109145 ⎘
Structure or type of the nucleic acid; Type of nucleic acid interfering N.A.
Sub-classes:COMPOSITIONS, METHODS AND KITS FOR CHARACTERIZING AND SCREENING FOR SMALL CELL OVARIAN CARCINOMA
#2INHIBITION OF SMOOTH MUSCLE CELL CONTRACTION BY ALTERING INTERLEUKIN 31 RECEPTOR ALPHA LEVELS
#3VIRAL VECTOR MEDIATED GENE THERAPY TRANSDUCTION AND SAFETY OR PROMOTING VIRAL CLEARANCE AND/OR INHIBITING VIRAL INFECTIVITY BY TARGETING CLASS B SCAVENGER RECEPTORS
#4METHODS OF TREATING IMPAIRED GLUCOCORTICOID SIGNALLING IN UTERINE DISORDERS
#5CORONAVIRUS IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#6OLIGONUCLEOTIDE-MEDIATED KNOCKDOWN OF PLN
#7OLIGONUCLEOTIDE-MEDIATED KNOCKDOWN OF DUX4
#8METHODS OF USING ZSCAN4 FOR REJUVENATING HUMAN CELLS
#9INTERFERING RNA FOR INHIBITING JAK1 GENE EXPRESSION AND USE THEREOF
#10ATTENUATION OF CYTOKINE RELEASE SYNDROME IN IMMUNOTHERAPY
#11ATTENUATION OF CYTOKINE RELEASE SYNDROME IN
#12INVERTED CHIMERIC siRNA MOLECULES AND METHODS OF USE THEREOF
#13COMPOSITIONS AND METHODS FOR TREATMENT OF CANCER
#14COMPOSITIONS AND METHODS FOR THE TREATMENT OF LEUKODYSTROPHY AND WHOLE ANIMAL AND CELLULAR MODELS FOR IDENTIFYING EFFICACIOUS AGENTS FOR TREATMENT OF THE SAME
#15SMALL RNA-BASED PROGNOSTIC SIGNATURES AND THERAPEUTIC COMPOSITIONS FOR IDIOPATHIC PULMONARY FIBROSIS
#16DOUBLE STRANDED RNAi AGENTS, COMPOSITIONS AND METHODS OF USE
#17COMPOSITION AND METHOD FOR TREATING CANCER WITH CHROMOSOME TRANSLOCATION FUSION
#18PLIN1 RNAi INTERFERENCE AGENTS
#19RNAi Agent Targeting PCSK9 and Use Thereof
#20INTERFERING RNA FOR INHIBITING TOP1 GENE EXPRESSION AND USE THEREOF
#21ANTI-CANCER TGFB2 AGENTS WITH IMMUNOTHERAPEUTICS
#22NANOCOMPLEX TARGETING NERVOUS NECROSIS VIRUS AS WELL AS PREPARATION METHOD AND USE THEREOF
#23RNAi Agents for Inhibiting Expression of Mucin 5AC (MUC5AC), Compositions Thereof, and Methods of Use
#24METHODS AND COMPOSITIONS FOR THE TREATMENT OF CANCER BY TARGETING ONCOGENIC TRANSFER RNAS
#25COMPOSITIONS AND METHODS FOR DELIVERING A MACROMOLECULE TO A CELL
#26POLYNUCLEOTIDES FOR SILENCING TRANSCRIPT VARIANT 1 OF ASSEMBLY FACTOR FOR SPINDLE MICROTUBULES AND APPLICATIONS THEREOF
#27RNAi Agents for Inhibiting Expression of Activin Receptor-Like Kinase 7 (ALK7), Compositions Thereof, and Methods of Use
#28MODIFIED OLIGONUCLEOTIDES AND DOUBLE-STRANDED RNAS
#29RNAi AGENTS FOR MODULATING SNCA
#30STABILIZED RNA AGENTS
#31GENE THERAPY FOR PRADER WILLI SYNDROME
#32METHODS OF TREATING CANCERS
#33RNA THERAPEUTICS FOR FIBRODYSPLASIA OSSIFICANS PROGRESSIVA AND USES THEREOF
#34COMPOSITIONS AND METHODS FOR MODULATION OF CFTR
#35THERAPEUTIC AGENT FOR TREATING HIF-1alpha-MEDIATED DISEASES BY INHIBITING AREL1 AND RESTORING PHD2 ACTIVITY
#36TREATMENT OF CANCERS HAVING A DRUG-RESISTANT MESENCHYMAL CELL STATE
#37CHEMICAL MODIFICATIONS OF SMALL INTERFERING RNA WITH MINIMAL FLUORINE CONTENT
#38DOUBLE-STRANDED RNAi AGENTS FOR TARGETING AND REGULATING HBV GENE EXPRESSION, AND A USE THEREOF
#39FINE-TUNING INFLAMMATION BY ALTERING 3'UTR LENGTH
#40COMPOSITIONS FOR AQUACULTURING
#41PLATELETS TRANSFECTED WITH SIRNA AND THE THERAPEUTICS USES THEREOF
#42COMPOSITIONS AND METHODS FOR TREATING MYOPATHY
#43MODULATORY POLYNUCLEOTIDES
#44SURF4 GENE KNOCKOUT ERYTHROID PROGENITOR CELLS AND METHODS OF ERYTHROID DIFFERENTIATION THEREOF
#45MEANS TO TREAT AUTOIMMUNITY BY REFINING REGULATORY T CELLS
#46EPO RECEPTOR AGONISTS AND ANTAGONISTS
#47METHODS AND COMPOSITIONS FOR TREATING CORNEAL WOUNDS
#48DRUG DELIVERY SYSTEM FOR BLOOD-BRAIN BARRIER PENETRATION
#49POLYMER DERIVATIVES AND THEIR USE AS LIPID NANOPARTICLE MODIFIERS
#50LIPID NANOPARTICLES
#51COMPOSITIONS AND METHODS TO MODULATE TUMOR MICROENVIRONMENT ASSOCIATED LONG NONCODING RNAS
#52PREPARATION AND USE OF NUCLEIC ACID WITH ANTI-HAIR LOSS AND OIL CONTROL EFFECTS AND COMPOSITION INCLUDING NUCLEIC ACID
#53METHODS, SYSTEMS, AND COMPOSITIONS FOR TREATMENT OF HEMOGLOBINOPATHY (E.G., BETA-THALASSEMIA AND SICKLE CELL DISEASE) BY INCREASING EXPRESSION OF NONCODING RNA ACTIVATED BY DNA DAMAGE
#54HIPPO AND DYSTROPHIN COMPLEX SIGNALING IN CARDIOMYOCYTE RENEWAL
#55OLIGONUCLEOTIDES FOR MAPT MODULATION
#56Methods for Preventing Cardiovascular Events Through Proprotein Convertase Subtilisin Kexin 9 (PCSK9) Reduction
#57METHODS AND COMPOSITIONS FOR SELECTIVE REGULATION OF PROTEIN EXPRESSION
#58ANTISENSE OLIGONUCLEOTIDES FOR THE TREATMENT OF CANAVAN DISEASE
#59C-MYC-TARGETING CHARGE-ALTERING RELEASABLE TRANSPORTERS AS ANTI-TUMOR AGENTS FOR BREAST CANCER THERAPY
#60NOVEL COMPOUND AND APPLICATION THEREOF
#61NOVEL COMPOUND AND APPLICATION THEREOF
#62siRNA COMPOSITIONS AND METHODS TARGETING ALPHA-SYNUCLEIN NUCLEIC ACIDS
#63KLRG1 SIGNALLING THERAPY FOR INFECTIOUS DISEASE
#64PKC INHIBITORS FOR THE TREATMENT OF SEPTIC CHOLESTASIS WITH POLYMETHINE DYE TARGETING
#65METHODS OF ATTENUATING AN IMMUNE RESPONSE BY INHIBITION OF BFL1
#66COMPOSITIONS AND METHODS FOR TREATMENT OF NEUROINFLAMMATORY DISEASES
#67COMPOSITIONS AND METHODS TO TREAT ALZHEIMER'S DISEASE AND OTHER BRAIN DISEASES
#68METHODS AND COMPOSITIONS FOR DESIGNING AND SELECTING TINYRNAS TO MAXIMIZE TARGET CLEAVAGE
#69COMPOSITIONS AND METHODS FOR TREATMENT OF SPINOCEREBELLAR ATAXIAS
#70COMPOSITIONS AND METHODS FOR TREATMENT OF NEUROLOGICAL DISORDERS
#71MODIFIED DOUBLE-STRANDED RNA AGENTS
#72INDUCTION OF STEM-LIKE ACTIVATED T CELLS
#73ANTI-C5 ANTIBODY/C5 IRNA DOSING REGIMENS FOR TREATING C5-ASSOCIATED DISEASES
#74RESPIRATORY SYNCYTIAL VIRUS (RSV) POLYANHYDRIDE NANOPARTICLE VACCINE
#75DNA-RNA HETERODUPLEX TARGETING ANDROGEN RECEPTOR
#76METHODS FOR TREATMENT OF ANEMIA
#77NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE
#78DOUBLE-STRANDED RNAI AGENTS AND COMPOSITIONS FOR REDUCING EXPRESSION OF ANGIOPOIETIN-LIKE 3 (ANGPTL3) AND METHODS OF USE THEREOF
#79Carbohydrate-oligonucleotide conjugates, pharmaceutical compositions, and therapeutic applications
#80PRODUCTS AND COMPOSITIONS
#81TREATMENT OF THYMIC STROMAL LYMPHOPOIETIN (TSLP) RELATED DISEASES BY INHIBITION OF LONG-FORM TSLP TRANSCRIPTS
#82MICRORNA AND USES THEREOF IN PREVENTION AND/OR TREATMENT OF FIBROPLASIA MEDICAL SIGN AND/OR SYNDROME
#83IRON METABOLISM TARGETS FOR OBESITY
#84GALNAC MONOMER COMPRISING RIBOSE RING OR DERIVATIVE STRUCTURE THEREOF AND USE THEREOF IN LIVER-TARGETED DELIVERY OF SMALL NUCLEIC ACID DRUGS
#85SIRNA FOR TARGETED INHIBITION OF AGT GENE EXPRESSION AND USE THEREOF IN TREATING HYPERTENSION
#86USE OF HOMEOBOX CONTAINING 1 (HMBOX1) INHIBITOR IN PREPARATION OF DRUG FOR PREVENTION AND/OR TREATMENT OF MUSCLE ATROPHY
#87CONJUGATED OLIGONUCLEOTIDE COMPOUNDS, METHODS OF MAKING AND USES THEREOF
#88DOWNREGULATING INOS TO INCREASE CAR-T KILLING
#89Methods for Directing Lipid Nanoparticles in Vivo
#90RNAi Agents for Inhibiting Influenza A Viral Gene Expression, Compositions Thereof, and Methods of Use
#91NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF LPA IN A CELL
#92Method of Inhibiting Durotaxis and/or Treating Fibrosis
#93DSRNA, USE THEREOF AND PREPARATION METHOD THEREFOR
#94MATERIALS AND PROCESSES FOR ENGINEERING HYPOIMMUNOGENICITY
#95LIPID CONJUGATES FOR THE DELIVERY OF THERAPEUTIC AGENTS TO ADIPOSE TISSUE
#96CONJUGATE OF NUCLEOTIDE ANALOG-CONTAINING DOUBLE-STRANDED RNAI ANALOG
#97COMPOSITIONS AND METHODS FOR INHIBITING LPA EXPRESSION
#98ORGANIC COMPOSITIONS TO TREAT KRAS-RELATED DISEASES
#99COMPOSITIONS AND METHODS FOR THE DELIVERY OF ACTIVE AGENTS INCLUDING NUCLEIC ACIDS
#100RNA INTERFERENCE (RNAI) FOR CONTROL OF JAPANESE BEETLE
#101METHODS FOR IMPROVING PRODUCTION OF BIOLOGICAL PRODUCTS BY REDUCING THE LEVEL OF ENDOGENOUS PROTEIN
#102Treatment Of Pan-Cancer Phenotype With Regulator of Telomere Elongation Helicase 1 (RTEL1) Inhibitors
#103TREATMENT FOR OVARIAN CANCER WITH OLIGONUCLEOTIDES TARGETING FIBROBLAST ACTIVATION PROTEIN ALPHA
#104OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#105METHODS AND COMPOSITIONS OF TREATING RETINAL DEGENERATIVE DISEASES
#106LIPOSOMAL PARTICLES, METHODS OF MAKING SAME AND USES THEREOF
#107USE OF PGAM2 IN BREEDING OF BLCATTLE BLACK CATTLE
#108MARKERS SELECTIVELY DEREGULATED IN TUMOR-INFILTRATING REGULATORY T CELLS
#109COMPOSITIONS AND METHODS FOR INHIBITING XDH EXPRESSION
#110REVERSIR MOLECULES AND METHODS OF USE THEREOF
#111SIRNA TARGETING ANGPTL4, AND CONJUGATES AND USES THEREOF
#112EXTRACELLULAR VESICLE COMPRISING A BIOLOGICALLY ACTIVE MOLECULE AND A DUAL CLEAVABLE LINKER
#113TREATMENT OF MST1 RELATED DISEASES AND DISORDERS
#114COMPOUNDS AND METHODS FOR TREATING HUMAN SUBJECTS
#115COMPOSITIONS AND METHODS FOR TREATING NONALCOHOLIC FATTY LIVER DISEASE
#116OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#117NONCODING RNA AGENTS (BCYRN1 AND DERIVATIVES THEREOF) TO TREAT DISEASES OF IMMUNITY
#118COMPOSITIONS AND METHODS FOR TREATING TRANSTHYRETIN (TTR) MEDIATED AMYLOIDOSIS
#119Therapeutic Strategies To Reduce Thrombotic Risk In Factor V Leiden (FVL) Carriers
#120TREM2 BINDS TO SPECIFICALLY STRUCTURED HEPARAN SULFATE
#121ANTISENSE OLIGONUCLEOTIDE-BASED ANTI-FIBROTIC THERAPEUTICS
#122REGULATION OF ACTIVITY OF RNAI MOLECULES
#123EXPRESSION OF FC-CONTAINING PROTEINS
#124COMPOSITIONS AND METHODS OF USING PRKAG2-TARGETING ANTIBODY-OLIGONUCLEOTIDE CONJUGATES
#125Inhibition of TCF4/ITF2 in the Treatment of Cancer
#126METHODS OF ALTERING THE STARCH GRANULE PROFILE IN PLANTS
#127COMPOSITIONS AND METHODS FOR INHIBITING ADENYLATE CYCLASE 9 (AC9)
#128Oligonucleotide for reducing the expression of leucine-rich repeat kinase 2 (LRRK2) and its use for preventing and/or treating human diseases
#129RNAi Agents for Inhibiting Expression of Thymic Stromal Lymphopoietin (TSLP), Compositions Thereof, and Methods of Use
#130LINKER, COMPOUND INCLUDING LINKER, METHOD OF PREPARING COMPOUND, USE OF LINKER, AND METHOD OF DELIVERING OLIGONUCLEOTIDES THROUGH LINKER
#131RNAi Agents And Compositions for Inhibiting Expression of Apolipoprotein C-III (APOC3)
#132METHODS FOR TREATING ENDOMETRIAL AND OVARIAN HYPERPROLIFERATIVE DISORDERS
#133VIRAL VECTOR
#134AGENTS THAT INHIBIT CCN LIGAND-INDUCED SIGNALLING FOR TREATING DISEASE
#135SIRNA TARGETING KEY GENE OF MAGNAPORTHE ORYZAE FOR CONTROLLING RICE BLAST, AND USE THEREOF
#136PLASMINOGEN (PLG) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#137METHODS AND COMPOSITIONS FOR TARGETING SERINE DEHYDRATASE
#138COMPOSITIONS AND METHODS FOR INHIBITION OF EXPRESSION OF INHIBIN SUBUNIT BETA E (INHBE) GENES
#139OLIGONUCLEOTIDES FOR PRNP MODULATION
#140COMBINATION TREATMENT FOR CANCER
#141SYSTEMS AND METHODS FOR TARGETING NAD-BASED PATHWAYS FOR TREATMENT OF CANCER
#142KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#143HYBRID OLIGONUCLEOTIDES
#144AGENTS FOR MODULATING EXPRESSION
#145COMPOSITIONS AND METHODS FOR INHIBITION OF EXPRESSION OF INHIBIN SUBUNIT BETA E (INHBE) GENES
#146RNAi AGENTS OF PRION EXPRESSION
#147POLYPEPTIDES SELF-ASSEMBLING INTO NANOPARTICLES
#148B CELL-SPECIFIC MAB-SIRNA CONJUGATES IMPROVE MYASTHENIA
#149COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#150ASPARAGINE SYNTHETASE INHIBITORS AND USES THEREOF
#151SUBPOPULATION-DIRECTED REMEDIATION OF DISEASE-ASSOCIATED GENE PRODUCTS
#152RNAi Agents for Inhibiting Expression of Complement Factor B (CFB), Pharmaceutical Compositions Thereof, and Methods of Use
#153GENETIC MODULATORS OF KRAS PROTEIN EXPRESSION AND THEIR USES
#154Optimized RNAi Agents for Inhibiting Expression of Coronavirus (CoV) Viral Genomes, Compositions Thereof, and Methods of Use
#155PHARMACEUTICAL COMPOSITION FOR PREVENTING OR TREATING CANCER COMPRISING SIRNA AS ACTIVE INGREDIENT
#156POLYNUCLEOTIDE COMPOSITIONS AND METHODS FOR TREATMENT OF NEURODEGENERATIVE DISEASES
#157TAU-SEED INTERACTOR INHIBTORS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS
#158METHODS AND COMPOSITIONS FOR SELECTIVELY MODULATING GENE EXPRESSION IN MEGAKARYOCYTES AND PLATELETS
#159METHODS FOR TREATING GLIOBLASTOMA OR RECURRENT GLIOBLASTOMA UTILIZING A WIRELESS SIGNAL ALONE OR IN COMBINATION WITH ONE OR MORE CANCER DRUGS, AND ASSOCIATED SYSTEMS, APPARATUSES, AND DEVICES
#1601'-ALKYL MODIFIED RIBOSE DERIVATIVES AND METHODS OF USE
#161LIPID NANOPARTICLE AND PHARMACEUTICAL COMPOSITION
#162DOUBLE STRANDED RNAi AGENTS, COMPOSITIONS AND METHODS OF USE
#163SPERMATOGENESIS ALTERATION
#164FACTOR XII (HAGEMAN FACTOR) (F12), KALLIKREIN B, PLASMA (FLETCHER FACTOR) 1 (KLKB1), AND KININOGEN 1 (KNG1) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#165NOVEL STAPLE NUCLEIC ACID
#166COMPOSITIONS AND METHODS OF TREATING MUSCLE DYSTROPHY
#167RNA-BASED CONTROL OF PRODUCTION OF DEOXYNIVALENOL BY FUSARIUM
#168RNAi Agents for Inhibiting Expression of Mitochondrial Amidoxime Reducing Component 1 (MARC1), Pharmaceutical Compositions Thereof, and Methods of Use
#169INHIBITORS OF EXPRESSION AND/OR FUNCTION
#170GALNAC COMPOUND CONTAINING RIBOSE RING OR ITS DERIVATIVE STRUCTURE AND OLIGONUCLEOTIDE CONJUGATE THEREOF
#171COMPOUND FOR INHIBITING AGT GENE EXPRESSION, AND PHARMACEUTICAL COMPOSITION AND USE THEREOF
#172COMPOUND FOR INHIBITING EXPRESSION OF LPA GENE, PHARMACEUTICAL COMPOSITION AND USE THEREOF
#173DESIGN AND APPLICATION OF NOVEL PHOTORECEPTOR-SPECIFIC PROMOTERS FOR RETINAL GENE THERAPY APPLICATIONS
#174COMPOSITIONS AND METHODS OF TREATING MUSCLE ATROPHY AND MYOTONIC DYSTROPHY
#175Neutral Liposomes Containing Biologically Active Agents
#176ADAM32 GENE IN THE DIAGNOSIS AND TREATMENT OF LUNG ADENOCARCINOMA
#177THERAPEUTIC COMPOUNDS AND COMPOSITIONS
#178SIRNA TARGETING AND REGULATING PCSK9 GENE EXPRESSION AND USE THEREOF
#179MODIFIED SHORT INTERFERING NUCLEIC ACID (siNA) MOLECULES AND USES THEREOF
#180MODULAR RNA DELIVERY PLATFORMS AND METHODS OF THEIR USE
#181SIRNA THERAPY FOR TRANSTHYRETIN (TTR) RELATED OCULAR AMYLOIDOSIS
#182COMPOUNDS AND METHODS FOR REDUCING PRION EXPRESSION
#183COMPOSITIONS AND METHOD FOR THE TREATMENT OF X-LINKED DYSTONIA PARKINSONISM
#184Antisense Nucleic Acids for Use in the Treatment for LMNA Mutation Carriers
#185METHODS AND COMPOSITIONS FOR WOUND HEALING
#186APPLICATION OF COMPOUND OR TRADITIONAL CHINESE MEDICINE EXTRACT IN PREPARATION OF NUCLEIC ACID DELIVERY AGENT, AND RELATED PRODUCTS
#187SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#188IONIZABLE LIPID CONTAINING BIODEGRADABLE DISULFIDE BOND AND LIPID NANOPARTICLES COMPRISING SAME
#189METHODS OF DIAGNOSING AND TREATING ALZHEIMER'S DISEASE
#190METHODS AND COMPOSITIONS FOR INTRON MEDIATED- EXPRESSION OF REGULATORY ELEMENTS FOR TRAIT DEVELOPMENT
#191ANTISENSE OLIGOMERS FOR TREATMENT OF NON-SENSE MEDIATED RNA DECAY BASED CONDITIONS AND DISEASES
#192ADVANCED RNA TARGETING (ARNATAR)
#193Compositions and Methods for Inhibition of Factor XII Gene Expression
#194RNA INTERFERENCE OLIGONUCLEOTIDES FOR INHIBITING PERINEURONAL NETWORK FORMATION
#195NUCLEIC ACID COMPOUNDS
#196EPO RECEPTOR AGONISTS AND ANTAGONISTS
#197RNA-DNA FUSOMERS AND METHODS OF USE THEREOF
#198DOUBLE-STRANDED RNA COMPRISING NUCLEOTIDE ANALOG CAPABLE OF REDUCING OFF-TARGET TOXICITY
#199METHODS OF IMPROVING SYSTEMIC DISEASE OUTCOMES BY INHIBITION OF ZHX2
#200IONIZABLE LIPIDS FOR MULTIPLE ORGAN TARGETING
#201GENERATION OF NEURONS BY REPROGRAMMING OF OLIGODENDROCYTES AND OLIGODENDROCYTE PRECURSOR CELLS
#202LOX3 GENE MODULATION AND ARMYWORM TOLERANCE
#203IMMUNE EFFECTOR CELL THERAPIES WITH ENHANCED EFFICACY
#204SIRNA TARGETING RECQL1 HELICASE GENE
#205METHODS AND COMPOSITIONS FOR INHIBITING VIRUS
#206DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS FOR RNA INTERFERENCE AND METHODS RELATING THERETO
#207SMALL INTERFERING RNA TARGETING CFB AND USES THEREOF
#208NOVEL RNA THERAPEUTICS AND USES THEREOF
#209MONOMERS AND METHODS FOR SYNTHESIS OF MODIFIED OLIGONUCLEOTIDES
#210COMPOSITIONS AND METHODS OF TREATING MUSCLE DYSTROPHY
#211PRNP RNAi AGENTS
#212METHODS AND COMPOSITIONS FOR CELL-PROLIFERATION-RELATED DISORDERS
#213HAPLOID INDUCTION COMPOSITIONS AND METHODS FOR USE THEREFOR
#214RNAi Agents for Inhibiting Expression of Proprotein Convertase Subtilisin Kexin 9 (PCSK9), Pharmaceutical Compositions Thereof, and Methods of Use
#215MULTI-FUNCTIONAL NEAR-INFRARED FLUORESCENT POLYMER DOT-SIRNA FOR GENE EXPRESSION REGULATION
#216COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF TRANSTHYRETIN
#217NUCLEIC ACID COMPOUNDS
#218METHODS AND COMPOSITIONS FOR INHIBITION OF IRF4
#219THERAPEUTIC AGENT FOR CANCER, TESTING ASSISTANCE METHOD, AND SCREENING METHOD FOR THERAPEUTIC AGENT
#220COMPOSITIONS AND METHODS FOR DELIVERY OF BIOMACROMOLECULE AGENTS
#221METHODS AND COMPOSITIONS RELATED TO ASSESSMENT AND TREATMENT OF KIDNEY DISEASE
#222IMPROVED RECOMBINANT ADENO-ASSOCIATED VIRUS PRODUCTION
#223NUCLEOTIDE ANALOGUES, AND PREPARATION AND APPLICATION THEREOF
#224Compositions and Methods for GYS1 Inhibition
#225COMPOSITIONS AND METHODS FOR CONTROL OF PSEUDOGYMNOASCUS DESTRUCTANS
#226NUCLEIC ACID COMPOUNDS
#227TREATMENT OF MS4A4E RELATED DISEASES AND DISORDERS
#228COMPOSITION COMPRISING TAF10 INHIBITOR FOR PREVENTING OR TREATING COLORECTAL CANCER
#229SHP INHIBITOR COMPOSITIONS AND USES FOR CHIMERIC ANTIGEN RECEPTOR THERAPY
#230Targeted Nanomedicine for Treating Fibrotic Lung Disorders
#231Inducing Proliferation of Cardiomyocytes and Therapeutic Uses Related Thereto
#232GENE EDITING SYSTEM FOR TREATING DUCHENNE MUSCULAR DYSTROPHY, AND METHOD OF TREATING DISEASE USING SAME
#233METHODS AND COMPOSITIONS FOR PRODUCING SELF-AMPLIFYING RNA FOR GENE SILENCING IN PLANTS
#234RNA VECTORS WITH HAIRPIN-LIKE INSERTS
#235NANOPARTICLE COMPOSITIONS CONTAINING SIRP-alpha siRNA FOR TREATMENT OF CANCER
#236COMPOSITIONS AND METHODS FOR INDUCED TISSUE REGENERATION IN MAMMALIAN SPECIES
#237POLYNUCLEIC ACID MOLECULES TARGETING AGT AND USES THEREOF
#238MODIFIED U7 SNRNA CONSTRUCT
#239MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING DYSTROPHINOPATHIES
#240POPULATION OF TRANSFECTED IMMUNE CELLS AND METHOD FOR THEIR PRODUCTION
#241Compositions and Methods for Treating Cancer
#242INHIBITORY AGENT FOR MYOCARDIAL CELL DEATH, AND PROPHYLACTIC OR THERAPEUTIC AGENT FOR MYOCARDIAL DISORDERS OR HEART FAILURE
#243TARGETING ARHGAP5 GENE FUNCTION IN CANCER WITH ARHGAP35 ALTERATION
#244CALCIUM SALTED SPHERICAL NUCLEIC ACIDS
#245Ligand-Modified Oligonucleotides
#246METHOD FOR TREATMENT OF MYOTONIC DYSTROPHY COMBINING PROTEIN EXPRESSION AND RNA INTERFERENCE VECTOR DELIVERY WITH TISSUE DETARGETING
#247COMPOSITIONS COMPRISING PLN-TARGETING ANTI-TRANSFERRIN RECEPTOR ANTIBODY-POLYNUCLEOTIDES AND METHODS OF USE THEREOF TO TREAT CARDIOMYOPATHY
#248COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF CD274/PD-L1 GENE
#249INTERFERING RNA THERAPY FOR PLN-R14del CARDIOMYOPATHY
#250CCR5 and CD4 siRNA-TARGETED PHOSPHOLIPID NANOSOMES THERAPEUTICS FOR TREATMENT OF HIV-1 AND OTHER DISEASES
#251RNAI AGENT INHIBITING PCSK9 GENE EXPRESSION AND APPLICATION THEREOF
#2525-HALOURACIL-MODIFIED MICRORNAS AND THEIR USE IN THE TREATMENT OF CANCER
#253PHARMACEUTICAL COMPOSITION FOR TREATING CANCER COMPRISING FOXM1 MUTANT OR FOXM1 SHRNA
#254Linkage Modified Oligomeric Compounds and Uses Thereof
#255COMPOSITIONS AND METHODS FOR TREATMENT OF MICROSATELLITE DNA EXPANSION DISORDERS
#256TARGETING MICRO RNA FOR TREATMENT OF HEART FAILURE WITH PRESERVED EJECTION FRACTION (HFPEF)
#257MODIFIED NUCLEIC ACID CONJUGATES
#258LEUKEMIA TREATMENT
#259EXTRACELLULAR VESICLES COMPRISING SMALL INTERFERING RNA
#260VASCULAR ENDOTHELIAL GROWTH FACTOR RECEPTOR-1 (VEGFR-1) INHIBITORS FOR PROMOTING MYELINATION AND NEUROPROTECTION
#261COMPOUNDS AND METHODS FOR REDUCING PLN EXPRESSION
#262COMPOSITIONS AND METHODS FOR MODULATING CONDITIONS ASSOCIATED WITH ALTERED ATP8B1 FUNCTION
#263ANTISENSE OLIGOMERS AGAINST MONOAMINE OXIDASE B AND USE THEREOF
#264ANTISENSE OLIGONUCLEOTIDES
#265PHARMACEUTICAL COMPOSITION FOR TREATING CANCER COMPRISING FOXM1 MUTANT OR FOXM1 SHRNA
#266COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#267COMPOSITIONS AND METHODS FOR NUCLEIC ACID TRANSFER
#268RNAi Agents for Inhibiting Expression of Complement Component C3 (C3), Pharmaceutical Compositions Thereof, and Methods of Use
#269SIRNA MOLECULE AGAINST HUMAN TENASCIN-C (TNC) AND A PHARMACEUTICAL COMPOSITION COMPRISING IT
#270COMPOUNDS AND METHODS FOR REDUCING PCDH19 EXPRESSION
#271Method for Treating Cyclophilin D Associated Diseases
#272COMPOUNDS AND METHODS FOR REDUCING TAU EXPRESSION
#273COMPOSITION FOR CONTROLLING DNA DAMAGE REPAIR EFFICIENCY
#274GLIOBLASTOMA TUMOR GROWTH INHIBITON BY SAT1 KNOCKDOWN
#275USE OF INTERFERING RNAS DIRECTED AGAINST THE CHOLINERGIC SYSTEM FOR CONTROLLING INSECT PESTS
#276TREATING TUBEROUS SCLEROSIS COMPLEX-ASSOCIATED DISEASES
#277OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#278COMPOSITION FOR REGULATING SPLICING OF POLYBROMO 1 GENE COMPRISING SPLICING-SWITCH OLIGONUCLEOTIDE AS EFFECTIVE COMPONENT
#279POLYNUCLEIC ACID MOLECULES FOR INHIBITING EXPRESSION OF ANGPTL3, PHARMACEUTICAL COMPOSITIONS, AND USES THEREOF
#28017ß-HYDROXYSTEROID DEHYDROGENASE TYPE 13 (HSD17B13) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#281RNAi Agents for Inhibiting Expression of Complement Component C3 (C3), Pharmaceutical Compositions Thereof, and Methods of Use
#282TREATMENT OF SOS2 RELATED DISEASES AND DISORDERS
#283SIRNA FOR INHIBITING ANGPTL3 GENE EXPRESSION AND USE THEREOF
#284ANTI-PVRIG ANTIBODIES AND METHODS OF USE
#285CARDIOPROTECTIVE HEART DISEASE THERAPIES
#286PHARMACEUTICAL COMPOSITION AND METHOD FOR TREATING GLIOBLASTOMAS
#287INHIBITION OF HISTONE METHYL TRANSFERASES TO TREAT CANCER
#288LPA-TARGETING SIRNA AND CONJUGATE
#289IONIZABLE CATIONIC LIPIDS FOR LIPID NANOPARTICLES
#290SCREENING METHODS FOR TARGETS FOR CANCER THERAPY
#291METHOD FOR TESTING PULMONARY HYPERTENSION, PATHOLOGICAL ANIMAL MODEL FOR PULMONARY ARTERIAL HYPERTENSION, AND PREVENTIVE OR THERAPEUTIC AGENT FOR PULMONARY HYPERTENSION
#292METHOD FOR CARDIAC REPAIR
#293Compositions for and Methods Creating Exon-Skipped mRNA Producing Internal Controls
#294ANTISENSE MODULATION OF SETBP1 EXPRESSION
#295COMPOSITIONS AND METHODS FOR INHIBITING COMPLEMENT FACTOR B
#296ROLE OF POLYPHOSPHATES IN NEUROLOGICAL DISORDERS
#297AGENT FOR AVOIDING IMMUNE RESPONSE OF TRANSGENIC CELLS
#298COMPOSITIONS AND METHODS FOR REDUCING CELL THERAPY IMMUNOGENICITY
#299POLYVALENT MOLECULE BASED LIPID NANOPARTICLES FOR NUCLEIC ACID DELIVERY
#300METHOD FOR PROMOTING SEXUAL MATURATION OF FISH