109146 ⎘
Structure or type of the nucleic acid; Type of nucleic acid interfering N.A. MicroRNAs, miRNAs
COMPOSITIONS AND METHODS FOR TREATMENT OF CANCERS
#2DNA COMPOSITIONS AND RELATED METHODS
#3ATTENUATION OF CYTOKINE RELEASE SYNDROME IN IMMUNOTHERAPY
#4MICROPARTICLE, PREVENTIVE DRUG OR THERAPEUTIC DRUG FOR ERECTILE DYSFUNCTION, AND METHOD FOR IMPROVING ERECTILE DYSFUNCTION
#5VIRAL EXPRESSION CONSTRUCT COMPRISING A FIBROBLAST GROWTH FACTOR (FGF21) CODING SEQUENCE
#6COMPOSITIONS OF EXTRACELLULAR VESICLES AND METHOD USING THE SAME
#7COMPOSITION AND METHODS TO REDUCE INFLAMMATION AND PROMOTE REJUVENATION
#8USE OF MIR-15A-5P IN TREATMENT OF FUNDUS OCULI DISEASE
#9OLIGONUCLEOTIDES CONJUGATED TO OLEIC ACID AND USES THEREOF
#10INHIBITORY RNA FOR THE CONTROL OF PHYTOPATHOGENS
#11LONG NON-CODING RNAS AS TARGET FOR TREATING FIBROSIS AND CANCER
#12MODULATORY POLYNUCLEOTIDES
#13CELLULAR COMPOSITIONS AND METHODS OF TREATMENT I
#14MICROPARTICLE, AGENT FOR ACTIVATING NK CELL, METHOD FOR CULTURING NK CELL, METHOD FOR PRODUCING ACTIVATED NK CELL, AND METHOD FOR ACTIVATING NK CELL
#15ANTI-FIBROTIC MICRORNA COMPOSITION
#16COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#17COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#18METHODS AND COMPOSITIONS FOR SINGLE-STRANDED RNA-INITIATED RISC ASSEMBLY
#19Treating herpesvirus-mediated intestinal dysfunction for prevention of age-related neurodegeneration
#20COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#21ZIKV-BASED GENE DELIVERY SYSTEM
#22NUCLEIC ACID CARRIER AND METHOD FOR ADMINISTERING NUCLEIC ACID
#23ONCOLYTIC VIRUS EXPRESSING AN IMMUNE CELL ENGAGER FOR TUMOR TARGETING
#24METHODS FOR IDENTIFYING TREATMENT TARGETS BASED ON MULTIOMICS DATA
#25BIOMATERIALS AND PROCESSES FOR IMMUNE SYNAPSE MODULATION OF HYPOIMMUNOGENICITY
#26LIPOSOMAL NANOCARRIER DELIVERY SYSTEM FOR TARGETING ACTIVE CD44 MOLECULE, PREPARATION METHOD THEREFOR, AND USES THEREOF
#27COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#28LIPOSOMAL PARTICLES, METHODS OF MAKING SAME AND USES THEREOF
#29TREATMENT
#30TREATMENT OF ALZHEIMER'S DISEASE WITH VASCULAR PROGENITOR-DERIVED EXOSOMES ENRICHED WITH MICRORNAS OR THIOREDOXIN
#31COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#32REGULATION OF NUCLEOTIDE EXCISION REPAIR (NER) BY MICRORNA FOR TREATMENT OF CANCER
#33Harnessing MicroRNAs (miRNAs) for Targeted Therapeutics in Cardiac Arrest
#34MIRNAS TARGETING ATNX2 FOR THE TREATMENT OF ALS AND SCA2
#35METHODS AND COMPOSITIONS FOR GENERATING DOMINANT ALLELES USING GENOME EDITING
#36COMPRISING EXOSOMAL MIR-664A-5P AS AN ACTIVE INGREDIENT, A DIAGNOSTIC BIOMARKER COMPOSITION FOR PARP INHIBITOR RESPONSE AND A PHARMACEUTICAL COMPOSITION FOR CANCER TREATMENT
#37SYSTEMS AND METHODS FOR TARGETING NAD-BASED PATHWAYS FOR TREATMENT OF CANCER
#38PLANT REGULATORY ELEMENTS AND USES THEREOF
#39AAV-MEDIATED DELIVERY OF OSTEOBLAST/OSTEOCLAST-REGULATING MIRNAS FOR OSTEOPOROSIS THERAPY
#40METHOD FOR PREPARING ENHANCED CAR-T-CELLS BASED ON INTERFERING OR KNOCKING OUT HUMAN PCSK9 GENE AND APPLICATION THEREOF
#41ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY
#42METHODS AND COMPOSITIONS FOR SELECTIVELY MODULATING GENE EXPRESSION IN MEGAKARYOCYTES AND PLATELETS
#43TXNIP INHIBITION TO ENHANCE ADOPTIVE IMMUNOTHERAPY
#44NOVEL THERAPY
#45MODIFYING THE SPECIFICITY OF PLANT NON-CODING RNA MOLECULES FOR SILENCING GENE EXPRESSION
#46METHODS OF MAKING AND USING IMMUNE-TOLERIZED FETAL STEM CELL-DERIVED EXTRACELLULAR VESICLES FOR HAIR LOSS TREATMENT
#47IONIZABLE LIPID CONTAINING BIODEGRADABLE DISULFIDE BOND AND LIPID NANOPARTICLES COMPRISING SAME
#48WNT-MODULATING GENE SILENCERS AS BONE ANABOLIC THERAPY FOR OSTEOPOROSIS AND CRITICAL-SIZED BONE DEFECT
#49COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#50POLYCISTRONIC miRNA CONSTRUCTS FOR IMMUNE CHECKPOINT INHIBITION
#51IONIZABLE LIPIDS FOR MULTIPLE ORGAN TARGETING
#52GENERATION OF NEURONS BY REPROGRAMMING OF OLIGODENDROCYTES AND OLIGODENDROCYTE PRECURSOR CELLS
#53HMGB1 EXPRESSION REGULATOR, PROPHYLACTIC AGENT OR THERAPEUTIC AGENT FOR ACUTE LUNG INJURY, ACUTE RESPIRATORY DISTRESS SYNDROME, OR SEPSIS, OR METHOD OF AMELIORATING SAME
#54Gene constructs for silencing alpha-synuclein and uses thereof
#55GENERATION OF NEURONS BY REPROGRAMMING OF OLIGODENDROCYTES AND OLIGODENDROCYTE PRECURSOR CELLS
#56MIR449A AS A THERAPEUTIC FOR NEURODEGENERATIVE DISORDERS
#57COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#58POLYMER NANOPARTICLE COMPOSITIONS FOR NON-VIRAL GENE DELIVERY
#59MICRORNAS FOR CARDIAC REGENERATION THROUGH INDUCTION OF CARDIAC MYOCYTE PROLIFERATION
#60PHARMACEUTICAL COMPOUND FOR PREVENTION OR TREATMENT OF LIVER FIBROSIS
#61ALU SINES OF THE MIR-498(46) CISTRON MEDIATE INTRINSIC INTERFERON AND ANTIVIRAL RESPONSE IN HUMAN PLACENTA
#62DELIVERING GENES TO THE BRAIN ENDOTHELIUM TO TREAT LYSOSOMAL STORAGE DISORDER-DERIVED NEUROPATHOLOGY
#63VIRAL VECTOR PRODUCTION
#64USE OF CONJUGATES OF MICRORNA AND CARDIAC TARGETING PEPTIDES FOR TREATING HEART FAILURE
#655-HALOURACIL-MODIFIED MICRORNAS AND THEIR USE IN THE TREATMENT OF CANCER
#66GENETIC SEQUENCE-CARBOHYDRATE CONJUGATES FOR ENHANCED LIVER- AND KIDNEY-SPECIFIC TARGETING
#67METHOD FOR PREPARING REASSORTANT ROTAVIRUS
#68METHOD FOR REPAIRING HAIR CYCLE-RELATED GENES AND METHOD FOR TREATING HAIR CYCLE-RELATED DISEASES USING MIR-520D-5P
#69APPLICATION OF COMPOUND OR TRADITIONAL CHINESE MEDICINE EXTRACT IN PREPARATION OF NUCLEIC ACID DELIVERY AGENT AND RELATED PRODUCTS THEREOF
#70COMPOSITIONS AND THERAPEUTIC METHODS OF MICRORNA GENE DELIVERY
#71COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#72PRODUCTS AND METHODS FOR TREATING DISEASES OR CONDITIONS ASSOCIATED WITH MUTANT OR PATHOGENIC KCNQ3 EXPRESSION
#73METHOD AND MEANS TO DELIVER miRNA TO TARGET CELLS
#74COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#75COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#76STEM CELL-DERIVED EXOSOMES FOR THE TREATMENT OF CORNEAL SCARRING
#77MODIFIED AAV CONSTRUCTS AND USES THEREOF
#78RNAS TARGETING ACTIVIN A SUBUNITS
#795-HALOURACIL-MODIFIED MICRORNAS AND THEIR USE IN THE TREATMENT OF CANCER
#80AAV VECTORS FOR RETINAL AND CNS GENE THERAPY
#81AAV VECTORS ENCODING SOD1-TARGETING ARTIFICIAL MIRNAS (AMI-RNA)
#82FLEXIBLE RNA SCAFFOLDING FOR REPROGRAMMABLE COMBINATORIAL RNAi ADMINISTRATION
#83IMPROVED PROTEIN PRODUCTION USING miRNA TECHNOLOGY
#84SEQUENCE DETERMINANTS OF DSRNA PROCESSING BY DICER
#85METHODS FOR EVALUATION OF EXTRACELLULAR VESICLES
#86COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#87NOVEL LIPIDS BASED ON OLIGO-y-GLUTAMIC ACID DERIVATIVES AND LIPID NANOPARTICLES CONTAINING THE SAME, AND USES THEREOF
#88SMALL RNA DRUG FOR INHIBITING ACTIVITY OF CANCER CELLS
#89SMALL RNA AND USE THEREOF IN TREATMENT OF HYPERLIPIDEMIA
#90TRANSGENE CASSETTES DESIGNED TO EXPRESS A HUMAN MECP2 GENE
#91COMPOSITIONS FOR DRG-SPECIFIC REDUCTION OF TRANSGENE EXPRESSION
#92DEFORMABLE NANO-SCALE VEHICLES (DNVS) FOR TRANS-BLOOD BRAIN BARRIER, TRANS-MUCOSAL, AND TRANSDERMAL DRUG DELIVERY
#93MIRNA COMBINATION FOR THE PREVENTION AND TREATMENT OF CANCER
#94COMPOSITION FOR WOUND TREATMENT COMPRISING STEM CELL-DERIVED EXTRACELLULAR VESICLES WITH ENHANCED EFFICACY
#95COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#96COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#97METHODS AND COMPOSITIONS FOR TREATING INFLAMMATORY CONDITIONS ASSOCIATED WITH INFECTIOUS DISEASE
#98SYNAPTOSOMAL MICRO RNAS AND SYNAPSE FUNCTIONS IN ALZHEIMER'S DISEASE
#99EXTRACELLULAR VESICLE SECRETION BOOSTER FOR BOOSTING EXTRACELLULAR VESICLE SECRETION, AND USE THEREOF
#100COMPOSITION AND METHOD FOR TREATING LUNG DISEASES
#101MICRORNA SYSTEM
#102COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#103COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#104COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#105COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#106COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#107COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#108COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#109COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#110COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#111COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#112COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#113COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#114COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#115COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#116IMPROVED CHIMERIC AND ENGINEERED SCAFFOLDS AND CLUSTERS OF MULTIPLEXED INHIBITORY RNA
#117COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#118COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#119COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#120COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#121COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#122COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#123COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#124COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#125EXOSOME THERAPY AND PROCESS TO IMPROVE FORMULATION AND PRODUCTION
#126PHARMACEUTICAL USE OF FAM19A5 INVOLVED IN REGULATING GLIOGENESIS
#127MATRIX BOUND NANOVESICLES AND THEIR USE
#128COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#129OLIGONUCLEOTIDE INTERFERENCE TREATMENTS OF PROSTATE CANCER
#130COMPOSITIONS AND METHODS FOR DELIVERING THERAPEUTICS TO THE HEART
#131METHODS AND COMPOSITIONS FOR TREATING ATHEROSCLEROSIS
#132GENE SILENCING BY RECOMBINANT AAV-AMIRNA IN ALEXANDER DISEASE
#133USING INFECTIOUS NUCLEIC ACID TO TREAT CANCER
#134COMPOSITIONS AND METHODS FOR MUSCLE DISORDERS
#135METHODS AND COMPOSITIONS FOR TRANSDUCING LYMPHOCYTES AND REGULATING THE ACTIVITY THEREOF
#136VECTORS COMBINING ANTI-SICKLING BETA-AS3-GLOBIN WITH ANTI BCEL11A SHRNAMIR TO TREAT BETA-HEMOGLOBINOPATHIES
#137PRODUCTION OF VIRAL VECTORS
#138Use of Trinucleotide Repeat RNAs To Treat Cancer
#139Process to Inhibit or Eliminate Eosinophilic Diseases of the Airway and Related Conditions
#140COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#141INITIALIZATION AGENT AND KIT FOR INITIALIZING BLOOD CELLS DERIVED FROM PERIPHERAL BLOOD, AND METHOD FOR INITIALIZING THE SAME
#142PHARMACEUTICAL COMPOSITION CONTAINING miR-140 AND METHOD FOR PRODUCING SAME
#143Compositions and Methods for Treatment of Liver Disease
#144ADENO-ASSOCIATED VIRUS VECTORS FOR NUCLEIC ACID DELIVERY ACROSS RETINAL REGIONS
#145Lipid Based Nanoparticles for Targeted Gene Delivery to the Brain
#146COMPOSITIONS AND METHODS FOR RECOMBINANT AAV PRODUCTION
#147ADENO-ASSOCIATED VIRUS VECTORS FOR NUCLEIC ACID DELIVERY TO RETINAL GANGLION CELLS AND/OR RETINAL PIGMENT EPITHELIUM CELLS
#148COMPOUNDS AND COMPOSITIONS INCLUDING PHOSPHOROTHIOATED OLIGODEOXYNUCLEOTIDE, AND METHODS OF USE THEREOF
#149ARTIFICIAL microRNAs TARGETING TAU
#150MIR-142 COMPOUNDS AND USES THEREOF
#151IMMUNOTHERAPEUTIC CONSTRUCTS AND METHODS OF THEIR USE
#152GENE EXPRESSION REGULATOR, AGENT FOR PREVENTING OR TREATING ALZHEIMER'S DISEASE AND METHOD FOR IMPROVING DEMENTIA
#153LIPID PARTICLE, COMPOSITION CONTAINING LIPID PARTICLE, KIT CONTAINING LIPID PARTICLE, AND ACTIVE AGENT DELIVERY METHOD USING LIPID PARTICLE
#154MICRORNAS FROM FORSYTHIAE FRUCTUS-ASTRAGALI RADIX COMPOUND TRADITIONAL CHINESE MEDICINE DECOCTION AS WELL AS PREPARATION METHOD AND USE THEREOF
#155METHODS OF TREATING OSMIDROSIS
#156PYK2 INHIBITION MODULATES IMMUNE CELL FUNCTION
#157ACTIVE TARGETING MICRORNA OLIGONUCLEOTIDE THERAPEUTICS FOR THE TREATMENT OF CARDIO-METABOLIC DISEASES
#158NON-INTEGRATING VIRAL DELIVERY SYSTEM AND METHODS RELATED THERETO
#159COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#160SMALL RNA-BASED DRUG, PREPARATION AND USE THEREOF IN PROPHYLAXIS AND/OR TREATMENT OF CARDIOMYOPATHY
#161Treatments of Disorders of Myelin
#162GENE THERAPEUTICS FOR TREATING BONE DISORDERS
#163ULTRASOUND RESPONSIVE LIPID NANOPARTICLE CARRYING GENES AND CELL MEMBRANE, ITS PREPARATION METHOD AND APPLICATION
#164COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#165COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#166COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#167COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#168COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#169COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#170COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#171COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#172INTRON FRAGMENTS
#173COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#174COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#175COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#176COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#177COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#178COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#179COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#180COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#181COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#182COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#183COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#184COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#185COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#186COMPOSITION FOR REGULATING PRODUCTION OF INTERFERING RIBONUCLEIC ACID
#187Promotion of Cardiomyocyte Proliferation and Regenerative Treatment of the Heart by Inhibition of microRNA-128
#188ACTIVATION OF NONCODING HOST GENE LOCI
#189USE OF miR-34b IN REGULATING LIPID METABOLISM OF SHANDONG BLACK CATTLE
#190COMPOSITION FOR PREVENTION OR TREATMENT OF LIVER CANCER, COMPRISING MODIFIED RT-LET7 AS ACTIVE INGREDIENT
#191METHODS OF GENERATING A POPULATION OF NEURONS FROM HUMAN GLIAL PROGENITOR CELLS AND GENETIC CONSTRUCTS FOR CARRYING OUT SUCH METHODS
#192ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY
#193ONCOLYTIC VIRUSES AND METHODS OF USE
#194GENETICALLY-MODIFIED IMMUNE CELLS COMPRISING A MICRORNA-ADAPTED SHRNA (SHRNAMIR)
#195EDIBLE PLANT-DERIVED NANOPARTICLES FOR REGULATION OF GUT MICROBIOTA
#196COMPOSITIONS AND METHODS FOR TREATING CONDITIONS RELATED TO CELLULAR SENESCENCE
#197T CELLS WITH IMPROVED FUNCTIONALITY
#198METHOD FOR PRODUCING STERILIZED MALE INDIVIDUALS OF MARINE FISH, METHOD FOR PREVENTING REPRODUCTION OF MARINE FISH, AND STERILIZED MALE INDIVIDUALS OF MARINE FISH
#199COMPOSITIONS AND METHODS TO RESTORE PATERNAL UBE3A GENE EXPRESSION IN HUMAN ANGELMAN SYNDROME
#200Methods and Compositions for Avoiding Off-Target Effects
#201METHODS TO ACCELERATE STEM CELL DIFFERENTIATION TO CARDIOMYOCYTES
#202RECOMBINANT OPTIMIZED MECP2 CASSETTES AND METHODS FOR TREATING RETT SYNDROME AND RELATED DISORDERS
#203DENDRIMER CONJUGATES OF SMALL MOLECULE BIOLOGICS FOR INTRACELLULAR DELIVERY
#204NANOPARTICLE VECTOR FOR RNA SELF-DELIVERY, AND PREPARATION METHOD THEREFOR AND USE THEREOF
#205COMPOSITIONS AND PROCESSES FOR TARGETED DELIVERY, EXPRESSION AND MODULATION OF CODING RIBONUCLEIC ACIDS IN TISSUE
#206METHOD FOR REDUCING HEPATIC TRIGLYCERIDES
#207COMPOSITIONS AND METHODS FOR TREATING CANCERS
#208COMPOSITIONS AND METHODS FOR ENGINEERING STABLE TREGS
#209ANISAMIDE-CONTAINING LIPIDS AND COMPOSITIONS AND METHODS OF USE THEREOF
#210HIV PRE-IMMUNIZATION AND IMMUNOTHERAPY
#211METHODS OF PRODUCING CELLS RESISTANT TO HIV INFECTION
#212MODULATORY POLYNUCLEOTIDES
#213AGENT AND PHARMACEUTICAL COMPOSITION FOR TREATING AND/OR PREVENTING JOINT DISEASE
#214LIPID NANOPARTICLE (LNP) COMPOSITIONS FOR BRAIN-SELECTIVE CARGO DELIVERY, AND METHODS OF USE THEREOF
#215METHODS FOR ENHANCING THERAPEUTIC EFFICACY OF ISOLATED CELLS FOR CELL THERAPY
#216COMPOSITIONS AND METHODS RELATING TO PEDIATRIC NEUROMUSCULAR DISEASES AND NEUROGENERATIVE DISORDERS
#217RIG1 Inhibition and Therapeutic Viral Protein Expression
#218COMPOSITIONS FOR TREATING NEUROLOGICAL DISEASE
#219MIRNA CIRCUITS FOR CONTROLLED GENE EXPRESSION
#220METHODS AND MODIFICATIONS THAT PRODUCE ssRNAi COMPOUNDS WITH ENHANCED ACTIVITY, POTENCY AND DURATION OF EFFECT
#221CONJUGATION OF LIPOPHILIC ALBUMIN-BINDING MOIETY TO RNA FOR IMPROVED CARRIER-FREE IN VIVO PHARMACOKINETICS AND GENE SILENCING
#222MICRORNA-198 AS A TUMOR SUPPRESSOR IN OVARIAN CANCER
#223METHODS OF TREATING OR PREVENTING PREMATURE OVARIAN INSUFFICIENCY, POLYCYSTIC OVARY SYNDROME, OR INFERTILITY USING EXOSOMES OR MESENCHYMAL STEM CELLS
#224ADENO-ASSOCIATED VIRUS VECTORS
#225NONVIRAL VECTORS FOR GENE THERAPY
#226COMPOSITIONS COMPRISING THERAPEUTIC NUCLEIC ACID AND TARGETED SAPONIN FOR THE TREATMENT OF MUSCLE-WASTING DISORDERS
#227m6A mRNA MODIFICATION IN CANCER TREATMENT
#228HIF1A OR GLUT1 INHIBITION IN INFLAMMATORY SKIN DISEASES
#229COMPOSITIONS AND METHODS FOR MODULATING NEURONAL EXCITABILITY AND MOTOR BEHAVIOR
#230TARGETING THE YTHDF1/ARHGEF2 AXIS FOR CANCER TREATMENT
#231NOVEL CATIONIC LIPID COMPOUNDS
#232Composition for Administration of Double-Stranded Oligonucleotide Structures Using Ultrasonic Nebulizer for Prevention or Treatment of Respiratory Viral Infection Including COVID-19, Pulmonary Fibrosis Caused by Viral Infection, or Respiratory Diseases
#233DEGRADABLE LIPID COMPOUND FOR ACTIVE MOLECULE DELIVERY AND NANOCOMPLEX THEREOF
#234IONIZABLE LIPIDS FOR MULTIPLE ORGAN TARGETING
#235Compositions and Methods for Treatment of Ocular Disease Associated with Angiogenesis
#236COMPOSITION FOR PROMOTING MIGRATION OF ADULT STEM CELLS USING INCREASE IN EXPRESSION OF MIRNA
#237Exosomes for treating glioblastoma multiforme and manufacturing method thereof
#238Compositions And Methods Targeting G12 Signaling For Bronchodilator Therapy
#239NON-CODING RNA-MEDIATED NEUROLOGICAL DISEASE TREATMENT
#240METHODS AND MOLECULES FOR RNA INTERFERENCE (RNAi)
#241COMPOSITIONS AND METHODS FOR REGULATING PRODUCTION OF AN ANTIBODY LIKE PROTEIN AND RIBONUCLEIC ACID
#242METHODS AND COMPOSITIONS FOR INHIBITING DETOXIFICATION RESPONSE
#243Mammalian ATG8 Proteins and ATG9A Direct Sealing of Autophagosomal Membranes
#244NON-INTEGRATING VIRAL DELIVERY SYSTEM AND METHODS RELATED THERETO
#245CONSTRUCTS COMPRISING TANDEM MICRORNA-ADAPTED SHORT HAIRPIN RNA (SHMIR) FOR INCREASING FETAL HEMOGLOBIN
#246GLYCAN CONJUGATE COMPOSITIONS AND METHODS
#247Novel Compositions for Conjugating Oligonucleotides and Carbohydrates
#248SYSTEMS AND METHODS FOR TRANS-MODULATION OF IMMUNE CELLS BY GENETIC MANIPULATION OF IMMUNE REGULATORY GENES
#249DNA COMPOSITIONS AND RELATED METHODS
#250Compositions and Methods of Generating Novel amiRNA
#251USE OF MIRNA-2911 MOLECULE AS NUCLEIC ACID STABILIZER
#252MESENCHYMAL STROMAL CELL DELIVERY VIA CARDIOPULMONARY BYPASS PROVIDES NEUROPROTECTION
#253ANTITUMORAL COMPOSITION
#254TREATMENT FOR INFLAMMATORY DISEASE
#255MODIFIED U6 PROMOTER SYSTEM FOR TISSUE SPECIFIC EXPRESSION
#256TARGETING LIGAND AND USE THEREOF
#257LIPID-BASED CONJUGATES FOR SYSTEMIC, CENTRAL NERVOUS SYSTEM, PERIPHERAL NERVOUS SYSTEM, AND OCULAR DELIVERY
#258RNAI THERAPY FOR APBD AND LAFORA DISEASE
#259GENE THERAPY FOR NEURODEGENERATIVE DISORDERS
#260COMPOSITIONS OF HUMAN HEART DERIVED EXTRACELLULAR VESICLES AND USES THEREOF
#261TARGETING APOE ENHANCES T-CELL KILLING IN CANCER IMMUNOTHERAPY
#262ANTISENSE TRANSFER VECTORS AND METHODS OF USE THEREOF
#263Engineered Exosome for Treating Hypertrophic Scar (Hts), and Preparation Method and Use Thereof
#264BLOCK COPOLYMERS AND USES THEREOF
#265Lipid nanoparticle compositions and uses thereof
#266METHODS FOR TREATING CELLULAR INFLAMMATION INDUCED BY AFB1
#267COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING LIVER FIBROSIS
#268COMPOSITION FOR TREATING MUSCLE LOSS-RELATED DISEASES COMPRISING EXOSOMES DERIVED FROM TONSIL MESENCHYMAL STEM CELLS
#269METHODS AND COMPOSITIONS FOR TREATING EPILEPSY
#270INHIBITION OF GLUTARYL-COA DEHYDROGENASE FOR THE TREATMENT OF MELANOMA
#271METHODS OF MODULATING RNA TRANSLATION
#272miRNA REPROGRAMMING OF SMOOTH MUSCLE CELLS INTO ENDOTHELIAL CELLS
#273AN ANTI-INFLAMMATORY COMPOSITION AND A METHOD OF OBTAINING THE SAME
#274GENE EDITING FOR HEMOPHILIA A WITH IMPROVED FACTOR VIII EXPRESSION
#275COMPOSITIONS AND METHODS FOR TREATING HUNTINGTON'S DISEASE
#276METHOD OF TREATING PANCREATIC CANCER
#277MICRORNA TARGETING REGENERATIVE TREATMENTS FOR HEART FAILURE
#278BIOACTIVE RENAL CELLS
#279MODIFIED AAV CONSTRUCTS AND USES THEREOF
#280CELL-DERIVED NANOVESICLES FOR IN VIVO TRANSPORT AND DELIVERY OF THERAPEUTIC MATERIALS
#281ENGINEERED CIRCULAR RNA CIRCMIR-29B AND USE THEREOF IN PREPARATION OF MEDICINE FOR TREATING MUSCLE ATROPHY
#282MICRORNA-541-3P AS A THERAPEUTIC AGENT AS WELL AS ZNF101 AND CASZ1 AS THERAPEUTIC TARGETS TO LOWER PLASMA LDL-C, INCREASE PLASMA HDL-C, AND REDUCE ATHEROSCLEROSIS
#283PRODUCTS AND METHODS FOR MYELIN PROTEIN ZERO SILENCING AND TREATING CMT1B DISEASE
#284PROGRAMMABLE CONDITIONAL SIRNAS AND USES THEREOF
#285METHODS FOR IMPROVING RELAXATION OF STRIATED MYOCYTES
#286COMPOSITIONS AND METHODS OF TREATING FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
#287RNAi induced C9ORF72 suppression for the treatment of ALS/FTD
#288MLK-Regulated microRNAs in Angiogenesis and Tumor Development
#289CATIONIC POLYMERS
#290STAUFEN1 REGULATING AGENTS AND ASSOCIATED METHODS
#291Utilization of Micro-RNA for Downregulation of Cytotoxic Transgene Expression by Modified Vaccinia Virus Ankara (MVA)
#292MICRORNA-29 COMPOUNDS, COMPOSITIONS AND USES IN THERAPY
#293GENE THERAPY CONSTRUCT FOR TREATING POMPE DISEASE, PHARMACEUTICAL COMPOSITION, AND METHOD
#294LIPOSOMAL PARTICLES, METHODS OF MAKING SAME AND USES THEREOF
#295PHARMACEUTICAL COMPOSITION FOR PREVENTING OR TREATING COLON CANCER INCLUDING EXTRACELLULAR VESICLES LOADED WITH MACC1 INHIBITOR AS ACTIVE INGREDIENT
#296USE OF microRNA MIMICS TO INHIBIT OR TREAT LIVER DISEASE
#297SELECTIVE INHIBITORS OF ROCK2 FOR THE TREATMENT OF MUSCULAR DYSTROPHY
#298NUCLEIC ACID MOLECULE AND USE OF THE NUCLEIC ACID MOLECULE IN THERAPY OF DISEASES INDUCED BY EXPANSION OF TRINUCLEOTIDE CAG REPEATS
#299METHOD FOR PRODUCING HIGHLY PROLIFERATIVE CELL, AND HIGHLY PROLIFERATIVE CELL AND USE THEREOF
#300COMPOSITION AND METHOD TO TREAT CACHEXIA