ClassID:

109145

C12N2310/14 - CPC Classification

Classification description:

Structure or type of the nucleic acid; Type of nucleic acid interfering N.A.

Sub-classes:
Recent Application in this class:
#1
20260159899
2026-06-11

COMPOSITIONS, METHODS AND KITS FOR CHARACTERIZING AND SCREENING FOR SMALL CELL OVARIAN CARCINOMA

#2
20260159845
2026-06-11

INHIBITION OF SMOOTH MUSCLE CELL CONTRACTION BY ALTERING INTERLEUKIN 31 RECEPTOR ALPHA LEVELS

#3
20260159842
2026-06-11

VIRAL VECTOR MEDIATED GENE THERAPY TRANSDUCTION AND SAFETY OR PROMOTING VIRAL CLEARANCE AND/OR INHIBITING VIRAL INFECTIVITY BY TARGETING CLASS B SCAVENGER RECEPTORS

#4
20260159840
2026-06-11

METHODS OF TREATING IMPAIRED GLUCOCORTICOID SIGNALLING IN UTERINE DISORDERS

#5
20260159837
2026-06-11

CORONAVIRUS IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#6
20260159836
2026-06-11

OLIGONUCLEOTIDE-MEDIATED KNOCKDOWN OF PLN

#7
20260159835
2026-06-11

OLIGONUCLEOTIDE-MEDIATED KNOCKDOWN OF DUX4

#8
20260158105
2026-06-11

METHODS OF USING ZSCAN4 FOR REJUVENATING HUMAN CELLS

#9
20260152751
2026-06-04

INTERFERING RNA FOR INHIBITING JAK1 GENE EXPRESSION AND USE THEREOF

#10
20260152749
2026-06-04

ATTENUATION OF CYTOKINE RELEASE SYNDROME IN IMMUNOTHERAPY

#11
20260152747
2026-06-04

ATTENUATION OF CYTOKINE RELEASE SYNDROME IN

#12
20260152746
2026-06-04

INVERTED CHIMERIC siRNA MOLECULES AND METHODS OF USE THEREOF

#13
20260152745
2026-06-04

COMPOSITIONS AND METHODS FOR TREATMENT OF CANCER

#14
20260151513
2026-06-04

COMPOSITIONS AND METHODS FOR THE TREATMENT OF LEUKODYSTROPHY AND WHOLE ANIMAL AND CELLULAR MODELS FOR IDENTIFYING EFFICACIOUS AGENTS FOR TREATMENT OF THE SAME

#15
20260146286
2026-05-28

SMALL RNA-BASED PROGNOSTIC SIGNATURES AND THERAPEUTIC COMPOSITIONS FOR IDIOPATHIC PULMONARY FIBROSIS

#16
20260146251
2026-05-28

DOUBLE STRANDED RNAi AGENTS, COMPOSITIONS AND METHODS OF USE

#17
20260146248
2026-05-28

COMPOSITION AND METHOD FOR TREATING CANCER WITH CHROMOSOME TRANSLOCATION FUSION

#18
20260139257
2026-05-21

PLIN1 RNAi INTERFERENCE AGENTS

#19
20260139255
2026-05-21

RNAi Agent Targeting PCSK9 and Use Thereof

#20
20260139254
2026-05-21

INTERFERING RNA FOR INHIBITING TOP1 GENE EXPRESSION AND USE THEREOF

#21
20260139253
2026-05-21

ANTI-CANCER TGFB2 AGENTS WITH IMMUNOTHERAPEUTICS

#22
20260139252
2026-05-21

NANOCOMPLEX TARGETING NERVOUS NECROSIS VIRUS AS WELL AS PREPARATION METHOD AND USE THEREOF

#23
20260139251
2026-05-21

RNAi Agents for Inhibiting Expression of Mucin 5AC (MUC5AC), Compositions Thereof, and Methods of Use

#24
20260139250
2026-05-21

METHODS AND COMPOSITIONS FOR THE TREATMENT OF CANCER BY TARGETING ONCOGENIC TRANSFER RNAS

#25
20260137807
2026-05-21

COMPOSITIONS AND METHODS FOR DELIVERING A MACROMOLECULE TO A CELL

#26
20260137713
2026-05-21

POLYNUCLEOTIDES FOR SILENCING TRANSCRIPT VARIANT 1 OF ASSEMBLY FACTOR FOR SPINDLE MICROTUBULES AND APPLICATIONS THEREOF

#27
20260132406
2026-05-14

RNAi Agents for Inhibiting Expression of Activin Receptor-Like Kinase 7 (ALK7), Compositions Thereof, and Methods of Use

#28
20260132404
2026-05-14

MODIFIED OLIGONUCLEOTIDES AND DOUBLE-STRANDED RNAS

#29
20260132401
2026-05-14

RNAi AGENTS FOR MODULATING SNCA

#30
20260132400
2026-05-14

STABILIZED RNA AGENTS

#31
20260131024
2026-05-14

GENE THERAPY FOR PRADER WILLI SYNDROME

#32
20260130910
2026-05-14

METHODS OF TREATING CANCERS

#33
20260125687
2026-05-07

RNA THERAPEUTICS FOR FIBRODYSPLASIA OSSIFICANS PROGRESSIVA AND USES THEREOF

#34
20260125686
2026-05-07

COMPOSITIONS AND METHODS FOR MODULATION OF CFTR

#35
20260125685
2026-05-07

THERAPEUTIC AGENT FOR TREATING HIF-1alpha-MEDIATED DISEASES BY INHIBITING AREL1 AND RESTORING PHD2 ACTIVITY

#36
20260125683
2026-05-07

TREATMENT OF CANCERS HAVING A DRUG-RESISTANT MESENCHYMAL CELL STATE

#37
20260125682
2026-05-07

CHEMICAL MODIFICATIONS OF SMALL INTERFERING RNA WITH MINIMAL FLUORINE CONTENT

#38
20260125681
2026-05-07

DOUBLE-STRANDED RNAi AGENTS FOR TARGETING AND REGULATING HBV GENE EXPRESSION, AND A USE THEREOF

#39
20260125679
2026-05-07

FINE-TUNING INFLAMMATION BY ALTERING 3'UTR LENGTH

#40
20260124233
2026-05-07

COMPOSITIONS FOR AQUACULTURING

#41
20260117233
2026-04-30

PLATELETS TRANSFECTED WITH SIRNA AND THE THERAPEUTICS USES THEREOF

#42
20260117231
2026-04-30

COMPOSITIONS AND METHODS FOR TREATING MYOPATHY

#43
20260117224
2026-04-30

MODULATORY POLYNUCLEOTIDES

#44
20260117182
2026-04-30

SURF4 GENE KNOCKOUT ERYTHROID PROGENITOR CELLS AND METHODS OF ERYTHROID DIFFERENTIATION THEREOF

#45
20260117178
2026-04-30

MEANS TO TREAT AUTOIMMUNITY BY REFINING REGULATORY T CELLS

#46
20260116986
2026-04-30

EPO RECEPTOR AGONISTS AND ANTAGONISTS

#47
20260115325
2026-04-30

METHODS AND COMPOSITIONS FOR TREATING CORNEAL WOUNDS

#48
20260115315
2026-04-30

DRUG DELIVERY SYSTEM FOR BLOOD-BRAIN BARRIER PENETRATION

#49
20260115143
2026-04-30

POLYMER DERIVATIVES AND THEIR USE AS LIPID NANOPARTICLE MODIFIERS

#50
20260115138
2026-04-30

LIPID NANOPARTICLES

#51
20260109988
2026-04-23

COMPOSITIONS AND METHODS TO MODULATE TUMOR MICROENVIRONMENT ASSOCIATED LONG NONCODING RNAS

#52
20260109987
2026-04-23

PREPARATION AND USE OF NUCLEIC ACID WITH ANTI-HAIR LOSS AND OIL CONTROL EFFECTS AND COMPOSITION INCLUDING NUCLEIC ACID

#53
20260109984
2026-04-23

METHODS, SYSTEMS, AND COMPOSITIONS FOR TREATMENT OF HEMOGLOBINOPATHY (E.G., BETA-THALASSEMIA AND SICKLE CELL DISEASE) BY INCREASING EXPRESSION OF NONCODING RNA ACTIVATED BY DNA DAMAGE

#54
20260109983
2026-04-23

HIPPO AND DYSTROPHIN COMPLEX SIGNALING IN CARDIOMYOCYTE RENEWAL

#55
20260109982
2026-04-23

OLIGONUCLEOTIDES FOR MAPT MODULATION

#56
20260108631
2026-04-23

Methods for Preventing Cardiovascular Events Through Proprotein Convertase Subtilisin Kexin 9 (PCSK9) Reduction

#57
20260103718
2026-04-16

METHODS AND COMPOSITIONS FOR SELECTIVE REGULATION OF PROTEIN EXPRESSION

#58
20260103714
2026-04-16

ANTISENSE OLIGONUCLEOTIDES FOR THE TREATMENT OF CANAVAN DISEASE

#59
20260103709
2026-04-16

C-MYC-TARGETING CHARGE-ALTERING RELEASABLE TRANSPORTERS AS ANTI-TUMOR AGENTS FOR BREAST CANCER THERAPY

#60
20260103708
2026-04-16

NOVEL COMPOUND AND APPLICATION THEREOF

#61
20260103707
2026-04-16

NOVEL COMPOUND AND APPLICATION THEREOF

#62
20260103703
2026-04-16

siRNA COMPOSITIONS AND METHODS TARGETING ALPHA-SYNUCLEIN NUCLEIC ACIDS

#63
20260103525
2026-04-16

KLRG1 SIGNALLING THERAPY FOR INFECTIOUS DISEASE

#64
20260102500
2026-04-16

PKC INHIBITORS FOR THE TREATMENT OF SEPTIC CHOLESTASIS WITH POLYMETHINE DYE TARGETING

#65
20260102424
2026-04-16

METHODS OF ATTENUATING AN IMMUNE RESPONSE BY INHIBITION OF BFL1

#66
20260098269
2026-04-09

COMPOSITIONS AND METHODS FOR TREATMENT OF NEUROINFLAMMATORY DISEASES

#67
20260098268
2026-04-09

COMPOSITIONS AND METHODS TO TREAT ALZHEIMER'S DISEASE AND OTHER BRAIN DISEASES

#68
20260098266
2026-04-09

METHODS AND COMPOSITIONS FOR DESIGNING AND SELECTING TINYRNAS TO MAXIMIZE TARGET CLEAVAGE

#69
20260098265
2026-04-09

COMPOSITIONS AND METHODS FOR TREATMENT OF SPINOCEREBELLAR ATAXIAS

#70
20260098264
2026-04-09

COMPOSITIONS AND METHODS FOR TREATMENT OF NEUROLOGICAL DISORDERS

#71
20260098263
2026-04-09

MODIFIED DOUBLE-STRANDED RNA AGENTS

#72
20260097120
2026-04-09

INDUCTION OF STEM-LIKE ACTIVATED T CELLS

#73
20260097063
2026-04-09

ANTI-C5 ANTIBODY/C5 IRNA DOSING REGIMENS FOR TREATING C5-ASSOCIATED DISEASES

#74
20260096999
2026-04-09

RESPIRATORY SYNCYTIAL VIRUS (RSV) POLYANHYDRIDE NANOPARTICLE VACCINE

#75
20260092282
2026-04-02

DNA-RNA HETERODUPLEX TARGETING ANDROGEN RECEPTOR

#76
20260092281
2026-04-02

METHODS FOR TREATMENT OF ANEMIA

#77
20260092280
2026-04-02

NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE

#78
20260092279
2026-04-02

DOUBLE-STRANDED RNAI AGENTS AND COMPOSITIONS FOR REDUCING EXPRESSION OF ANGIOPOIETIN-LIKE 3 (ANGPTL3) AND METHODS OF USE THEREOF

#79
20260092276
2026-04-02

Carbohydrate-oligonucleotide conjugates, pharmaceutical compositions, and therapeutic applications

#80
20260092275
2026-04-02

PRODUCTS AND COMPOSITIONS

#81
20260091053
2026-04-02

TREATMENT OF THYMIC STROMAL LYMPHOPOIETIN (TSLP) RELATED DISEASES BY INHIBITION OF LONG-FORM TSLP TRANSCRIPTS

#82
20260091052
2026-04-02

MICRORNA AND USES THEREOF IN PREVENTION AND/OR TREATMENT OF FIBROPLASIA MEDICAL SIGN AND/OR SYNDROME

#83
20260085321
2026-03-26

IRON METABOLISM TARGETS FOR OBESITY

#84
20260085320
2026-03-26

GALNAC MONOMER COMPRISING RIBOSE RING OR DERIVATIVE STRUCTURE THEREOF AND USE THEREOF IN LIVER-TARGETED DELIVERY OF SMALL NUCLEIC ACID DRUGS

#85
20260085317
2026-03-26

SIRNA FOR TARGETED INHIBITION OF AGT GENE EXPRESSION AND USE THEREOF IN TREATING HYPERTENSION

#86
20260085316
2026-03-26

USE OF HOMEOBOX CONTAINING 1 (HMBOX1) INHIBITOR IN PREPARATION OF DRUG FOR PREVENTION AND/OR TREATMENT OF MUSCLE ATROPHY

#87
20260085314
2026-03-26

CONJUGATED OLIGONUCLEOTIDE COMPOUNDS, METHODS OF MAKING AND USES THEREOF

#88
20260083844
2026-03-26

DOWNREGULATING INOS TO INCREASE CAR-T KILLING

#89
20260078381
2026-03-19

Methods for Directing Lipid Nanoparticles in Vivo

#90
20260078375
2026-03-19

RNAi Agents for Inhibiting Influenza A Viral Gene Expression, Compositions Thereof, and Methods of Use

#91
20260078372
2026-03-19

NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF LPA IN A CELL

#92
20260078369
2026-03-19

Method of Inhibiting Durotaxis and/or Treating Fibrosis

#93
20260076990
2026-03-19

DSRNA, USE THEREOF AND PREPARATION METHOD THEREFOR

#94
20260071238
2026-03-12

MATERIALS AND PROCESSES FOR ENGINEERING HYPOIMMUNOGENICITY

#95
20260071223
2026-03-12

LIPID CONJUGATES FOR THE DELIVERY OF THERAPEUTIC AGENTS TO ADIPOSE TISSUE

#96
20260071220
2026-03-12

CONJUGATE OF NUCLEOTIDE ANALOG-CONTAINING DOUBLE-STRANDED RNAI ANALOG

#97
20260071219
2026-03-12

COMPOSITIONS AND METHODS FOR INHIBITING LPA EXPRESSION

#98
20260069625
2026-03-12

ORGANIC COMPOSITIONS TO TREAT KRAS-RELATED DISEASES

#99
20260069541
2026-03-12

COMPOSITIONS AND METHODS FOR THE DELIVERY OF ACTIVE AGENTS INCLUDING NUCLEIC ACIDS

#100
20260068892
2026-03-12

RNA INTERFERENCE (RNAI) FOR CONTROL OF JAPANESE BEETLE

#101
20260062709
2026-03-05

METHODS FOR IMPROVING PRODUCTION OF BIOLOGICAL PRODUCTS BY REDUCING THE LEVEL OF ENDOGENOUS PROTEIN

#102
20260062706
2026-03-05

Treatment Of Pan-Cancer Phenotype With Regulator of Telomere Elongation Helicase 1 (RTEL1) Inhibitors

#103
20260062705
2026-03-05

TREATMENT FOR OVARIAN CANCER WITH OLIGONUCLEOTIDES TARGETING FIBROBLAST ACTIVATION PROTEIN ALPHA

#104
20260062435
2026-03-05

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF

#105
20260061077
2026-03-05

METHODS AND COMPOSITIONS OF TREATING RETINAL DEGENERATIVE DISEASES

#106
20260060927
2026-03-05

LIPOSOMAL PARTICLES, METHODS OF MAKING SAME AND USES THEREOF

#107
20260060792
2026-03-05

USE OF PGAM2 IN BREEDING OF BLCATTLE BLACK CATTLE

#108
20260056201
2026-02-26

MARKERS SELECTIVELY DEREGULATED IN TUMOR-INFILTRATING REGULATORY T CELLS

#109
20260055414
2026-02-26

COMPOSITIONS AND METHODS FOR INHIBITING XDH EXPRESSION

#110
20260055413
2026-02-26

REVERSIR MOLECULES AND METHODS OF USE THEREOF

#111
20260055412
2026-02-26

SIRNA TARGETING ANGPTL4, AND CONJUGATES AND USES THEREOF

#112
20260055411
2026-02-26

EXTRACELLULAR VESICLE COMPRISING A BIOLOGICALLY ACTIVE MOLECULE AND A DUAL CLEAVABLE LINKER

#113
20260055410
2026-02-26

TREATMENT OF MST1 RELATED DISEASES AND DISORDERS

#114
20260055409
2026-02-26

COMPOUNDS AND METHODS FOR TREATING HUMAN SUBJECTS

#115
20260055407
2026-02-26

COMPOSITIONS AND METHODS FOR TREATING NONALCOHOLIC FATTY LIVER DISEASE

#116
20260055402
2026-02-26

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF

#117
20260053852
2026-02-26

NONCODING RNA AGENTS (BCYRN1 AND DERIVATIVES THEREOF) TO TREAT DISEASES OF IMMUNITY

#118
20260053839
2026-02-26

COMPOSITIONS AND METHODS FOR TREATING TRANSTHYRETIN (TTR) MEDIATED AMYLOIDOSIS

#119
20260049360
2026-02-19

Therapeutic Strategies To Reduce Thrombotic Risk In Factor V Leiden (FVL) Carriers

#120
20260049319
2026-02-19

TREM2 BINDS TO SPECIFICALLY STRUCTURED HEPARAN SULFATE

#121
20260049314
2026-02-19

ANTISENSE OLIGONUCLEOTIDE-BASED ANTI-FIBROTIC THERAPEUTICS

#122
20260049309
2026-02-19

REGULATION OF ACTIVITY OF RNAI MOLECULES

#123
20260049120
2026-02-19

EXPRESSION OF FC-CONTAINING PROTEINS

#124
20260048135
2026-02-19

COMPOSITIONS AND METHODS OF USING PRKAG2-TARGETING ANTIBODY-OLIGONUCLEOTIDE CONJUGATES

#125
20260048075
2026-02-19

Inhibition of TCF4/ITF2 in the Treatment of Cancer

#126
20260043039
2026-02-12

METHODS OF ALTERING THE STARCH GRANULE PROFILE IN PLANTS

#127
20260043031
2026-02-12

COMPOSITIONS AND METHODS FOR INHIBITING ADENYLATE CYCLASE 9 (AC9)

#128
20260043030
2026-02-12

Oligonucleotide for reducing the expression of leucine-rich repeat kinase 2 (LRRK2) and its use for preventing and/or treating human diseases

#129
20260043029
2026-02-12

RNAi Agents for Inhibiting Expression of Thymic Stromal Lymphopoietin (TSLP), Compositions Thereof, and Methods of Use

#130
20260043027
2026-02-12

LINKER, COMPOUND INCLUDING LINKER, METHOD OF PREPARING COMPOUND, USE OF LINKER, AND METHOD OF DELIVERING OLIGONUCLEOTIDES THROUGH LINKER

#131
20260043025
2026-02-12

RNAi Agents And Compositions for Inhibiting Expression of Apolipoprotein C-III (APOC3)

#132
20260042843
2026-02-12

METHODS FOR TREATING ENDOMETRIAL AND OVARIAN HYPERPROLIFERATIVE DISORDERS

#133
20260041793
2026-02-12

VIRAL VECTOR

#134
20260041702
2026-02-12

AGENTS THAT INHIBIT CCN LIGAND-INDUCED SIGNALLING FOR TREATING DISEASE

#135
20260041102
2026-02-12

SIRNA TARGETING KEY GENE OF MAGNAPORTHE ORYZAE FOR CONTROLLING RICE BLAST, AND USE THEREOF

#136
20260035702
2026-02-05

PLASMINOGEN (PLG) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#137
20260035701
2026-02-05

METHODS AND COMPOSITIONS FOR TARGETING SERINE DEHYDRATASE

#138
20260035700
2026-02-05

COMPOSITIONS AND METHODS FOR INHIBITION OF EXPRESSION OF INHIBIN SUBUNIT BETA E (INHBE) GENES

#139
20260035699
2026-02-05

OLIGONUCLEOTIDES FOR PRNP MODULATION

#140
20260035696
2026-02-05

COMBINATION TREATMENT FOR CANCER

#141
20260034213
2026-02-05

SYSTEMS AND METHODS FOR TARGETING NAD-BASED PATHWAYS FOR TREATMENT OF CANCER

#142
20260028631
2026-01-29

KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#143
20260028630
2026-01-29

HYBRID OLIGONUCLEOTIDES

#144
20260028629
2026-01-29

AGENTS FOR MODULATING EXPRESSION

#145
20260028628
2026-01-29

COMPOSITIONS AND METHODS FOR INHIBITION OF EXPRESSION OF INHIBIN SUBUNIT BETA E (INHBE) GENES

#146
20260028623
2026-01-29

RNAi AGENTS OF PRION EXPRESSION

#147
20260028375
2026-01-29

POLYPEPTIDES SELF-ASSEMBLING INTO NANOPARTICLES

#148
20260027223
2026-01-29

B CELL-SPECIFIC MAB-SIRNA CONJUGATES IMPROVE MYASTHENIA

#149
20260027146
2026-01-29

COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#150
20260022384
2026-01-22

ASPARAGINE SYNTHETASE INHIBITORS AND USES THEREOF

#151
20260022383
2026-01-22

SUBPOPULATION-DIRECTED REMEDIATION OF DISEASE-ASSOCIATED GENE PRODUCTS

#152
20260022381
2026-01-22

RNAi Agents for Inhibiting Expression of Complement Factor B (CFB), Pharmaceutical Compositions Thereof, and Methods of Use

#153
20260022380
2026-01-22

GENETIC MODULATORS OF KRAS PROTEIN EXPRESSION AND THEIR USES

#154
20260022379
2026-01-22

Optimized RNAi Agents for Inhibiting Expression of Coronavirus (CoV) Viral Genomes, Compositions Thereof, and Methods of Use

#155
20260022378
2026-01-22

PHARMACEUTICAL COMPOSITION FOR PREVENTING OR TREATING CANCER COMPRISING SIRNA AS ACTIVE INGREDIENT

#156
20260022377
2026-01-22

POLYNUCLEOTIDE COMPOSITIONS AND METHODS FOR TREATMENT OF NEURODEGENERATIVE DISEASES

#157
20260022376
2026-01-22

TAU-SEED INTERACTOR INHIBTORS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS

#158
20260022375
2026-01-22

METHODS AND COMPOSITIONS FOR SELECTIVELY MODULATING GENE EXPRESSION IN MEGAKARYOCYTES AND PLATELETS

#159
20260021315
2026-01-22

METHODS FOR TREATING GLIOBLASTOMA OR RECURRENT GLIOBLASTOMA UTILIZING A WIRELESS SIGNAL ALONE OR IN COMBINATION WITH ONE OR MORE CANCER DRUGS, AND ASSOCIATED SYSTEMS, APPARATUSES, AND DEVICES

#160
20260021188
2026-01-22

1'-ALKYL MODIFIED RIBOSE DERIVATIVES AND METHODS OF USE

#161
20260021046
2026-01-22

LIPID NANOPARTICLE AND PHARMACEUTICAL COMPOSITION

#162
20260015617
2026-01-15

DOUBLE STRANDED RNAi AGENTS, COMPOSITIONS AND METHODS OF USE

#163
20260015615
2026-01-15

SPERMATOGENESIS ALTERATION

#164
20260015613
2026-01-15

FACTOR XII (HAGEMAN FACTOR) (F12), KALLIKREIN B, PLASMA (FLETCHER FACTOR) 1 (KLKB1), AND KININOGEN 1 (KNG1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF

#165
20260015612
2026-01-15

NOVEL STAPLE NUCLEIC ACID

#166
20260014266
2026-01-15

COMPOSITIONS AND METHODS OF TREATING MUSCLE DYSTROPHY

#167
20260013515
2026-01-15

RNA-BASED CONTROL OF PRODUCTION OF DEOXYNIVALENOL BY FUSARIUM

#168
20260009037
2026-01-08

RNAi Agents for Inhibiting Expression of Mitochondrial Amidoxime Reducing Component 1 (MARC1), Pharmaceutical Compositions Thereof, and Methods of Use

#169
20260009036
2026-01-08

INHIBITORS OF EXPRESSION AND/OR FUNCTION

#170
20260009035
2026-01-08

GALNAC COMPOUND CONTAINING RIBOSE RING OR ITS DERIVATIVE STRUCTURE AND OLIGONUCLEOTIDE CONJUGATE THEREOF

#171
20260009030
2026-01-08

COMPOUND FOR INHIBITING AGT GENE EXPRESSION, AND PHARMACEUTICAL COMPOSITION AND USE THEREOF

#172
20260009029
2026-01-08

COMPOUND FOR INHIBITING EXPRESSION OF LPA GENE, PHARMACEUTICAL COMPOSITION AND USE THEREOF

#173
20260007776
2026-01-08

DESIGN AND APPLICATION OF NOVEL PHOTORECEPTOR-SPECIFIC PROMOTERS FOR RETINAL GENE THERAPY APPLICATIONS

#174
20260007766
2026-01-08

COMPOSITIONS AND METHODS OF TREATING MUSCLE ATROPHY AND MYOTONIC DYSTROPHY

#175
20260007602
2026-01-08

Neutral Liposomes Containing Biologically Active Agents

#176
20260002215
2026-01-01

ADAM32 GENE IN THE DIAGNOSIS AND TREATMENT OF LUNG ADENOCARCINOMA

#177
20260002162
2026-01-01

THERAPEUTIC COMPOUNDS AND COMPOSITIONS

#178
20260002160
2026-01-01

SIRNA TARGETING AND REGULATING PCSK9 GENE EXPRESSION AND USE THEREOF

#179
20260002157
2026-01-01

MODIFIED SHORT INTERFERING NUCLEIC ACID (siNA) MOLECULES AND USES THEREOF

#180
20260002156
2026-01-01

MODULAR RNA DELIVERY PLATFORMS AND METHODS OF THEIR USE

#181
20260002155
2026-01-01

SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS

#182
20260002154
2026-01-01

COMPOUNDS AND METHODS FOR REDUCING PRION EXPRESSION

#183
20260002153
2026-01-01

COMPOSITIONS AND METHOD FOR THE TREATMENT OF X-LINKED DYSTONIA PARKINSONISM

#184
20260002152
2026-01-01

Antisense Nucleic Acids for Use in the Treatment for LMNA Mutation Carriers

#185
20260000805
2026-01-01

METHODS AND COMPOSITIONS FOR WOUND HEALING

#186
20260000768
2026-01-01

APPLICATION OF COMPOUND OR TRADITIONAL CHINESE MEDICINE EXTRACT IN PREPARATION OF NUCLEIC ACID DELIVERY AGENT, AND RELATED PRODUCTS

#187
20260000701
2026-01-01

SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#188
20260000624
2026-01-01

IONIZABLE LIPID CONTAINING BIODEGRADABLE DISULFIDE BOND AND LIPID NANOPARTICLES COMPRISING SAME

#189
20250388969
2025-12-25

METHODS OF DIAGNOSING AND TREATING ALZHEIMER'S DISEASE

#190
20250388915
2025-12-25

METHODS AND COMPOSITIONS FOR INTRON MEDIATED- EXPRESSION OF REGULATORY ELEMENTS FOR TRAIT DEVELOPMENT

#191
20250388902
2025-12-25

ANTISENSE OLIGOMERS FOR TREATMENT OF NON-SENSE MEDIATED RNA DECAY BASED CONDITIONS AND DISEASES

#192
20250388901
2025-12-25

ADVANCED RNA TARGETING (ARNATAR)

#193
20250388900
2025-12-25

Compositions and Methods for Inhibition of Factor XII Gene Expression

#194
20250388899
2025-12-25

RNA INTERFERENCE OLIGONUCLEOTIDES FOR INHIBITING PERINEURONAL NETWORK FORMATION

#195
20250388897
2025-12-25

NUCLEIC ACID COMPOUNDS

#196
20250388687
2025-12-25

EPO RECEPTOR AGONISTS AND ANTAGONISTS

#197
20250388621
2025-12-25

RNA-DNA FUSOMERS AND METHODS OF USE THEREOF

#198
20250388617
2025-12-25

DOUBLE-STRANDED RNA COMPRISING NUCLEOTIDE ANALOG CAPABLE OF REDUCING OFF-TARGET TOXICITY

#199
20250387512
2025-12-25

METHODS OF IMPROVING SYSTEMIC DISEASE OUTCOMES BY INHIBITION OF ZHX2

#200
20250387490
2025-12-25

IONIZABLE LIPIDS FOR MULTIPLE ORGAN TARGETING

#201
20250382635
2025-12-18

GENERATION OF NEURONS BY REPROGRAMMING OF OLIGODENDROCYTES AND OLIGODENDROCYTE PRECURSOR CELLS

#202
20250382630
2025-12-18

LOX3 GENE MODULATION AND ARMYWORM TOLERANCE

#203
20250382621
2025-12-18

IMMUNE EFFECTOR CELL THERAPIES WITH ENHANCED EFFICACY

#204
20250382620
2025-12-18

SIRNA TARGETING RECQL1 HELICASE GENE

#205
20250382618
2025-12-18

METHODS AND COMPOSITIONS FOR INHIBITING VIRUS

#206
20250382617
2025-12-18

DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS FOR RNA INTERFERENCE AND METHODS RELATING THERETO

#207
20250382616
2025-12-18

SMALL INTERFERING RNA TARGETING CFB AND USES THEREOF

#208
20250382615
2025-12-18

NOVEL RNA THERAPEUTICS AND USES THEREOF

#209
20250382324
2025-12-18

MONOMERS AND METHODS FOR SYNTHESIS OF MODIFIED OLIGONUCLEOTIDES

#210
20250381285
2025-12-18

COMPOSITIONS AND METHODS OF TREATING MUSCLE DYSTROPHY

#211
20250381284
2025-12-18

PRNP RNAi AGENTS

#212
20250378926
2025-12-11

METHODS AND COMPOSITIONS FOR CELL-PROLIFERATION-RELATED DISORDERS

#213
20250376692
2025-12-11

HAPLOID INDUCTION COMPOSITIONS AND METHODS FOR USE THEREFOR

#214
20250376688
2025-12-11

RNAi Agents for Inhibiting Expression of Proprotein Convertase Subtilisin Kexin 9 (PCSK9), Pharmaceutical Compositions Thereof, and Methods of Use

#215
20250376686
2025-12-11

MULTI-FUNCTIONAL NEAR-INFRARED FLUORESCENT POLYMER DOT-SIRNA FOR GENE EXPRESSION REGULATION

#216
20250376682
2025-12-11

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TRANSTHYRETIN

#217
20250376680
2025-12-11

NUCLEIC ACID COMPOUNDS

#218
20250376679
2025-12-11

METHODS AND COMPOSITIONS FOR INHIBITION OF IRF4

#219
20250376678
2025-12-11

THERAPEUTIC AGENT FOR CANCER, TESTING ASSISTANCE METHOD, AND SCREENING METHOD FOR THERAPEUTIC AGENT

#220
20250375388
2025-12-11

COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS

#221
20250369050
2025-12-04

METHODS AND COMPOSITIONS RELATED TO ASSESSMENT AND TREATMENT OF KIDNEY DISEASE

#222
20250369017
2025-12-04

IMPROVED RECOMBINANT ADENO-ASSOCIATED VIRUS PRODUCTION

#223
20250368998
2025-12-04

NUCLEOTIDE ANALOGUES, AND PREPARATION AND APPLICATION THEREOF

#224
20250368997
2025-12-04

Compositions and Methods for GYS1 Inhibition

#225
20250368994
2025-12-04

COMPOSITIONS AND METHODS FOR CONTROL OF PSEUDOGYMNOASCUS DESTRUCTANS

#226
20250368992
2025-12-04

NUCLEIC ACID COMPOUNDS

#227
20250368990
2025-12-04

TREATMENT OF MS4A4E RELATED DISEASES AND DISORDERS

#228
20250368987
2025-12-04

COMPOSITION COMPRISING TAF10 INHIBITOR FOR PREVENTING OR TREATING COLORECTAL CANCER

#229
20250368750
2025-12-04

SHP INHIBITOR COMPOSITIONS AND USES FOR CHIMERIC ANTIGEN RECEPTOR THERAPY

#230
20250367319
2025-12-04

Targeted Nanomedicine for Treating Fibrotic Lung Disorders

#231
20250367152
2025-12-04

Inducing Proliferation of Cardiomyocytes and Therapeutic Uses Related Thereto

#232
20250361529
2025-11-27

GENE EDITING SYSTEM FOR TREATING DUCHENNE MUSCULAR DYSTROPHY, AND METHOD OF TREATING DISEASE USING SAME

#233
20250361520
2025-11-27

METHODS AND COMPOSITIONS FOR PRODUCING SELF-AMPLIFYING RNA FOR GENE SILENCING IN PLANTS

#234
20250361513
2025-11-27

RNA VECTORS WITH HAIRPIN-LIKE INSERTS

#235
20250361511
2025-11-27

NANOPARTICLE COMPOSITIONS CONTAINING SIRP-alpha siRNA FOR TREATMENT OF CANCER

#236
20250361510
2025-11-27

COMPOSITIONS AND METHODS FOR INDUCED TISSUE REGENERATION IN MAMMALIAN SPECIES

#237
20250361508
2025-11-27

POLYNUCLEIC ACID MOLECULES TARGETING AGT AND USES THEREOF

#238
20250361506
2025-11-27

MODIFIED U7 SNRNA CONSTRUCT

#239
20250360223
2025-11-27

MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES

#240
20250360211
2025-11-27

POPULATION OF TRANSFECTED IMMUNE CELLS AND METHOD FOR THEIR PRODUCTION

#241
20250354156
2025-11-20

Compositions and Methods for Treating Cancer

#242
20250354151
2025-11-20

INHIBITORY AGENT FOR MYOCARDIAL CELL DEATH, AND PROPHYLACTIC OR THERAPEUTIC AGENT FOR MYOCARDIAL DISORDERS OR HEART FAILURE

#243
20250354141
2025-11-20

TARGETING ARHGAP5 GENE FUNCTION IN CANCER WITH ARHGAP35 ALTERATION

#244
20250354140
2025-11-20

CALCIUM SALTED SPHERICAL NUCLEIC ACIDS

#245
20250353872
2025-11-20

Ligand-Modified Oligonucleotides

#246
20250352672
2025-11-20

METHOD FOR TREATMENT OF MYOTONIC DYSTROPHY COMBINING PROTEIN EXPRESSION AND RNA INTERFERENCE VECTOR DELIVERY WITH TISSUE DETARGETING

#247
20250352651
2025-11-20

COMPOSITIONS COMPRISING PLN-TARGETING ANTI-TRANSFERRIN RECEPTOR ANTIBODY-POLYNUCLEOTIDES AND METHODS OF USE THEREOF TO TREAT CARDIOMYOPATHY

#248
20250346906
2025-11-13

COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF CD274/PD-L1 GENE

#249
20250346905
2025-11-13

INTERFERING RNA THERAPY FOR PLN-R14del CARDIOMYOPATHY

#250
20250346904
2025-11-13

CCR5 and CD4 siRNA-TARGETED PHOSPHOLIPID NANOSOMES THERAPEUTICS FOR TREATMENT OF HIV-1 AND OTHER DISEASES

#251
20250346902
2025-11-13

RNAI AGENT INHIBITING PCSK9 GENE EXPRESSION AND APPLICATION THEREOF

#252
20250346901
2025-11-13

5-HALOURACIL-MODIFIED MICRORNAS AND THEIR USE IN THE TREATMENT OF CANCER

#253
20250346900
2025-11-13

PHARMACEUTICAL COMPOSITION FOR TREATING CANCER COMPRISING FOXM1 MUTANT OR FOXM1 SHRNA

#254
20250346898
2025-11-13

Linkage Modified Oligomeric Compounds and Uses Thereof

#255
20250346897
2025-11-13

COMPOSITIONS AND METHODS FOR TREATMENT OF MICROSATELLITE DNA EXPANSION DISORDERS

#256
20250346896
2025-11-13

TARGETING MICRO RNA FOR TREATMENT OF HEART FAILURE WITH PRESERVED EJECTION FRACTION (HFPEF)

#257
20250346891
2025-11-13

MODIFIED NUCLEIC ACID CONJUGATES

#258
20250346890
2025-11-13

LEUKEMIA TREATMENT

#259
20250346859
2025-11-13

EXTRACELLULAR VESICLES COMPRISING SMALL INTERFERING RNA

#260
20250346635
2025-11-13

VASCULAR ENDOTHELIAL GROWTH FACTOR RECEPTOR-1 (VEGFR-1) INHIBITORS FOR PROMOTING MYELINATION AND NEUROPROTECTION

#261
20250340888
2025-11-06

COMPOUNDS AND METHODS FOR REDUCING PLN EXPRESSION

#262
20250340885
2025-11-06

COMPOSITIONS AND METHODS FOR MODULATING CONDITIONS ASSOCIATED WITH ALTERED ATP8B1 FUNCTION

#263
20250340884
2025-11-06

ANTISENSE OLIGOMERS AGAINST MONOAMINE OXIDASE B AND USE THEREOF

#264
20250340882
2025-11-06

ANTISENSE OLIGONUCLEOTIDES

#265
20250340881
2025-11-06

PHARMACEUTICAL COMPOSITION FOR TREATING CANCER COMPRISING FOXM1 MUTANT OR FOXM1 SHRNA

#266
20250340880
2025-11-06

COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY

#267
20250340879
2025-11-06

COMPOSITIONS AND METHODS FOR NUCLEIC ACID TRANSFER

#268
20250340877
2025-11-06

RNAi Agents for Inhibiting Expression of Complement Component C3 (C3), Pharmaceutical Compositions Thereof, and Methods of Use

#269
20250340875
2025-11-06

SIRNA MOLECULE AGAINST HUMAN TENASCIN-C (TNC) AND A PHARMACEUTICAL COMPOSITION COMPRISING IT

#270
20250340874
2025-11-06

COMPOUNDS AND METHODS FOR REDUCING PCDH19 EXPRESSION

#271
20250340873
2025-11-06

Method for Treating Cyclophilin D Associated Diseases

#272
20250340872
2025-11-06

COMPOUNDS AND METHODS FOR REDUCING TAU EXPRESSION

#273
20250340871
2025-11-06

COMPOSITION FOR CONTROLLING DNA DAMAGE REPAIR EFFICIENCY

#274
20250339546
2025-11-06

GLIOBLASTOMA TUMOR GROWTH INHIBITON BY SAT1 KNOCKDOWN

#275
20250338857
2025-11-06

USE OF INTERFERING RNAS DIRECTED AGAINST THE CHOLINERGIC SYSTEM FOR CONTROLLING INSECT PESTS

#276
20250334588
2025-10-30

TREATING TUBEROUS SCLEROSIS COMPLEX-ASSOCIATED DISEASES

#277
20250333740
2025-10-30

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF

#278
20250333739
2025-10-30

COMPOSITION FOR REGULATING SPLICING OF POLYBROMO 1 GENE COMPRISING SPLICING-SWITCH OLIGONUCLEOTIDE AS EFFECTIVE COMPONENT

#279
20250333738
2025-10-30

POLYNUCLEIC ACID MOLECULES FOR INHIBITING EXPRESSION OF ANGPTL3, PHARMACEUTICAL COMPOSITIONS, AND USES THEREOF

#280
20250333737
2025-10-30

17ß-HYDROXYSTEROID DEHYDROGENASE TYPE 13 (HSD17B13) iRNA COMPOSITIONS AND METHODS OF USE THEREOF

#281
20250333735
2025-10-30

RNAi Agents for Inhibiting Expression of Complement Component C3 (C3), Pharmaceutical Compositions Thereof, and Methods of Use

#282
20250333732
2025-10-30

TREATMENT OF SOS2 RELATED DISEASES AND DISORDERS

#283
20250333730
2025-10-30

SIRNA FOR INHIBITING ANGPTL3 GENE EXPRESSION AND USE THEREOF

#284
20250333503
2025-10-30

ANTI-PVRIG ANTIBODIES AND METHODS OF USE

#285
20250332288
2025-10-30

CARDIOPROTECTIVE HEART DISEASE THERAPIES

#286
20250332279
2025-10-30

PHARMACEUTICAL COMPOSITION AND METHOD FOR TREATING GLIOBLASTOMAS

#287
20250332238
2025-10-30

INHIBITION OF HISTONE METHYL TRANSFERASES TO TREAT CANCER

#288
20250332190
2025-10-30

LPA-TARGETING SIRNA AND CONJUGATE

#289
20250332112
2025-10-30

IONIZABLE CATIONIC LIPIDS FOR LIPID NANOPARTICLES

#290
20250327803
2025-10-23

SCREENING METHODS FOR TARGETS FOR CANCER THERAPY

#291
20250327124
2025-10-23

METHOD FOR TESTING PULMONARY HYPERTENSION, PATHOLOGICAL ANIMAL MODEL FOR PULMONARY ARTERIAL HYPERTENSION, AND PREVENTIVE OR THERAPEUTIC AGENT FOR PULMONARY HYPERTENSION

#292
20250327079
2025-10-23

METHOD FOR CARDIAC REPAIR

#293
20250327078
2025-10-23

Compositions for and Methods Creating Exon-Skipped mRNA Producing Internal Controls

#294
20250327077
2025-10-23

ANTISENSE MODULATION OF SETBP1 EXPRESSION

#295
20250327070
2025-10-23

COMPOSITIONS AND METHODS FOR INHIBITING COMPLEMENT FACTOR B

#296
20250327046
2025-10-23

ROLE OF POLYPHOSPHATES IN NEUROLOGICAL DISORDERS

#297
20250327032
2025-10-23

AGENT FOR AVOIDING IMMUNE RESPONSE OF TRANSGENIC CELLS

#298
20250325585
2025-10-23

COMPOSITIONS AND METHODS FOR REDUCING CELL THERAPY IMMUNOGENICITY

#299
20250325491
2025-10-23

POLYVALENT MOLECULE BASED LIPID NANOPARTICLES FOR NUCLEIC ACID DELIVERY

#300
20250324954
2025-10-23

METHOD FOR PROMOTING SEXUAL MATURATION OF FISH