109146 ⎘
Structure or type of the nucleic acid; Type of nucleic acid interfering N.A. MicroRNAs, miRNAs
TREATMENT AND DIAGNOSIS OF IMMUNE DISORDERS RELATING TO ABERRANT IMMUNE CELLS
#302Cationic Polymeric Nanoparticles and Their Uses in Treating Diseases
#303SPINK1 AS A TARGET FOR THERAPEUTIC INTERVENTION IN LUNG DISEASES
#304METHODS FOR TREATING SICKLE CELL DISEASE OR BETA THALASSEMIA USING COMPLEMENT ALTERNATIVE PATHWAY INHIBITORS
#305OPTIMIZING T CELL DIFFERENTIATION STATE WITH MICRORNAS
#306Riboswitch modulated gene therapy for retinal diseases
#307COMPOSITIONS AND METHODS FOR TARGETED DELIVERY OF THERAPEUTIC AND/OR DIAGNOSTIC SPECIES
#308COMPOSITIONS AND METHODS FOR CELLULAR REPROGRAMMING USING CIRCULAR RNA
#309Therapeutic Compounds for Inhibiting and Reducing the Expression of Cell Surface Proteins
#310COMPOSITIONS AND METHODS FOR TREATMENT OF GAUCHER DISEASE
#311RECOMBINANT VIRUS PRODUCTS AND METHODS FOR INHIBITION OF EXPRESSION OF DUX4
#312MESENCHYMAL STEM CELL-DERIVED MICRORIBONUCLEIC ACID-MEDIATED TREATMENTS FOR THE PREVENTION AND TARGETED TREATMENT OF CANCER AND OTHER DISORDERS
#313PRODUCTS AND METHODS FOR INHIBITION OF EXPRESSION OF PERIPHERAL MYELIN PROTEIN-22
#314COMPOSITIONS AND METHODS FOR ENHANCING THE THERAPEUTIC POTENTIAL OF STEM CELLS
#315ANTI-FIBROSIS PHARMACEUTICAL COMPOSITION AND APPLICATION THEREOF
#316METHOD FOR SILENCING GENES
#317METHODS AND COMPOSITIONS FOR SENSITIZATION OF TUMOR CELLS TO IMMUNE THERAPY
#318METHODS AND COMPOSITIONS TO DIAGNOSE AND TREAT TAUOPATHIES UTILIZING TRANSCRIPT VARIANTS OF PSEN2
#319COMBINATION THERAPEUTICS FOR TREATMENT OF PROLIFERATIVE DISORDERS
#320COMPOSITIONS AND METHODS FOR THE GENERATION OF NEURONS AND USES THEREOF
#321METHODS AND COMPOSITIONS FOR CANCER TREATMENT BY TARGETING AXL SIGNALING
#322MICRORNA 195 COMPOSITIONS AND METHODS FOR TREATING COGNITIVE IMPAIRMENT
#323METHOD FOR IMPROVING GENETIC ENGINEERING OF ADOPTIVE CELL THERAPIES
#324AGENTS, COMPOSITIONS, AND METHODS FOR THE TREATMENT OF HYPOXIA AND ISCHEMIA-RELATED DISORDERS
#325RNA-ONLY DERIVED ORTHOMYXOVIRUSES AND ASSOCIATED VECTORS AND USES THEREOF
#326PLANT REGULATORY ELEMENTS AND USES THEREOF
#327COMPOSITIONS AND METHODS FOR DELIVERING THERAPEUTIC OLIGONUCLEOTIDES TO THE CENTRAL NERVOUS SYSTEM
#328NANO COMPLEX FOR TARGETED REPAIRING OF NEUROVASCULAR LESION, AND PREPARATION AND USE THEREOF
#329COMPOSITIONS AND METHODS FOR CELL TYPE-SPECIFIC GENE EXPRESSION IN THE INNER EAR
#330HIGHLY STABLE AND SPECIFIC MOLECULAR BEACONS ENCAPSULATED IN CATIONIC LIPOPLEX NANOPARTICLES AND APPLICATION THEREOF
#331Methods and Compositions for Managing Vascular Conditions Using miR-483 Mimics and HIF1alpha Pathway Inhibitors
#332MIRNA INHIBITORS FOR PREVENTING AND TREATING ANEURYSMS, HYPERTENSION, ARDS AND OTHER DISEASES ASSOCIATED WITH ENDOTHELIAL DYSFUNCTION
#333EXTRACELLULAR VESICLE-ENRICHED SECRETOME COMPOSITION DERIVED FROM INDUCED PLURIPOTENT STEM CELL DERIVED-MICROGLIA AND METHODS OF USE THEREOF
#334METHODS AND COMPOSITIONS FOR TAU REDUCTION GENE THERAPY
#335COMPOSITION FOR TREATING METASTATIC SOLID CANCER, COMPRISING TSG6 INHIBITOR
#336EXPRESSION-INDUCING AGENT FOR CLASS I GLUCOSE TRANSPORTER (GLUT), AND MEDICINAL COMPOSITION AND FOOD COMPOSITION USING SAME
#337MODIFIED NUCLEIC ACID INHIBITING MICRO RNA, AND USE THEREOF
#338FATTY ACID CONJUGATES OF NUCLEIC ACIDS
#339miRNA Switches for RNA-Triggered Control of RNA Interference
#340METHODS OF USING USP15 INHIBITORS
#341PRODUCTION OF THERAPEUTIC MESENCHYMAL STEM CELL-DERIVED EXOSOMES
#342COMPOSITIONS AND THERAPEUTIC METHODS OF MICRORNA GENE DELIVERY
#343CANCER TREATMENT BY TARGETING PROTEINS OR INTERACTIONS OF EPHRINB-RGS3-KIF20A-SEPT7 AXIS
#344MICRORNAS FOR CARDIAC REGENERATION THROUGH INDUCTION OF CARDIAC MYOCYTE PROLIFERATION
#345RAAV-BASED COMPOSITIONS AND METHODS
#346HIV PRE-IMMUNIZATION AND IMMUNOTHERAPY
#347IMPROVED NUCLEIC ACID SEQUENCE FOR CELL TYPE SPECIFIC EXPRESSION
#348MICRORNA COMPOSITIONS AND METHODS OF USE THEREOF FOR THE TREATMENT OF NERVOUS SYSTEM DYSFUNCTION
#349NUCLEIC ACID DELIVERY SYSTEM AND APPLICATION THEREOF
#350ELECTROPORATION, DEVELOPMENTALLY-ACTIVATED CELLS, PLURIPOTENT-LIKE CELLS, CELL REPROGRAMMING AND REGENERATIVE MEDICINE
#351TM4SF19 INHIBITOR AND USES THEREOF
#352Compositions and Methods for Treatment of Ocular Disease Associated with Angiogenesis
#353MIR200C-EPCAM AXIS REPROGRAMED IMMUNE CELLS FOR ENHANCED ANTI-TUMOR FUNCTION
#354USE OF MICRORNAS IN THE TREATMENT OF FIBROSIS
#355COMPOSITION FOR TREATING OSTEOARTHRITIS
#356CHLORELLA-BASED PRODUCTION OF EXTRACELLULAR VESICLE-EMBEDDED SMALL RNAs FOR PROPHYLACTIC OR THERAPEUTIC APPLICATIONS
#357EXTRACELLULAR VESICLES WITH TARGETING MOIETY
#358COMPOSITIONS AND METHODS FOR TARGETED DELIVERY TO CELLS
#359METHODS OF MODULATING ALK
#360INHIBITORY NUCLEIC ACIDS FOR FACTOR H FAMILY PROTEINS
#361METHOD FOR IMPROVING DIABETIC WOUND HEALING USING MIR-200B
#362TREATING CANCER
#363UMBILICAL CORD MESENCHYMAL CELL EXTRACELLULAR VESICLES FOR THE TREATMENT OF OSTEOARTICULAR AND AUTOIMMUNE DISEASES
#364TARGETING PIEZO1 TO TREAT INHERITED AND AGE-RELATED MACULAR DEGENERATIONS
#365ORAL DELIVERY OF OLIGONUCLEOTIDES
#366MICRORNA-DEPENDENT MRNA SWITCHES FOR TISSUE-SPECIFIC MRNA-BASED THERAPIES
#367METHOD AND COMPOSITIONS FOR PREVENTING TUMOR DEVELOPMENT AND METASTASIS
#368Allogeneic Cartilage Regeneration
#369NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF A TARGET GENE COMPRISING PHOSPHORODITHIOATE LINKAGES
#370GENE THERAPY FOR INFLAMMATORY CONDITIONS
#371ORAL DELIVERY OF NANOPARTICLES FOR KIDNEY DISEASE
#372SYSTEMS AND METHODS FOR EXOSOME DELIVERY OF MICRORNAS FOR CELLULAR REPROGRAMMING
#373TRANSGENE CASSETTES DESIGNED TO EXPRESS A HUMAN MECP2 GENE
#374TREATMENT OF TUMORS WITH MIRNA TARGETING CDK4/CDK6
#375NOVEL PEPTIDE-OLIGONUCLEOTIDE CONJUGATE AND USE THEREOF
#376USE OF MICRORNA-146A AND NANOCERIA CONJUGATE TO IMPROVE WOUND HEALING AND PROMOTE TISSUE REGENERATION
#377MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes
#378CATIONIC LIPIDS AND USES THEREOF
#379GENOMIC INSULATOR ELEMENTS AND USES THEREOF
#380MICRORNA BLOCKADE FOR THE TREATMENT OF DISEASE
#381OLIGONUCLEOTIDE THERAPEUTICS AND APPLICATION THEREOF
#382REPROGRAMMING OF CELLS AND USES THEREOF
#383ENGINEERED CHIMERIC FUSION PROTEIN COMPOSITIONS AND METHODS OF USE THEREOF
#384VIRAL EXPRESSION CONSTRUCT COMPRISING A FIBROBLAST GROWTH FACTOR 21 (FGF21) CODING SEQUENCE
#385IMMUNOFUNCTIONAL CARRIER, METHODS OF USES, AND COMPOSITION MATTERS AS AN ANTITUMOR IMMUNOTHERAPY
#386COMPOSITIONS AND METHODS FOR TREATING HYPERCHOLESTEROLEMIA
#387RELIABLE IDENTIFICATION OF REGIONS ('A SITES') IN COMPLEX RNA MOLECULES THAT ARE ACCESSIBLE TO NUCLEIC ACIDS OR COMPLEXES OF NUCLEIC ACIDS WITH ENDONUCLEASES
#388METHOD FOR TREATING LUNG INJURY
#389CANCER THERAPY
#390METHODS AND COMPOSITIONS FOR REJUVENATING CNS GLIAL POPULATIONS BY SUPPRESION OF TRANSCRIPTION FACTORS
#391METHODS OF TREATING OSMIDROSIS
#392TEMPLATE DIRECTED IMMUNOMODULATION FOR CANCER THERAPY
#393PHARMACEUTICAL USE OF FAM19A5 INVOLVED IN REGULATING GLIOGENESIS
#394RIBOSWITCH MODULATED GENE THERAPY FOR RETINAL DISEASES
#395METHOD OF TREATING FATTY LIVER DISEASE
#396USE OF miRNA408 IN REGULATION OF CADMIUM ACCUMULATION IN CROP
#397IN VITRO AND IN VIVO INTRACELLULAR DELIVERY OF SIRNA VIA SELF-ASSEMBLED NANOPIECES
#398MERCAPTOPURINE-MODIFIED MIRNA FOR TREATING CANCER
#399TARGETED INHIBITION USING ENGINEERED OLIGONUCLEOTIDES
#400GENERATION OF NOVEL CRISPR GENOME EDITING AGENTS USING COMBINATORIAL CHEMISTRY
#401MICRORNA COMPOSITIONS AND METHODS OF USE THEREOF FOR THE TREATMENT OF NERVOUS SYSTEM DYSFUNCTION
#402Synergistic Genome-Nonintegrating Reprogramming by Micrornas and Transcription Factors
#403Compositions and methods of treating facioscapulohumeral muscular dystrophy
#404TM4SF19 INHIBITOR AND USES THEREOF
#405Compositions and Methods for Treatment of Ocular Disease Associated with Angiogenesis
#406MIR200C-EPCAM AXIS REPROGRAMED IMMUNE CELLS FOR ENHANCED ANTI-TUMOR FUNCTION
#407USE OF MICRORNAS IN THE TREATMENT OF FIBROSIS
#408INHIBITION OF EXPANSION AND FUNCTION OF PATHOGENIC AGE-ASSOCIATED B CELLS AND USE FOR THE PREVENTION AND TREATMENT OF AUTOIMMUNE DISEASE
#409Compositions and methods of treating facioscapulohumeral muscular dystrophy
#410METHOD FOR MODULATING PLANT PROCESSES
#411USE OF MIRNA-485 INHIBITOR TO REGULATE PSD95, SYNAPTOPHYSIN, AND CASPASE-3 EXPRESSION
#412METHODS OF MANUFACTURING GENETICALLY-MODIFIED LYMPHOCYTES
#413Methods for Treatment of Alport Syndrome
#414PRE-IMMUNIZATION AND IMMUNOTHERAPY
#415Novel Structurally Designed shRNAs
#416ARTIFICIALLY SYNTHESIZED SPHINGOSINE DERIVATIVE LIPOID MONOMER AND USE OF SAME FOR DELIVERING NUCLEIC ACID
#417MODIFICATIONS OF MAMMALIAN CELLS USING ARTIFICIAL MICRO-RNA TO ALTER THEIR PROPERTIES AND THE COMPOSITIONS OF THEIR PRODUCTS
#418MIR-7-5P MIMIC FOR INHIBITING MIGRATION AND INVASION OF BREAST CANCER, SCREENING METHOD AND APPLICATION THEREOF
#419COMPOSITIONS AND METHODS FOR TREATING DISEASE ASSOCIATED WITH DUX4 OVEREXPRESSION
#420VECTORS COMPRISING STUFFER POLYNUCLEOTIDE SEQUENCES
#421METHODS OF MEAT PRODUCTION BY IN VITRO CELL CULTIVATION
#422SYNERGISTIC EFFECT OF SMN1 AND MIR-23A IN TREATING SPINAL MUSCULAR ATROPHY
#423METHODS OF MODULATING NEURONAL AND OLIGODENDROCYTE SURVIVAL
#424MODULATION OF CHITINASE PROTEIN EXPRESSION
#425AAV TREATMENT OF HUNTINGTON’S DISEASE
#426MIRNA COMPOSITION COMPRISING 11 SPECIFIC MIRNAS AND ITS USE IN THE TREATMENT OF CANCER
#427DRUG DELIVERY COMPOSITION, METHOD FOR PRODUCING SAME AND USE THEREOF
#428SINGLE-STRANDED OLIGONUCLEOTIDE
#429GENETICALLY-MODIFIED IMMUNE CELLS COMPRISING A MICRORNA-ADAPTED SHRNA (SHRNAMIR)
#430TOXIC RNAi ACTIVE SEED SEQUENCES FOR KILLING CANCER CELLS
#431DOUBLE-HELIX OLIGONUCLEOTIDE CONSTRUCT COMPRISING DOUBLE-STRANDED MIRNA AND USE THEREOF
#432RAAV-BASED COMPOSITIONS AND METHODS FOR TREATING AMYOTROPHIC LATERAL SCLEROSIS
#433TRIPLE FUNCTION ADENO-ASSOCIATED VIRUS (AAV)VECTORS FOR THE TREATMENT OF C9ORF72 ASSOCIATED DISEASES
#434COMPOSITIONS AND METHODS FOR TREATMENT OF CARDIAC DISEASES
#435PROTOPARVOVIRUS AND TETRAPARVOVIRUS COMPOSITIONS AND METHODS FOR GENE THERAPY
#436COMPOSITIONS AND METHODS FOR SILENCING KRAS
#437Method for Producing Naive Human IPS Cells From Somatic Cells
#438ANTISENSE OLIGONUCLEOTIDES AND THEIR USE FOR THE TREATMENT OF PAIN
#439COMPLEX FOR TREATING OPTIC NERVE DISEASE, AND PREPARATION METHOD THEREFOR AND USE THEREOF
#440Therapeutic agent targeted to receptor protein, test agent, antibody that binds to receptor protein, and screening method for molecularly targeted drugs
#441CARDIOMYOCYTE-DERIVED NUCLEIC ACID REGULATORY ELEMENTS AND METHODS AND USE THEREOF
#442VIRAL VECTOR PRODUCTION
#443COMPOSITIONS FOR FACILITATING MEMBRANE FUSION AND USES THEREOF
#444MICRORNA-BASED COMPOSITIONS AND METHODS USED IN DISEASE TREATMENT
#445Compositions and methods for regulating production of a fusion protein and ribonucleic acid
#446Modified ribonucleic acids and uses thereof
#447Methods of Treating of Spinal Stenosis and Ligamentum Flavum Hypertrophy
#448MODIFIED MIR-135, CONJUGATED FORM THEREOF, AND USES OF SAME
#449TARGETING MICRORNA TO REGULATE NATIVE GENE FUNCTION BY GENOME EDITING
#450Method for preparing compound or biological drug enhancing CNPase activity for treating heart diseases
#451CYTARABINE-MODIFIED miRNA FOR TREATING CANCER
#452VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF ILD, PF-ILD AND IPF
#453METHODS FOR ENHANCING THERAPEUTIC EFFICACY OF ISOLATED CELLS FOR CELL THERAPY
#454PMO-BASED UTROPHIN::LET-7C MIRNA SITE BLOCKING OLIGONUCLEOTIDES (SBOS) FOR TREATING DUCHENNE MUSCULAR DYSTROPHY (DMD)
#455COMPOSITIONS AND METHODS FOR THE DIAGNOSIS AND TREATMENT OF ITCH
#456DEVELOPMENT OF NOVEL GENE THERAPEUTICS FOR INFLAMMATION-INDUCED BONE LOSS
#457SELF-REGULATING AAV VECTORS FOR SAFE EXPRESSION OF MECP2 IN RETT SYNDROME
#458bZIP TRANSCRIPTION FACTORS REGULATE CONVERSION OF NICOTINE TO NORNICOTINE
#459VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF ILD, PF-ILD AND IPF
#460miRNA PROFILING COMPOSITIONS AND METHODS OF USE
#461MODIFIED RIBONUCLEIC ACIDS AND USES THEREOF
#462Oligonucleotides conjugated to oleic acid and uses thereof
#463VIRAL VECTORS AND NUCLEIC ACIDS FOR USE IN THE TREATMENT OF ILD, PF-ILD AND IPF
#464NOVEL EFFICACIOUS MICRORNA-30C ANALOGS REDUCE APOLIPOPROTEIN B SECRETION IN HUMAN LIVER CELLS
#465BIOENGINEERED WNT5A THERAPEUTICS FOR ADVANCED CANCERS
#466USE OF FcgammaRIII INHIBITOR IN PREPARATION OF MEDICAMENT FOR TREATING PULMONARY FIBROSIS
#467GENE THERAPY FOR ALZHEIMER'S DISEASE
#468EXOSOMAL LOADING USING HYDROPHOBICALLY MODIFIED OLIGONUCLEOTIDES
#469SELECTIVE RNA-MODULATING AGENTS
#470COMPOSITIONS AND METHODS OF TREATING HUNTINGTON'S DISEASE
#471EXOSOMES CONTAINING MIRNAS TARGETING HER2 SYNTHESIS AND PHARMACEUTICAL COMPOSITIONS
#472miRNA, and Derivative Thereof and Use Thereof
#473COMPOSITION FOR TREATING RETINAL OR CHOROIDAL DISEASES, CONTAINING ACTA2 INHIBITOR AS ACTIVE INGREDIENT
#474METHODS FOR PRODUCTION OF MSC-DERIVED EXOSOMES
#475PLATELETS AS DELIVERY AGENTS
#476STABLE TARGETED INTEGRATION
#4775-HALOURACIL-MODIFIED MICRORNAS AND THEIR USE IN THE TREATMENT OF CANCER
#478METHODS FOR TREATING NEUROLOGICAL DISEASE
#479METHOD FOR DIRECT REPROGRAMMING FROM SOMATIC CELLS INTO PANCREATIC BETA CELLS BY USING MICRORNA, AND DIFFERENTIATION COMPOSITION
#480HISTONE DEACETYLASE 6 (HDAC6) BIOMARKERS IN MULTIPLE MYELOMA
#481BIFUNCTIONAL LENTIVIRAL VECTORS ALLOWING THE BS-GLOBIN SILENCING AND EXPRESSION OF AN ANTI-SICKLING HBB AND USES THEREOF FOR GENE THERAPY OF SICKLE CELL DISEASE
#482Methods and compositions for transducing lymphocytes and regulating the activity thereof
#483METHODS AND COMPOSITIONS FOR THE ACTIVATION OF GAMMA-DELTA T-CELLS
#484Modifying the specificity of plant non-coding RNA molecules for silencing gene expression
#485Compounds and compositions including phosphorothioated oligodeoxynucleotide, and methods of use thereof
#486miR-3132 upregulation of the trail pathway and apoptotic activity in cancer cells
#487ELECTROPORATION, DEVELOPMENTALLY-ACTIVATED CELLS, PLURIPOTENT-LIKE CELLS, CELL REPROGRAMMING AND REGENERATIVE MEDICINE
#488Methods for therapeutic administration of messenger ribonucleic acid drugs
#489USE OF NOVEL MIRNA-BINDING SITE CASSETTES FOR ANTIGEN-PRESENTING CELL DETARGETING OF TRANSGENE EXPRESSION BY RAAV GENE THERAPY
#490TRANSGENE EXPRESSION SYSTEM
#491miR-17˜92 for Treatment or Protection Against Acute Kidney Injury
#492Genetic Construct
#493MODIFICATIONS OF MAMMALIAN CELLS USING ARTIFICIAL MICRO-RNA TO ALTER THEIR PROPERTIES AND THE COMPOSITIONS OF THEIR PRODUCTS
#494ARC-BASED CAPSIDS AND USES THEREOF
#495MICRORNA OLIGONUCLEOTIDE THERAPEUTICS FOR OVARIAN CANCER
#496COMPOSITIONS FOR DRG-SPECIFIC REDUCTION OF TRANSGENE EXPRESSION
#497COMPOSITIONS AND METHODS OF TREATMENT OF MUSCLE DISORDERS BY TARGETING H19X-ENCODED NON-CODING RNAS
#498RNAS for complement inhibition
#499REPEAT RNA AS BIOMARKERS OF TUMOR IMMUNE RESPONSE
#500NUTRITIONAL COMPOSITION COMPRISING MIR-3141
#501GENE THERAPEUTICS FOR FIBRODYSPLASIA OSSIFICANS PROGRESSIVA
#502TARGETING PEPTIDES FOR DIRECTING ADENO-ASSOCIATED VIRUSES (AAVs)
#503COMPOSITIONS AND METHODS FOR THE TREATMENT OF DISEASES BY ENHANCING ARGINASE 2 IN MACROPHAGES
#504MICRORNAS AND METHODS OF THEIR USE
#505Novel Replicase Cycling Reaction (RCR) and the Related SamRNA Designs Thereof
#506Targeted inhibition using engineered oligonucleotides
#507MODIFICATIONS OF MAMMALIAN CELLS USING ARTIFICIAL MICRO-RNA TO ALTER THEIR PROPERTIES AND THE COMPOSITIONS OF THEIR PRODUCTS
#508METHODS AND COMPOSITIONS OF BIOLOGICALLY ACTIVE AGENTS
#509MAGNETIC INORGANIC IRON-BASED NANOPARTICLES
#510TARGETED DELIVERY OF AN INHIBITOR OF MIR-21 TO MACROPHAGES FOR THE TREATMENT OF PULMONARY FIBROSIS
#511COMPOSITIONS AND METHODS FOR TREATING NEURODEGENERATIVE DISEASES
#512NUCLEIC ACID CONSTRUCTS FOR DELIVERING POLYNUCLEOTIDES INTO EXOSOMES
#513PHARMACEUTICAL COMPOSITIONS FOR TREATMENT OF MICRORNA RELATED DISEASES
#514Gene editing for hemophilia A with improved factor VIII expression
#515COMPOSITIONS COMPRISING CURONS AND USES THEREOF
#516MODIFYING THE SPECIFICITY OF PLANT NON-CODING RNA MOLECULES FOR SILENCING GENE EXPRESSION
#517Genetically-modified immune cells comprising a microRNA-adapted shRNA (shRNAmiR)
#518Methods of Prevention or Treatment of Alzheimer's Disease by Blocking or Decreasing STING Signaling Activation
#519COMPOSITION COMPRISING OSTEOPONTIN INHIBITOR AS ACTIVE INGREDIENT FOR PREVENTION, ALLEVIATION, OR TREATMENT OF NEURODEGENERATIVE DISEASE
#520COMBINATORIAL INHIBITION OF MIRNAS FOR TREATMENT OF HEART FAILURE
#521NUCLEOSIDE DERIVATIVE AND USE THEREOF
#522METHODS AND COMPOSITIONS FOR TRANSDUCING LYMPHOCYTES AND REGULATING THE ACTIVITY THEREOF
#523TARGETING ZNF410 FOR FETAL HEMOGLOBIN INDUCTION IN BETAHEMOGLOBINOPATHIES
#524COMPOSITIONS AND METHODS FOR PREPARING AN ALZHEIMER'S DISEASE ANIMAL MODEL USING MICRORNA
#525NUTRITIONAL COMPOSITION COMPRISING MIR-3126
#526METHOD FOR TREATING AND PROGNOSING CANCER LIKE GLIOBLASTOMA
#527Composition for regulating expression of PROX1 or expression of telomerase reverse transcriptase comprising activity regulator or method for screening telomerase reverse transcriptase regulator
#528NUTRITIONAL COMPOSITION COMPRISING MIR-3184
#529SYNTHETIC RNA FRAGMENT AND ITS USES FOR RNA-DEPENDENT AMPLIFICATION
#530METHODS AND COMPOSITIONS RELATED TO CATALYTIC ACTIVATION OF HUMAN ARGONAUTE-3
#531MicroRNA-TARGETED THERAPY FOR CARDIAC REPAIR
#532PLURIPOTENT STEM CELL AND DERIVATIVE THEREOF
#533REJUVENATION TREATMENT OF AGE-RELATED WHITE MATTER LOSS
#534METHODS AND PHARMACEUTICAL COMPOSITIONS FOR TREATING OCULAR DISEASES
#535PHARMACEUTICAL COMPOSITION FOR TREATING ALZHEIMER'S DISEASE
#536Selective inhibition of T follicular helper cells for treatment of autoimmune disorders
#537COMPOSITION FOR PREVENTING OR TREATING ALZHEIMER'S DISEASE COMPRISING INHIBITOR OF ATLASTIN 2, AND METHOD FOR DIAGNOSING ALZHEIMER'S DISEASE BY DETERMINING ATLASTIN 2
#538RNA INTERFERENCE-INDUCING NUCLEIC ACID COMPRISING 8-OXOGUANINE, MODIFIED NUCLEIC ACID BINDING TO MICRORNA COMPRISING 8-OXOGUANINE, AND USES THEREOF
#539Extracellular Vesicles Engineered to Be Loaded with Distinct RNA Cargo for Improved Therapeutic Efficacy
#540METHODS AND MODIFICATIONS THAT PRODUCE ssRNAi COMPOUNDS WITH ENHANCED ACTIVITY, POTENCY AND DURATION OF EFFECT
#541MICRORNA AS A THERAPEUTIC AGENT
#542COMPOSITIONS AND METHODS FOR DELIVERING POLYNUCLEOTIDES
#543CELL-PENETRATING PEPTIDE-MICRORNA CONJUGATES FOR INTRACELLULAR CELL DELIVERY
#544MICRORNA-MEDIATED METHODS FOR REJUVENATING CNS GLIAL POPULATIONS
#545EDIBLE PLANT EXOSOME-LIKE NANOVECTORS FOR VACCINATION
#546COMPOSITIONS FOR THE TREATMENT OF NASH AND ASSOCIATED DISORDERS AND METHODS OF USING SAME
#547Modified ribonucleic acids and uses thereof
#548EXOSOME-DERIVED PIWI-INTERACTING RNA AND METHODS OF USE THEREOF
#549Application of transgenic stem cell-derived exosome in preparing medicament or whitening cosmetic
#550Nucleic acid molecules capable of modulating target gene expression and uses thereof
#551VIRAL VECTOR FOR COMBINATION THERAPY
#552AMINE-CONTAINING TRANSFECTION REAGENTS AND METHODS FOR MAKING AND USING SAME
#553BOTTOM-UP ASSEMBLY OF SYNTHETIC EXTRACELLULAR VESICLES
#554IMMUNOLOGICALLY COMPATIBLE AND REVERSIBLE UNIVERSAL PLURIPOTENT STEM CELL AND APPLICATION THEREOF
#555COMPOSITIONS AND METHODS FOR TREATMENT OF FAMILIAL HYPERCHOLESTEROLEMIA AND ELEVATED LOW-DENSITY LIPOPROTEIN CHOLESTEROL
#556ADENO-ASSOCIATED VIRUS VECTOR DELIVERY OF MICRO-DYSTROPHIN TO TREAT MUSCULAR DYSTROPHY
#557Nucleoporins as drug targets for anti-proliferative therapeutics
#558Compositions for FNIP1/FNIP2 Gene Modulation and Methods Thereof
#559METHODS AND COMPOSITIONS FOR TREATING INFLAMMATORY CONDITIONS ASSOCIATED WITH INFECTIOUS DISEASE
#560IMPROVED SCAFFOLDS FOR MULTIPLEXED INHIBITORY RNA
#561EXTRACELLULAR VESICLE SECRETION REDUCING AGENT FOR REDUCING EXTRACELLULAR VESICLE SECRETION, AND USE OF THE SAME
#562METHODS FOR ENHANCING VASCULAR DENSITY
#563Purified Enriched Population Exosomes Derived From Individuals With A Chronic Progressive Lung Disease For Noninvasive Detection, Staging, And Medical Monitoring Of Disease Progression
#564ISOLATION AND PURIFICATION OF EXOSOMES FOR REGENERATIVE MEDICINE
#565COMPOSITIONS AND METHODS FOR MODULATING RPGR EXPRESSION
#566COMPOSITIONS AND METHODS FOR INCREASING OR ENHANCING TRANSDUCTION OF GENE THERAPY VECTORS AND FOR REMOVING OR REDUCING IMMUNOGLOBULINS
#567METHOD FOR TREATING CARDIOVASCULAR DISEASE
#568CATIONIC LIPIDS FOR LIPID NANOPARTICLE DELIVERY OF THERAPEUTICS TO HEPATIC STELLATE CELLS
#569CARDIAC CELL REPROGRAMMING WITH MICRORNAS AND OTHER FACTORS
#570GENE THERAPY FOR NEURODEGENERATIVE DISORDERS USING POLYNUCLEOTIDE SILENCING AND REPLACEMENT
#571miRNA-193a for Promoting Immunogenic Cell Death
#572METHODS AND COMPOSITIONS FOR REJUVENATING CNS GLIAL POPULATIONS BY SUPPRESION OF TRANSCRIPTION FACTORS
#573Targeted Inhibition Using Engineered Oligonucleotides
#574USE OF MIRNA-485 INHIBITORS FOR TREATING AMYOTROPHIC LATERAL SCLEROSIS (ALS)
#575MIRNA-485 INHIBITOR FOR GENE UPREGULATION
#576MicroRNA-based logic gates and uses thereof
#577METHOD OF DELIVERING NUCLEIC ACID TO IMMUNE CELLS USING RBCEV
#578HYPERBRANCHED POLYMERS AND POLYPLEXES AND DNA OR RNA DELIVERY SYSTEMS INCLUDING THE SAME
#579RNAI INDUCED HUNTINGTIN GENE SUPPRESSION
#580ONCOLYTIC VIRAL VECTORS AND USES THEREOF
#581EDIBLE PLANT-DERIVED MICROVESICLE COMPOSITIONS FOR DELIVERY OF miRNA AND METHODS FOR TREATMENT OF CANCER
#582MESENCHYMAL STROMAL CELLS AND EXTRACELLULAR VESICLES FOR TREATING VIRAL INFECTIONS, INFLAMMATION, AND TISSUE FIBROSIS
#583GENE VECTOR CONTROL BY CARDIOMYOCYTE-EXPRESSED MICRORNAS
#584Compositions comprising reversibly modified oligonucleotides and uses thereof
#585USE OF MIRNA-485 INHIBITORS FOR TREATING TAUOPATHY
#586SERINE PROTEASE INHIBITORS FOR SUPPRESSING OR PREVENTING ANAPHYLACTIC REACTION
#587MICRORNA COMPOSITIONS AND METHODS OF USE
#588REAGENTS FOR TREATMENT OF HEPATITIS B VIRUS (HBV) INFECTION AND USE THEREOF
#589Compositions and methods of treating facioscapulohumeral muscular dystrophy
#590INDUCIBLE SINGLE AAV SYSTEM AND USES THEREOF
#591MIR-149-3P AND METHOD FOR TREATING METABOLIC DISEASE USING THE SAME
#592DRUG FOR CURATIVE THERAPY OF INTRACTABLE HEREDITARY RENAL ALPORT SYNDROME
#593Therapeutic agent targeted to receptor protein, test agent, antibody that binds to receptor protein, and screening method for molecularly targeted drugs
#594ENHANCED PLACENTAL STEM CELLS AND USES THEREOF
#595COMPOSITIONS COMPRISING BACTERIALLY DERIVED MINICELLS AND METHODS OF USING THE SAME
#596Modified U6 promoter system for tissue specific expression
#597COMPOSITIONS AND METHODS FOR TREATING OR AMELIORATING A MYCOBACTERIUM TUBERCULOSIS INFECTION
#598VECTORIZED ANTIBODIES (vAb) AND USES THEREOF
#599MICRORNA-7 COMPOSITIONS FOR PROMOTING FUNCTIONAL RECOVERY FOLLOWING SPINAL CORD INJURY AND METHODS OF USE THEREOF
#600AAV capsids identified by in vivo library selection