ACID FOR TRANSFECTION

#321
20250313837
2025-10-09

PRODUCTS AND COMPOSITIONS

#322
20250313834
2025-10-09

RNAI CONSTRUCTS FOR INHIBITING SCAP EXPRESSION AND METHODS OF USE THEREOF

#323
20250313833
2025-10-09

ANTISENSE OLIGONUCLEOTIDE FOR TREATING MELANOMA

#324
20250313832
2025-10-09

COMPOSITIONS FOR TREATING SYNGAP-1 RELATED NEURODEVELOPMENTAL DISORDERS

#325
20250313675
2025-10-09

Facile Assembly of Soft Nanoarchitectures and Co-Loading of Hydrophilic and Hydrophobic Molecules via Flash Nanoprecipitation

#326
20250312490
2025-10-09

SYSTEMIC DELIVERY OF MYOSTATIN SHORT INTERFERING NUCLEIC ACIDS (SINA) CONJUGATED TO A LIPOPHILIC MOIETY

#327
20250312481
2025-10-09

GELATIN AND LIPIDOID GENETIC DELIVERY PARTICLE

#328
20250312430
2025-10-09

COMPOSITIONS OF LIPID NANOPARTICLES FOR PLASMID DNA DELIVERY TO THE LIVER AND METHODS FOR PREPARING THE SAME

#329
20250306008
2025-10-02

PHARMACEUTICAL COMPOSITION FOR TREATING OR PREVENTING MALIGNANT BREAST CANCER

#330
20250304969
2025-10-02

INHIBITORS OF EXPRESSION AND/OR FUNCTION

#331
20250304967
2025-10-02

17BETA-HYDROXYSTEROID DEHYDROGENASE TYPE 13 (HSD17B13) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#332
20250304966
2025-10-02

TREATMENT OF CARDIOVASCULAR DISEASE

#333
20250304965
2025-10-02

DOUBLE-STRANDED RNA MOLECULE AND PHARMACEUTICAL USE THEREOF

#334
20250304957
2025-10-02

SINGLE-STRANDED LOOP OLIGONUCLEOTIDES

#335
20250304956
2025-10-02

miRNA-BASED COMPOSITIONS AND METHODS OF USE THEREOF

#336
20250304704
2025-10-02

HUMAN ANTIBODIES TO THE GLUCAGON RECEPTOR

#337
20250304613
2025-10-02

AMINOOXY CLICK CHEMISTRY (AOCC): A VERSATILE CONJUGATION APPROACH

#338
20250304532
2025-10-02

METHOD OF SYNTHESIS OF AN IONIZABLE CATIONIC LIPID

#339
20250302991
2025-10-02

NOVEL LIPIDS BASED ON OLIGO-y-GLUTAMIC ACID DERIVATIVES AND LIPID NANOPARTICLES CONTAINING THE SAME, AND USES THEREOF

#340
20250302951
2025-10-02

COMPOSITIONS AND METHODS FOR TREATING HEPATITIS D VIRUS (HDV) INFECTION AND ASSOCIATED DISEASES

#341
20250302918
2025-10-02

METHODS AND COMPOSITIONS RELATING TO TREATMENT OF CNS DISEASES

#342
20250297263
2025-09-25

ONE-STEP CONSTRUCTION OF ALLOGENIC CAR-NK CELLS WITH INCREASED ANTI-TUMOR CYTOTOXICITY AND RESISTANCE TO HOST CELL REJECTION

#343
20250297262
2025-09-25

REGULATION OF TYPE I IFN SIGNALING BY TARGETING A DECOY RECEPTOR

#344
20250297261
2025-09-25

SYNTHETIC TRANSFER RNA WITH MODIFIED NUCLEOTIDES

#345
20250297260
2025-09-25

COMPOSITIONS AND METHODS FOR INHIBITING CYTOCHROME P450 FAMILY 7 SUBFAMILY A MEMBER 1 (CYP7A1) EXPRESSION

#346
20250297258
2025-09-25

OLIGONUCLEOTIDE-BASED DELIVERY VEHICLE FOR OLIGONUCLEOTIDES AGENTS AND METHODS OF USE THEREOF

#347
20250297251
2025-09-25

CERTAIN DUX4 INHIBITORS AND METHODS OF USE THEREOF

#348
20250297250
2025-09-25

COMPOSITION AND METHOD FOR INHIBITING EXPRESSION OF PROTEIN LPA(APO(A))

#349
20250297248
2025-09-25

METHODS AND COMPOSITIONS FOR INHIBITING MISMATCH REPAIR

#350
20250297247
2025-09-25

MUC5AC-TARGETED ANTISENSE OLIGONUCLEOTIDES AND RELATED METHODS FOR MODULATING MUCIN EXPRESSION

#351
20250297024
2025-09-25

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES

#352
20250296946
2025-09-25

NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF

#353
20250295806
2025-09-25

IMMUNOSTIMULATORY NANOPARTICLE

#354
20250295805
2025-09-25

COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS

#355
20250295692
2025-09-25

ISOLATION OF ANTI-INFLAMMATORY NEUTROPHIL OR MONOCYTE SUBSET AND USE IN TREATING CARDIOVASCULAR DISEASES

#356
20250295688
2025-09-25

COMPOSITIONS AND METHODS OF MODULATING XANTHINE DEHYDROGENASE

#357
20250290077
2025-09-18

USE OF ANTISENSE OLIGONUCLEOTIDE IN PREPARATION OF DRUG FOR TREATING DISEASE CAUSED BY ABNORMAL THYROID

#358
20250290076
2025-09-18

EPICARDIAL CELL REGENERATION PROMOTER AND METHOD FOR PROMOTING EPICARDIAL CELL REGENERATION

#359
20250290075
2025-09-18

VARIANT RNAi

#360
20250290071
2025-09-18

STAT3 TARGETING OLIGONUCLEOTIDES AND USES THEREOF

#361
20250288604
2025-09-18

SUGAR-CONJUGATED LIPID NANOPARTICLES FOR TARGETED DELIVERY OF SIRNA TO HEPATOCYTES

#362
20250283112
2025-09-11

Compositions and Methods for RNA Editing

#363
20250283093
2025-09-11

COMPOSITIONS AND METHODS FOR TREATING RETINAL DISEASES

#364
20250283085
2025-09-11

Oligonucleotide Terminal Phosphate Derivatives and Method of Use

#365
20250283079
2025-09-11

ACTIN-BINDING LIM PROTEIN 3 (ABLIM3) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF

#366
20250283078
2025-09-11

RNA COMPOSITIONS AND THERAPEUTIC METHODS THEREOF

#367
20250283076
2025-09-11

TREATMENT OF CARDIOVASCULAR DISEASE

#368
20250282740
2025-09-11

COMPOSITIONS FOR TREATING AND/OR PREVENTING CELL OR TISSUE NECROSIS SPECIFICALLY TARGETING CATHEPSIN C AND/OR CELA1 AND/OR CELA3A AND/OR STRUCTURALLY RELATED ENZYMES THERETO

#369
20250281622
2025-09-11

FN3 DOMAIN-siRNA CONJUGATES AND USES THEREOF

#370
20250281422
2025-09-11

CATIONIC LIPIDS CONTAINING SILICON

#371
20250277221
2025-09-04

OLIGONUCLEOTIDES FOR PRNP MODULATION

#372
20250277218
2025-09-04

METHODS AND COMPOSITIONS FOR TREATING A PROPROTEIN CONVERTASE SUBTILISIN KEXIN (PCSK9) GENE-ASSOCIATED DISORDER

#373
20250277216
2025-09-04

Allele-Specific Silencing of Transforming Growth Factor Beta Induced Gene with R124H Mutation Using Short Interfering RNA

#374
20250277211
2025-09-04

LPA inhibitors and uses thereof

#375
20250276089
2025-09-04

CO-DELIVERY OF INHIBITORY NUCLEIC ACIDS AND GENOME EDITORS FOR TUMOR THERAPY

#376
20250276073
2025-09-04

BICYCLIC PEPTIDE LIGANDS SPECIFIC FOR TRANSFERRIN RECEPTOR 1 (TfR1)

#377
20250276001
2025-09-04

SERUM AMYLOID P COMPONENT (APCS) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#378
20250275931
2025-09-04

TOPICAL PATCH COMPOSITION FOR TARGETED SIRNA NANOPLEX DELIVERY AND GENE THERAPIES AND METHOD OF MAKING AND USE THEREOF

#379
20250275921
2025-09-04

COMPOSITION FOR PREVENTING OR TREATING CANCER, CONTAINING LIPID NANOPARTICLES

#380
20250270661
2025-08-28

NOVEL FISH TOTIVIRUS

#381
20250270583
2025-08-28

Methods for Suppression of Gene Silencing in Plants

#382
20250270562
2025-08-28

BIS-RNAI COMPOUNDS FOR CNS DELIVERY

#383
20250270560
2025-08-28

ANTI-CANCER AGENTS

#384
20250270558
2025-08-28

CIRCRNAS FOR GENE SILENCING

#385
20250270555
2025-08-28

ORGANIC COMPOSITIONS TO TREAT BETA-CATENIN-RELATED DISEASES

#386
20250270549
2025-08-28

MSI2 AS A THERAPEUTIC TARGET FOR THE TREATMENT OF MYOTONIC DYSTROPHY

#387
20250270169
2025-08-28

CATIONIC SULFONAMIDE AMINO LIPIDS AND AMPHIPHILIC ZWITTERIONIC AMINO LIPIDS

#388
20250269053
2025-08-28

LIPID NANOPARTICLES COMPRISING MANNOSE OR USES THEREOF

#389
20250269038
2025-08-28

Olfactory Delivery Scaffolds Using Antisense Oligonucleotides and Methods for Making and Using Same

#390
20250263792
2025-08-21

METHODS FOR THE IDENTIFICATION AND TREATMENT OF SEVERE FORMS OF COVID-19

#391
20250263705
2025-08-21

PHARMACEUTICAL COMBINATIONS FOR TREATMENT OF HBV

#392
20250263704
2025-08-21

NUCLEIC ACID-POLYPEPTIDE NANO-PHARMACEUTICAL COMPOSTION FOR TREATING AND PREVENTING HUMAN PAPILLOMA VIRUS INFECTION

#393
20250263702
2025-08-21

RNAI AGENTS TARGETING CIDEB AND RELATED METHODS

#394
20250263701
2025-08-21

COMPOSITIONS AND METHODS FOR MODULATING APOC3 EXPRESSION

#395
20250263700
2025-08-21

METHOD OF TREATING, AMELIORATING AND/OR PREVENTING POLYCYSTIC KIDNEY DISEASE

#396
20250263699
2025-08-21

COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH siRNAS TARGETING TBX3

#397
20250263697
2025-08-21

COMPOSITIONS AND METHODS OF MODULATING RNA AND PROTEIN INTERACTIONS

#398
20250262158
2025-08-21

NANO-IN-MICRO ENCAPSULATED siRNA DRY POWDER, METHOD FOR PRODUCING THE SAME AND USE OF A POWDER FORMULATION

#399
20250257361
2025-08-14

COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH SIRNAS TARGETING SMYD2

#400
20250257359
2025-08-14

MUSK-TARGETING OLIGONUCLEOTIDES

#401
20250257358
2025-08-14

KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#402
20250257357
2025-08-14

TREATMENT OF H3.3-MUTANT BRAIN CANCER WITH PNKP INHIBITORS

#403
20250257356
2025-08-14

COMPOSITION AND METHOD FOR INHIBITING EXPRESSION OF PROTEIN LPA(APO(A))

#404
20250257353
2025-08-14

SIGNAL ACTIVATABLE NUCLEIC ACID COMPLEXES

#405
20250255913
2025-08-14

NON-HALLUCINOGENIC PSYCHEDELIC FUNGI

#406
20250251401
2025-08-07

MARKERS SELECTIVELY DEREGULATED IN TUMOR-INFILTRATING REGULATORY T CELLS

#407
20250250576
2025-08-07

METHODS AND COMPOSITIONS FOR TREATING ATHEROSCLEROSIS

#408
20250250574
2025-08-07

SIRNA OR SALT THEREOF AND MEDICAMENT FOR INHIBITING EXPRESSION OF TMPRSS6 GENE, AND USE THEREOF

#409
20250250573
2025-08-07

POLYNUCLEIC ACID MOLECULES FOR INHIBITING EXPRESSION OF FXI, PHARMACEUTICAL COMPOSITIONS, AND USES THEREOF

#410
20250250572
2025-08-07

XANTHINE DEHYDROGENASE (XDH) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#411
20250250571
2025-08-07

DOUBLE-STRANDED RNA MOLECULE FOR ADMINISTRATION TO THE EYE

#412
20250250568
2025-08-07

MODIFIED OLIGONUCLEOTIDES

#413
20250249119
2025-08-07

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES

#414
20250249118
2025-08-07

SARM1 RNAi AGENTS

#415
20250249110
2025-08-07

ANTIMICROBIAL PEPTIDE DERIVATIVE AND USE THEREOF

#416
20250248939
2025-08-07

LIPID NANOPARTICLES, NUCLEIC ACIDS, AND METHODS OF USE

#417
20250248379
2025-08-07

piRNA-BASED CONSTRUCTS FOR REGULATING GENE EXPRESSION AND METHODS OF USE THEREOF

#418
20250243492
2025-07-31

COMPOSITIONS AND METHODS FOR TREATMENT OF PRION DISEASES

#419
20250243491
2025-07-31

PNPLA3-TARGETING SHORT INTERFERING RNA (SIRNA) MOLECULES AND USES THEREOF

#420
20250243490
2025-07-31

UNIVERSAL NON-TARGETING SIRNA COMPOSITIONS AND METHODS OF USE THEREOF

#421
20250243486
2025-07-31

COMPOSITIONS AND METHODS FOR INHIBITING STAG1 EXPRESSION AND USES THEREOF

#422
20250243485
2025-07-31

Targeting Ligands For Therapeutic Compounds

#423
20250243285
2025-07-31

CAR-EXPRESSING CELLS AGAINST MULTIPLE TUMOR ANTIGENS AND USES THEREOF

#424
20250242035
2025-07-31

GLYCAN CONJUGATE COMPOSITIONS AND METHODS

#425
20250241858
2025-07-31

METHOD OF DELIVERY OF DNA OR RNA CARGO USING UNSHIELDED LIPID NANOPARTICLES AND COMPOSITIONS THEREOF

#426
20250237666
2025-07-24

POLY-GA PROTEINS IN ALZHEIMER’S DISEASE

#427
20250236873
2025-07-24

Methods Of Treating Decreased Bone Mineral Density With Cluster Of Differentiation 109 (CD109) Inhibitors

#428
20250236871
2025-07-24

MULTI-TARGETED SINGLE ENTITY CONJUGATES

#429
20250236868
2025-07-24

COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH SIRNAS TARGETING CIDEB

#430
20250235554
2025-07-24

METHODS FOR IMPROVING ADENO-ASSOCIATED VIRUS (AAV) DELIVERY

#431
20250235470
2025-07-24

Methods and Compositions for Inhibiting the Growth and/or proliferation of MYC-Driven Tumor Cells

#432
20250232838
2025-07-17

METHODS AND SYSTEMS FOR IDENTIFYING AND VALIDATING A GENE COMBINATION ASSOCIATED WITH A TRAIT AND USES THEREOF

#433
20250230444
2025-07-17

Use of Trinucleotide Repeat RNAs To Treat Cancer

#434
20250230443
2025-07-17

PRODUCTS AND METHODS FOR INHIBITION OF EXPRESSION OF DYNAMIN-1 VARIANTS

#435
20250230441
2025-07-17

Nucleic acids for inhibiting expression of MASP-2 in a cell

#436
20250230439
2025-07-17

Methods For The Treatment Of ANGPTL3-Related Diseases And Disorders

#437
20250229008
2025-07-17

DELIVERY OF HYDROPHOBIC ACTIVE AGENT PARTICLES

#438
20250228898
2025-07-17

METHODS AND COMPOSITIONS FOR NON-MYELOABLATIVE BONE MARROW RECONSTITUTION

#439
20250228895
2025-07-17

COMPOUNDS TO INHIBIT YTHDF2, T HELPER CELLS LACKING EXPRESSION OF YTHDF2, AND METHODS TO TREAT CANCER

#440
20250228886
2025-07-17

COMPOSITIONS AND METHODS FOR TREATMENT OF SEPSIS-RELATED DISORDERS

#441
20250228885
2025-07-17

COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH SIRNAS TARGETING GPAM

#442
20250228883
2025-07-17

Process to Inhibit or Eliminate Eosinophilic Diseases of the Airway and Related Conditions

#443
20250228826
2025-07-17

COMBINATION OF A GREMLIN-1 ANTAGONIST WITH AN INHIBITOR OF RAS-RAF-MEK-ERK SIGNALLING

#444
20250228788
2025-07-17

COMPOSITIONS AND METHODS FOR ORGAN SPECIFIC DELIVERY OF NUCLEIC ACIDS

#445
20250223599
2025-07-10

PREPARATION AND ANTI-TUMOR APPLICATION OF GENE THERAPY VECTOR INTERFERING CKLF-LIKE MARVEL TRANSMEMBRANE DOMAIN-CONTAINING PROTEIN 6 (CMTM6) EXPRESSION

#446
20250223597
2025-07-10

LIPID CONJUGATES FOR THE DELIVERY OF THERAPEUTIC AGENTS TO CNS TISSUE

#447
20250223596
2025-07-10

ANTISENSE NUCLEIC ACID CAPABLE OF INHIBITING BIOSYNTHESIS OF CHONDROITIN SULFATE

#448
20250223595
2025-07-10

METHOD FOR CONSTRUCTING GENE NETWORK THROUGH SINGLE-CELL TRANSCRIPTOME AND METHOD FOR DISCOVERING KEY GENE IN DIFFERENTIATION USING SAME

#449
20250223594
2025-07-10

MODIFIED DOUBLE-STRANDED OLIGONUCLEOTIDE MOLECULE, MODIFIED DOUBLE-STRANDED OLIGONUCLEOTIDE CONJUGATE, AND USE THEREOF

#450
20250223590
2025-07-10

Nucleic acid regulation of ApoE

#451
20250223588
2025-07-10

OLIGONUCLEOTIDES WITH 2'-DEOXY-2'-F-2'-C-METHYL NUCLEOTIDES

#452
20250222103
2025-07-10

IMMUNE CELLS WITH COMBINATION GENE PERTURBATIONS

#453
20250221953
2025-07-10

TRANS-VACCENIC ACID (TVA) AND DERIVATIVES THEREOF IN T CELL-BASED CANCER THERAPIES

#454
20250215438
2025-07-03

IMMUNE CELLS HAVING CO-EXPRESSED TGFBR SHRNAS

#455
20250215437
2025-07-03

COMPOSITIONS AND METHODS FOR TREATMENT OF DOMINANT RETINITIS PIGMENTOSA

#456
20250215435
2025-07-03

ANTI-HELICASE THERAPY FOR TREATMENT OF REPEAT EXPANSION DISEASE

#457
20250215434
2025-07-03

COMPOSITION FOR PREVENTION OR TREATMENT OF CANCER COMPRISING DDX54 INHIBITOR AND CANCER IMMUNOTHERAPY AGENT

#458
20250215433
2025-07-03

RNAi Agents for Inhibiting Expression of Complement Factor B (CFB), Pharmaceutical Compositions Thereof, and Methods of Use

#459
20250215432
2025-07-03

BRANCHED TRIPLE LIPID-MODIFIED NUCLEIC ACID COMPOUNDS

#460
20250213731
2025-07-03

TREATING METASTATIC CANCER AND MODEL SYSTEMS FOR METASTATIC DISEASE

#461
20250213698
2025-07-03

BICYCLIC HETEROCYCLES AND THEIR LIGANDS FOR TARGETED DELIVERY OF THERAPEUTIC AGENTS

#462
20250213681
2025-07-03

NOVEL APPROACH FOR TREATMENT OF CANCER USING IMMUNOMODULATION

#463
20250207139
2025-06-26

RNAi Agents for Inhibiting Expression of Activin Receptor-Like Kinase 7 (ALK7), Compositions Thereof, and Methods of Use

#464
20250207138
2025-06-26

RNAI CONSTRUCTS FOR INHIBITING PNPLA3 EXPRESSION AND METHODS OF USE THEREOF

#465
20250207137
2025-06-26

AMPHIREGULIN GENE-SPECIFIC DOUBLE-STRANDED OLIGONUCLEOTIDE AND COMPOSITION FOR PREVENTING AND TREATING FIBROSIS-RELATED DISEASES AND RESPIRATORY DISEASES, COMPRISING SAME

#466
20250207134
2025-06-26

Use of Non-Coding Nucleic Acid for Crop Improvement and Protection Against Microbes

#467
20250207132
2025-06-26

ASYMMETRIC RNA MOLECULES

#468
20250207131
2025-06-26

MODIFIED RNA AGENTS WITH REDUCED OFF-TARGET EFFECT

#469
20250207129
2025-06-26

METHODS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS

#470
20250207128
2025-06-26

POLYNUCLEOTIDE AGENTS TARGETING COMPLEMENT COMPONENT C5 AND METHODS OF USE THEREOF

#471
20250206825
2025-06-26

COMPOSITION FOR PREVENTING OR TREATING MYOCARDITIS, COMPRISING VLA-4 INHIBITOR

#472
20250206786
2025-06-26

CRY PROTEIN CRYSTALS AND METHODS OF USE

#473
20250205362
2025-06-26

LIPID NANOPARTICLES

#474
20250205352
2025-06-26

COMPOSITIONS AND METHODS FOR MODULATING NaV1.8

#475
20250205272
2025-06-26

MODIFIED RNA AGENTS WITH REDUCED OFF-TARGET EFFECT

#476
20250197866
2025-06-19

Treatment Of Liver Disease With Mitochondrial Glycerol-3-Phosphate Acyltransferase (GPAM) Inhibitors

#477
20250197865
2025-06-19

PHARMACEUTICAL COMPOSITION FOR TREATMENT OR PREVENTION OF FIBROTIC DISEASE

#478
20250197864
2025-06-19

LNCRNA TRANSCRIPTS IN MELANOMAGENESIS

#479
20250197863
2025-06-19

GALNAC COMPOSITIONS FOR IMPROVING SIRNA BIOAVAILABILITY

#480
20250197861
2025-06-19

COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION OF ALPHA-1 ANTITRYPSIN

#481
20250197859
2025-06-19

COMPOSITIONS AND METHODS FOR THE TREATMENT OF ANGIOPOIETIN LIKE 7 (ANGPTL7) RELATED DISEASES

#482
20250197858
2025-06-19

RNAi Agents of Modulating PLP1

#483
20250197853
2025-06-19

SIRNA TARGETING ANGIOTENSINOGEN AND PHARMACEUTICAL USE OF SIRNA

#484
20250197852
2025-06-19

LIPID NANOPARTICLES USED TO TRANSPORT NUCLEIC ACIDS INTO LYMPHATIC ENDOTHELIUM CELLS

#485
20250197805
2025-06-19

COMPOSITIONS AND METHODS FOR IMPROVING PERSISTENCE OF CELLS FOR ADOPTIVE TRANSFER

#486
20250195694
2025-06-19

METHODS AND COMPOSITIONS FOR TREATING TNNT2 RELATED CARDIOMYOPATHY WITH A VIRAL VECTOR

#487
20250195676
2025-06-19

COMPOSITIONS AND METHODS OF TREATING MUSCLE ATROPHY AND MYOTONIC DYSTROPHY

#488
20250195667
2025-06-19

PHOSPHORODIAMIDATE MORPHOLINO OLIGOMER CONJUGATES

#489
20250195641
2025-06-19

IMMUNOTHERAPEUTIC CONSTRUCTS AND METHODS OF THEIR USE

#490
20250195577
2025-06-19

GENE-REGULATING COMPOSITIONS AND METHODS FOR IMPROVED IMMUNOTHERAPY

#491
20250195514
2025-06-19

METHODS OF TREATING CHOLANGIOCARCINOMA

#492
20250195430
2025-06-19

LIPID PARTICLE, COMPOSITION CONTAINING LIPID PARTICLE, KIT CONTAINING LIPID PARTICLE, AND ACTIVE AGENT DELIVERY METHOD USING LIPID PARTICLE

#493
20250194603
2025-06-19

COMPOSITIONS AND METHODS FOR MANAGEMENT OF WHITEFLY

#494
20250191692
2025-06-12

METHODS OF DESIGNING CONDITIONAL-ACTIVATABLE SMALL INTERFERING RNA SENSORS

#495
20250189515
2025-06-12

METHODS FOR IDENTIFYING THERAPEUTIC AGENTS

#496
20250188478
2025-06-12

siRNA SUPPRESSING EXPRESSION OF TRANSFERRIN RECEPTOR 2

#497
20250188477
2025-06-12

CHEMICALLY MODIFIED OLIGONUCLEOTIDE HAVING RNAi ACTIVITY

#498
20250188476
2025-06-12

COMPOUNDS AND METHODS FOR REDUCING IFNAR1 EXPRESSION

#499
20250188475
2025-06-12

KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#500
20250188474
2025-06-12

TREATMENT AND DIAGNOSIS OF INFLAMMATORY DISORDERS

#501
20250188473
2025-06-12

Methods Of Treating Liver Diseases With Phosphodiesterase 3B (PDE3B) Inhibitors

#502
20250188472
2025-06-12

SARM1 RNA INTERFERENCE AGENTS

#503
20250188471
2025-06-12

NONCOVALENTLY BRANCHED OLIGONUCLEOTIDE COMPOSITIONS

#504
20250188465
2025-06-12

POLYNUCLEIC ACID MOLECULES TARGETING APOC3 AND USES THEREOF

#505
20250188464
2025-06-12

POLYNUCLEIC ACID MOLECULES FOR INHIBITING EXPRESSION OF LP(A), PHARMACEUTICAL COMPOSITIONS, AND USES THEREOF

#506
20250188458
2025-06-12

FULLY STABILIZED ASYMMETRIC SIRNA

#507
20250188456
2025-06-12

HIGH MOBILITY GROUP BOX-1 (HMGB1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#508
20250188455
2025-06-12

LIPOPHILIC OLIGONUCLEOTIDE CONJUGATES

#509
20250188454
2025-06-12

SIGNAL ACTIVATABLE NUCLEIC ACID CONSTRUCTS WITH WOBBLE BASE PAIRINGS

#510
20250188453
2025-06-12

CONDITIONALLY ACTIVATABLE NUCLEIC ACID COMPLEXES

#511
20250188149
2025-06-12

ENHANCING ESTROGEN RECEPTOR ALPHA IN OSTEOARTHRITIS

#512
20250186605
2025-06-12

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES

#513
20250186599
2025-06-12

BLOCK COPOLYMERS

#514
20250186480
2025-06-12

Treatment Methods for Fibrosis Targeting SMOC2

#515
20250186439
2025-06-12

PYK2 INHIBITION MODULATES IMMUNE CELL FUNCTION

#516
20250179502
2025-06-05

TARGETING NEUROPILIN 2 (NRP2) IN LETHAL PROSTATE CANCER

#517
20250179499
2025-06-05

USE OF CDK16 AS TARGET IN PREPARATION OF MEDICINE FOR TREATING TRIPLE-NEGATIVE BREAST CANCER

#518
20250179498
2025-06-05

RNAI AGENT TARGETING MARC1 GENE, AND USE THEREOF

#519
20250179497
2025-06-05

USE OF DINUCLEOTIDE REPEAT RNAS TO TREAT CANCER

#520
20250179496
2025-06-05

TARGETED COMPOSITIONS

#521
20250179491
2025-06-05

ATXN2 RNA INTERFERENCE AGENTS

#522
20250179489
2025-06-05

SYSTEMS

#523
20250179167
2025-06-05

IL-6 INHIBITOR AS TREATMENT FOR NEPHROPATHY

#524
20250177549
2025-06-05

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES

#525
20250177478
2025-06-05

G ALPHA Q/11 INHIBITORS FOR USE AS AN ANALGESIC

#526
20250177377
2025-06-05

TARGETING PTCHD1 AND NEURONAL CHOLESTEROL TO ENHANCE SAFETY OF OPIOID ANALGESICS

#527
20250171821
2025-05-29

HIF-1 ACTIVATORS AND USES THEREOF

#528
20250171786
2025-05-29

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE SIGNAL REGULATORY PROTEIN ALPHA (SIRPa) GENE

#529
20250171785
2025-05-29

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE PCSK9 GENE

#530
20250171784
2025-05-29

APPLICATION OF MECHANICAL-FORCE SENSITIVE MACROPHAGE SUBSET IN PANCREATIC CANCER DIAGNOSIS OR PROGNOSIS EVALUATION

#531
20250171777
2025-05-29

Microtubule Associated Protein Tau (MAPT) iRNA Agent Compositions and Methods of Use Thereof

#532
20250171765
2025-05-29

METHODS OF PREPARING HIGH CONCENTRATION LIQUID DRUG SUBSTANCES

#533
20250171544
2025-05-29

NUCLEIC ACID-POLYPEPTIDE COMPOSITIONS AND USES THEREOF

#534
20250170274
2025-05-29

GENE THERAPEUTICS FOR TREATING BONE DISORDERS

#535
20250170261
2025-05-29

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES

#536
20250170161
2025-05-29

INHIBIN SUBUNIT BETA E INHIBITOR AND METHODS OF USE THEREOF

#537
20250170071
2025-05-29

ULTRASOUND RESPONSIVE LIPID NANOPARTICLE CARRYING GENES AND CELL MEMBRANE, ITS PREPARATION METHOD AND APPLICATION

#538
20250163431
2025-05-22

SIRNA SPECIFICALLY BINDING TO M2 MACROPHAGE CD206 AND APPLICATION THEREOF

#539
20250163430
2025-05-22

METHOD FOR TREATING TUBULAR AGGREGATE MYOPATHY AND STORMORKEN SYNDROME

#540
20250163420
2025-05-22

Promotion of Cardiomyocyte Proliferation and Regenerative Treatment of the Heart by Inhibition of microRNA-128

#541
20250163418
2025-05-22

Brush polymer-oligonucleotide conjugates for the treatment of muscular dystrophy

#542
20250163417
2025-05-22

COMPOSITIONS AND METHODS FOR IMPROVING STRAND BIASED

#543
20250163415
2025-05-22

Therapeutic Inhibition of LPA Expression

#544
20250162978
2025-05-22

CATIONIC LIPIDS FOR NUCLEIC ACID DELIVERY AND PREPARATION THEREOF

#545
20250161414
2025-05-22

METHOD FOR IMPROVING AUDITORY PERCEPTION USING A VIPR1 INHIBITOR

#546
20250161398
2025-05-22

DESIGN AND DEVELOPMENT OF A NOVEL MESSENGER RNA THERAPEUTIC TO TREAT ATHEROSCLEROSIS

#547
20250160307
2025-05-22

BRAIN TUMOR MODEL

#548
20250154512
2025-05-15

RNAI CONSTRUCTS FOR INHIBITING PNPLA3 EXPRESSION AND METHODS OF USE THEREOF

#549
20250154511
2025-05-15

Products and Methods for Treatment of Amyotrophic Lateral Sclerosis

#550
20250154506
2025-05-15

LINKAGE MODIFIED OLIGOMERIC COMPOUNDS AND USES THEREOF

#551
20250154460
2025-05-15

GENETICALLY-MODIFIED IMMUNE CELLS COMPRISING A MICRORNA-ADAPTED SHRNA (SHRNAMIR)

#552
20250152727
2025-05-15

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES

#553
20250152513
2025-05-15

METHOD FOR PREPARING LIPOSOMES

#554
20250146024
2025-05-08

Methods and Compositions for RNA-Directed Target DNA Modification and For RNA-Directed Modulation of Transcription

#555
20250146001
2025-05-08

Compositions and Methods for Enhancing AAV Therapy and Decreasing Tropism of AAV to the Liver

#556
20250146000
2025-05-08

COMPOSITIONS AND METHODS OF TREATING AMYOTROPHIC LATERAL SCLEROSIS (ALS)

#557
20250145999
2025-05-08

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF PREKALLIKREIN (PKK) PROTEIN

#558
20250145992
2025-05-08

OLIGONUCLEOTIDES WITH ETHYLENE GLYCOL MODIFICATION

#559
20250145702
2025-05-08

EGFL6 SPECIFIC MONOCLONAL ANTIBODIES AND METHODS OF THEIR USE

#560
20250136996
2025-05-01

TREATMENT OF SMOKING WITH CHOLINERGIC RECEPTOR NICOTINIC BETA 3 SUBUNIT (CHRNB3) INHIBITORS

#561
20250136992
2025-05-01

ANTI-PTEN RNA INTERFERENCE OLIGONUCLEOTIDES AND USES THEREOF

#562
20250136990
2025-05-01

ANTISENSE OLIGONUCLEOTIDES TARGETING ADENOSINE KINASE

#563
20250136981
2025-05-01

COMPOSITIONS AND METHODS COMPRISING ENGINEERED SHORT NUCLEAR RNA (SNRNA)

#564
20250136978
2025-05-01

iRNA Compositions and Methods for Silencing ANGPTL4

#565
20250136977
2025-05-01

NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF COMPLEMENT FACTOR B (CFB) IN A CELL

#566
20250136976
2025-05-01

USE OF ETV3 OR ETV6 INHIBITORS FOR BLOCKING THE DIFFERENTIATION OF MONOCYTES INTO DENDRITIC CELLS

#567
20250136936
2025-05-01

NUCLEIC ACID MODIFIED BIOLOGICAL CELL WITH EXPANSION-DEPENDENT GENE EXPRESSION

#568
20250135036
2025-05-01

COMPOSITIONS FOR EDITING MECP2 TRANSCRIPTS AND METHODS THEREOF

#569
20250134920
2025-05-01

Treatment Of Myeloid Cell Dysfunction With Membrane Spanning 4-Domains A6A (MS4A6A) Inhibitors

#570
20250130219
2025-04-24

COMPOSITION FOR PREVENTING OR TREATING CANCER COMPRISING MSH2 OR MSH6 INHIBITOR AS ACTIVE INGREDIENT

#571
20250129386
2025-04-24

NANOPARTICLE VECTOR FOR RNA SELF-DELIVERY, AND PREPARATION METHOD THEREFOR AND USE THEREOF

#572
20250129372
2025-04-24

Treatment Of Osteoarthritis With Procollagen Galactosyl Transferase 2 (COLGALT2) Inhibitors

#573
20250129371
2025-04-24

Treatment Of Macular Degeneration With Complement Factor D (CFD) Inhibitors

#574
20250129368
2025-04-24

siRNA based on RNA sequence of SARS-CoV-2 and use thereof

#575
20250129366
2025-04-24

Treatment Of Liver Disease Or Metabolic Disorder With Folliculin Interacting Protein 1 (FNIP1) Inhibitors And/Or Folliculin (FLCN) Inhibitors

#576
20250129170
2025-04-24

EPO RECEPTOR AGONISTS AND ANTAGONISTS

#577
20250129147
2025-04-24

EPO RECEPTOR AGONISTS AND ANTAGONISTS

#578
20250129137
2025-04-24

CD71 BINDING FIBRONECTIN TYPE III DOMAINS

#579
20250127917
2025-04-24

COMPOSITIONS AND METHODS FOR TREATING CANCERS

#580
20250127886
2025-04-24

ASSESSMENT AND TREATMENT OF CHRONIC HEPATITIS B

#581
20250127811
2025-04-24

MODULATION OF TGF BETA SIGNALING IN GENETICALLY-MODIFIED EUKARYOTIC CELLS

#582
20250127719
2025-04-24

ANISAMIDE-CONTAINING LIPIDS AND COMPOSITIONS AND METHODS OF USE THEREOF

#583
20250122537
2025-04-17

Methods and Compositions for RNA-Directed Target DNA Modification and for RNA-Directed Modulation of Transcription

#584
20250122507
2025-04-17

DEPLETION OF FNDC5 REDUCES CANCER INDUCED MUSCLE LOSS/CACHEXIA

#585
20250122506
2025-04-17

Modulation of TJPI Expression to Treat Liver Diseases

#586
20250122505
2025-04-17

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE

#587
20250122503
2025-04-17

THERAPEUTIC SUPPRESSOR TRNA TO TREAT GENETIC DISEASES

#588
20250122501
2025-04-17

ANTIVIRAL HAIRPIN CONSTRUCTS AND METHODS OF USE THEREOF

#589
20250121051
2025-04-17

HIV PRE-IMMUNIZATION AND IMMUNOTHERAPY

#590
20250121050
2025-04-17

METHODS OF PRODUCING CELLS RESISTANT TO HIV INFECTION

#591
20250120914
2025-04-17

LIPID NANOPARTICLES

#592
20250115918
2025-04-10

Treatment Of Uveitis With Endoplasmic Reticulum Aminopeptidase 1 (ERAP1) Inhibitors

#593
20250115917
2025-04-10

MODULATORY POLYNUCLEOTIDES

#594
20250115916
2025-04-10

MODULATION OF SUV39H1 EXPRESSION BY RNAS

#595
20250115912
2025-04-10

METHOD FOR THE DIAGNOSIS, PROGNOSIS AND TREATMENT OF CANCER METASTASIS

#596
20250115907
2025-04-10

COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION OF LPA

#597
20250114478
2025-04-10

LIPID NANOPARTICLE (LNP) COMPOSITIONS FOR BRAIN-SELECTIVE CARGO DELIVERY, AND METHODS OF USE THEREOF

#598
20250114470
2025-04-10

THERAPY FOR POLYCYSTIC KIDNEY DISEASE

#599
20250114306
2025-04-10

METHOD OF DELIVERY OF DNA OR RNA CARGO USING UNSHIELDED LIPID NANOPARTICLES AND COMPOSITIONS THEREOF

#600
20250113829
2025-04-10

HIGH MOLECULAR WEIGHT MODIFIED RNA COMPOSITIONS