109162 ⎘
Structure or type of the nucleic acid; Chemical structure of the backbone Phosphorothioates
GLP-1 RECEPTOR LIGAND MOIETY CONJUGATED OLIGONUCLEOTIDES AND USES THEREOF
#602NOVEL PROCESSES FOR THE PRODUCTION OF OLIGONUCLEOTIDES
#603TRANSGLUTAMINASE-MEDIATED CONJUGATION
#604COMPOSITIONS AND METHODS FOR DELIVERING THERAPEUTIC OLIGONUCLEOTIDES TO THE CENTRAL NERVOUS SYSTEM
#605GLUCOKINASE (GCK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#606TREATMENT OF MST1 RELATED DISEASES AND DISORDERS
#607TREATMENT OF DKK2 RELATED DISEASES AND DISORDERS
#608TREATMENT OF MTRES1 RELATED DISEASES AND DISORDERS
#609TREATMENT OF PLIN1 RELATED DISEASES AND DISORDERS
#610RNA INTERFERENCE MEDIATED INHIBITION OF GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACIDS (SINA)
#611OLIGONUCLEOTIDES FOR IFN-GAMMA SIGNALING PATHWAY MODULATION
#612Compounds and Methods for Modulating Splicing of Pre-MRNA
#613LIPID CONJUGATION FOR TARGETING NEURONS OF THE CENTRAL NERVOUS SYSTEM
#614OLIGONUCLEOTIDES
#615Compounds and Methods for Modulating GFAP
#616Conjugated antisense compounds and their use
#617TREATMENT OF ANGPTL4 RELATED DISEASES
#618DOUBLE STRANDED OLIGONUCLEOTIDE COMPOSITIONS AND METHODS RELATING THERETO
#619LIGAND-BINDING NUCLEIC ACID COMPLEX
#620COMPOUNDS FOR REDUCING PTBP1 EXPRESSION
#621FOLLICULIN iRNA COMPOSITIONS AND METHODS THEREOF
#622RNAi AGENTS, COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING TRANSTHYRETIN (TTR) ASSOCIATED DISEASES
#623SODIUM-GLUCOSE COTRANSPORTER-2 (SGLT2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#624POLYNUCLEIC ACID MOLECULES TARGETING PCSK9 AND USES THEREOF
#625COMPOSITION AND METHOD FOR INHIBITING EXPRESSION OF HEPATITIS B VIRUS (HBV)PROTEIN
#626COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#627MIRNA INHIBITORS FOR PREVENTING AND TREATING ANEURYSMS, HYPERTENSION, ARDS AND OTHER DISEASES ASSOCIATED WITH ENDOTHELIAL DYSFUNCTION
#628LIPOPHILIC SIRNA CONJUGATES FOR THE TREATMENT OF INFLAMMATORY DISEASES
#629METHODS FOR THE TREATMENT OF NUCLEOTIDE REPEAT EXPANSION DISORDERS ASSOCIATED WITH MSH3 ACTIVITY
#630Methods and Compositions for Adar-Mediated Editing
#631COMPOSITIONS AND METHODS FOR SILENCING CARBONIC ANHYDRASE 2 EXPRESSION
#632BETA-CATENIN (CTNNB1) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#633Short Duplex DNA as a Novel Gene Silencing Technology and Use Thereof
#634MICROTUBULE ASSOCIATED PROTEIN TAU (MAPT) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#635COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE ALAS1 GENE
#636SIGNAL TRANSDUCER AND ACTIVATOR OF TRANSCRIPTION FACTOR 6 (STAT6) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#637METHODS FOR TREATING OR PREVENTING CONTACT-ACTIVATION PATHWAY-ASSOCIATED DISEASES USING iRNA COMPOSITIONS TARGETING FACTOR XII (HAGEMAN FACTOR) (F12)
#638ANTISENSE OLIGONUCLEOTIDE TARGETING CAV3.1 GENE AND USES THEREOF
#639RNA INTERFERENCE MEDIATED INHIBITION OF CATENIN (CADHERIN-ASSOCIATED PROTEIN), BETA 1 (CTNNB1) GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACID (SINA)
#640Modulators of Complement Factor B
#641METHODS AND COMPOSITIONS FOR TREATING AN ANGIOTENSINOGEN- (AGT-) ASSOCIATED DISORDER
#642METHOD FOR DESIGNING OLIGONUCLEOTIDE HAVING REDUCED CENTRAL TOXICITY
#643CONJUGATED ANTISENSE COMPOUNDS AND THEIR USE
#644TARGETED NUCLEIC ACID CONJUGATE COMPOSITIONS
#645ANTISENSE OLIGONUCLEOTIDES TARGETING ADENOSINE KINASE
#646SIRNA TARGETING TMPRSS6 FOR THE TREATMENT OF MYELOPROLIFERATIVE DISORDERS
#647COMB SHAPED ANTIVIRALS ENDING WITH OR WITHOUT CHAIN TERMINATING BASES
#648HUMAN CHROMOSOME 9 OPEN READING FRAME 72 (C9ORF72) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#649POLYANIONIC ACIDS TO IMPROVE RECOVERY AND MINIMIZE SYSTEM LOSS
#650COMPOSITIONS, SYSTEMS AND METHODS OF RNA EDITING USING DKC1
#651COMPOSITIONS AND METHODS FOR CD123 MODIFICATION
#652COMPOUNDS AND METHODS FOR REDUCING KCNT1 EXPRESSION
#653SIRNA TARGETING 17Beta-HYDROXYSTEROID DEHYDROGENASE TYPE 13 AND SIRNA CONJUGATE
#654NUCLEIC ACID MOLECULES FOR PSEUDOURIDYLATION
#655COMPOSITIONS AND METHODS FOR TREATMENT OF FRIEDREICH'S ATAXIA
#656SPLICE-SWITCHING OLIGONUCLEOTIDES AND METHODS OF USE
#657CHIRAL CONTROL
#658siRNA AND USE THEREOF
#659MODIFIED NUCLEIC ACIDS, HYBRID GUIDE RNAS, AND USES THEREOF
#660TUNING CRISPR/CAS9 ACTIVITY WITH CHEMICALLY MODIFIED NUCLEOTIDE SUBSTITUTIONS
#661Programmed Cell Death Protein 1 (PD1) Compositions and Methods for Cell-Based Therapy
#662Materials and Methods for Treatment of Hemoglobinopathies
#663CORRECTION OF DUCHENNE MUSCULAR DYSTROPHY MUTATIONS WITH ALL-IN-ONE ADENO-ASSOCIATED VIRUS-DELIVERED SINGLE-CUT CRISPR
#664COMPOSITIONS OF MATTER FOR DETECTION ASSAYS
#665MODULATING APOLIPOPROTEIN (A) EXPRESSION
#666GUIDE RNAS WITH CHEMICAL MODIFICATION FOR PRIME EDITING
#667MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING FRIEDREICH'S ATAXIA
#668TREATMENT OF NEUROLOGICAL DISORDERS
#669THERAPEUTIC COMPOSITIONS FOR TREATING PAIN VIA MULTIPLE TARGETS
#670Specific Oligonucleotide-Programmed Readthrough of Nonsense Codons
#671iRNA COMPOSITIONS AND METHODS FOR SILENCING CHITINASE 3-LIKE PROTEIN 1/YKL-40 (CHI3L1/YKL-40) PROTEIN
#672ELONGATION OF VERY LONG CHAIN FATTY ACIDS PROTEIN 1 (ELOVL1) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#673PROLINE DEHYDROGENASE 2 (PRODH2) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#674COMPOSITIONS AND METHODS FOR TREATING CANCER
#675Complement component C3 iRNA compositions and methods of use thereof
#676COMPOUNDS AND METHODS FOR MODULATING PLP1
#677Linear DNA with Enhanced Resistance Against Exonucleases
#678PHARMACEUTICAL COMPOSITION CONTAINING CELL-DERIVED NATURAL OR ARTIFICIAL NANOVESICLES LOADED WITH ANTISENSE OLIGONUCLEOTIDE-BASED DRUG
#679NUCLEIC ACID MOLECULE CONJUGATE HAVING PROLONGED IN VIVO HALF-LIFE
#680ANGIOPOIETIN-LIKE 3 (ANGPTL3) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#681Allogeneic Cartilage Regeneration
#682NUCLEIC ACIDS FOR INHIBITING EXPRESSION OF A TARGET GENE COMPRISING PHOSPHORODITHIOATE LINKAGES
#683Compositions for Modulating C9ORF72 Expression
#684GENE THERAPY FOR INFLAMMATORY CONDITIONS
#685MICROGLIAL GENE SILENCING USING DOUBLE-STRANDED SIRNA
#686TRANSTHYRETIN (TTR) iRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING TTR-ASSOCIATED OCULAR DISEASES
#687NUCLEIC ACID, PHARMACEUTICAL COMPOSITION, CONJUGATE, PREPARATION METHOD, AND USE
#688Muscle targeting complexes and uses thereof for treating myotonic dystrophy
#689TRANSGENE CASSETTES DESIGNED TO EXPRESS A HUMAN MECP2 GENE
#690TRANSGLUTAMINASE-MEDIATED CONJUGATION
#691DEFINED MULTI-CONJUGATES OLIGONUCLEOTIDES
#692ANGIOTENSINOGEN (AGT) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#693Tuning cascade assay kinetics via molecular design
#694COMPOUNDS AND METHODS FOR REDUCING NLRP3 EXPRESSION
#695COMPOUNDS AND METHODS FOR REDUCING PLN EXPRESSION
#696SPINAL MUSCULAR ATROPHY (SMA) TREATMENT VIA TARGETING OF SMN2 SPLICE SITE INHIBITORY SEQUENCES
#697RNA SILENCING AGENTS AND METHODS OF USE
#698MODIFIED CELLS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES
#699NOVEL PEPTIDE-OLIGONUCLEOTIDE CONJUGATE AND USE THEREOF
#700MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes
#701TRANSMEMBRANE PROTEASE, SERINE 6 (TMPRSS6) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#702OLIGONUCLEOTIDES TARGETING S6K1
#703TREATMENT OF AMYOTROPHIC LATERAL SCLEROSIS
#704KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#705METHODS AND COMPOSITIONS FOR INHIBITING EXPRESSION OF LDHA
#706MICRORNA BLOCKADE FOR THE TREATMENT OF DISEASE
#707ENHANCED OLIGONUCLEOTIDES FOR INHIBITING RTELl EXPRESSION
#708DOUBLE-STRANDED SIRNA HAVING PATTERNED CHEMICAL MODIFICATIONS
#709COMPOSITIONS AND METHODS FOR SITE-SPECIFIC MODIFICATION
#710MICRORNA-27B INHIBITORS
#711CALCIUM VOLTAGE-GATED CHANNEL AUXILIARY SUBUNIT GAMMA 1 (CACNG1) BINDING PROTEINS AND CACNG1-MEDIATED DELIVERY TO SKELETAL MUSCLE
#712FN3 DOMAIN-SIRNA CONJUGATES AND USES THEREOF
#713COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF PCSK9
#714TREATMENT OF MST1 RELATED DISEASES AND DISORDERS
#715ANGIOPOIETIN-LIKE 3 (ANGPTL3) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#716SMALL INTERFERING RNA TARGETING C3 AND USES THEREOF
#717DOSAGES AND METHODS FOR DELIVERING LIPID FORMULATED NUCLEIC ACID MOLECULES
#718GalNAc compositions for improving siRNA bioavailability
#719METHODS FOR MODULATING FMR1 EXPRESSION
#720OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#721COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#722OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#723FLAP PROBE AND USE THEREOF
#724Methods for Treatment of Alport Syndrome
#725NUCLEIC ACID DELIVERY TO THE CENTRAL NERVOUS SYSTEM
#726MODIFIED GUIDE RNAS FOR CRISPR GENOME EDITING
#727KETOHEXOKINASE (KHK) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#728METHOD OF TREATING FATTY LIVER DISEASE
#729THERAPEUTIC SPLICE-SWITCHING OLIGONUCLEOTIDES FOR CANCER
#730Modified Guide RNAs Comprising an Internal Linker for Gene Editing
#731ANTISENSE OLIGONUCLEOTIDES TARGETING FOXG1
#732OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#733OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF MAKING THE SAME
#734MODULATORS AND MODULATION OF THE RECEPTOR FOR ADVANCED GLYCATION END-PRODUCTS RNA
#735MODULATION OF GYS1 EXPRESSION
#736ALPHA-1 ANTITRYPSIN (AAT) RNAI AGENTS, COMPOSITIONS INCLUDING AAT RNAI AGENTS, AND METHODS OF USE
#737ALLELE SELECTIVE INHIBITION OF MUTANT C9ORF72 FOCI EXPRESSION BY DUPLEX RNAS TARGETING THE EXPANDED HEXANUCLEOTIDE REPEAT
#738Selective Antisense Compounds and Uses Thereof
#739ANTISENSE OLIGONUCLEOTIDES FOR USE IN THE TREATMENT OF CORNEAL DYSTROPHIES
#740Oligonucleotide Comprising Inosine for Treating DMD
#741TARGETED RNA EDITING
#742GLYCOGEN SYNTHASE KINASE 3 ALPHA (GSK3 ALPHA) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#743OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#744NUCLEIC ACID MOLECULES FOR PSEUDOURIDYLATION
#745COMPOSITIONS AND METHODS FOR TREATMENT OF FRIEDREICH'S ATAXIA
#746COMPLEMENT COMPONENT 9 (C9) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#747MODULATION OF TRANSTHYRETIN EXPRESSION
#748Compositions and methods of treating facioscapulohumeral muscular dystrophy
#749PRION PROTEIN (PRNP) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#750RNAI AGENT FOR INHIBITING HBV EXPRESSION AND USE THEREOF
#751Compositions and methods of treating facioscapulohumeral muscular dystrophy
#752METHODS AND COMPOSITIONS FOR PRODUCTION OF GENETICALLY MODIFIED PRIMARY CELLS
#753MUSCLE TARGETING COMPLEXES AND USES THEREOF FOR TREATING MYOTONIC DYSTROPHY
#754COMPOSITIONS AND METHODS FOR INHIBITING GENE EXPRESSION IN THE CENTRAL NERVOUS SYSTEM
#755iRNA COMPOSITIONS AND METHODS FOR SILENCING AMYLOID PRECURSOR PROTEIN (APP)
#756COAGULATION FACTOR X (F10) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#757OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#758MODIFIED HETERO NUCLEIC ACIDS
#759METHODS FOR PERFORMING ANTISENSE OLIGONUCLEOTIDE-MEDIATED EXON SKIPPING IN THE RETINA OF A SUBJECT IN NEED THEREOF
#760MODIFIED OLIGONUCLEOTIDES
#761COMPOSITIONS AND METHODS FOR TREATING PULMONARY ARTERIAL HYPERTENSION (PAH) AND OTHER DISORDERS
#762COMPOSITIONS AND METHODS FOR INHIBITION OF EXPRESSION OF APOLIPOPROTEIN C-III (APOC3) GENES
#763PHOSPHOROTHIOATE NUCLEIC ACID CONJUGATES INCLUDING DNA EDITING ENZYMES
#764OLIGONUCLEOTIDE COMPOSITIONS AND METHODS OF USE THEREOF
#765POLYNUCLEOTIDE AGENTS TARGETING PROGRAMMED CELL DEATH 1 LIGAND 1 (PD-L1) AND METHODS OF USE THEREOF
#766OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#767OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#768Tuning cascade assay kinetics via molecular design
#769Compounds and methods for modulating SCN2A
#770OPA1 ANTISENSE OLIGOMERS FOR TREATMENT OF CONDITIONS AND DISEASES
#771CONJUGATED OLIGONUCLEOTIDE COMPOUNDS, METHODS OF MAKING AND USES THEREOF
#772MODULATION OF AAV-BASED GENE EXPRESSION
#773METHODS FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES USING TRANSTHYRETIN (TTR) iRNA COMPOSITIONS
#774GENE CORRECTION FOR SCID-X1 IN LONG-TERM HEMATOPOIETIC STEM CELLS
#775STABLE TARGET-EDITING GUIDE RNA TO WHICH CHEMICALLY MODIFIED NUCLEIC ACID IS INTRODUCED
#776COMPOSITIONS AND METHODS FOR ENHANCED INTESTINAL ABSORPTION OF CONJUGATED OLIGOMERIC COMPOUNDS
#777COMPOSITIONS AND METHODS FOR INHIBITING EXPRESSION OF THE PCSK9 GENE
#778ANTISENSE OLIGONUCLEOTIDES INCREASING FOXG1 EXPRESSION
#779RNAi AGENT TARGETING MYD88 AND USE THEREOF
#780OLIGONUCLEOTIDES FOR INDUCING PATERNAL UBE3A EXPRESSION
#781Methods and Systems for Guide RNA Design and Use
#782RNAI CONSTRUCTS AND METHODS FOR INHIBITING FAM13A EXPRESSION
#783CONJUGATED OLIGONUCLEOTIDES
#784SINGLE-STRANDED OLIGONUCLEOTIDE
#785Heteromultivalent Nucleic Acid Scaffolds and Uses Thereof
#786COMPOUNDS AND METHODS FOR REDUCING ATXN3 EXPRESSION
#787MODULATORS OF PNPLA3 EXPRESSION
#788MODULATORS OF PNPLA3 EXPRESSION
#789Oligonucleotides reducing the amount of CD73 mRNA and CD73 protein expression
#790Linear DNA With Enhanced Resistance Against Exonucleases and Methods for the Production Thereof
#791METHOD OF ALLELE SPECIFIC SILENCING FOR THE TREATMENT OF AUTOSOMAL DOMINANT CATECHOLAMINERGIC POLYMORPHIC VENTRICULAR TACHYCARDIA (CPVT)
#792Target Ligand
#793Compositions, systems, and methods for regulation of hepatitis B virus through targeted gene repression
#794Compositions, systems, and methods for regulation of hepatitis b virus through targeted gene repression
#795OPTIMIZED ANTI-FLT1 OLIGONUCLEOTIDE COMPOUNDS FOR TREATMENT OF PREECLAMPSIA AND OTHER ANGIOGENIC DISORDERS
#796METHODS AND COMPOSITIONS FOR MODULATING APOLIPOPROTEIN (A) EXPRESSION
#797COMPOSITIONS AND METHODS FOR TREATMENT OF CARDIAC DISEASES
#798Compounds and methods for modulating ATXN1
#799Muscle targeting complexes and uses thereof for treating dystrophinopathies
#800POLY-MORPHOLINO OLIGONUCLEOTIDE GAPMERS
#801TRANSFERRIN RECEPTOR BINDING PROTEINS AND CONJUGATES
#802ANTISENSE COMPOUNDS
#803ANTISENSE OLIGONUCLEOTIDES AND THEIR USE FOR THE TREATMENT OF PAIN
#804OLIGONUCLEOTIDE AND USE THEREOF AGAINST HEPATITIS B VIRUS AND HEPATITIS D VIRUS
#805DOUBLE STRANDED RNA TARGETING ANGIOTENSINOGEN (AGT) AND METHODS OF USE THEREOF
#806PHARMACEUTICAL COMPOSITION
#807OLIGONUCLEOTIDES FOR PMS1 MODULATION
#808NEW THERAPY
#809CHEMICALLY MODIFIED CRISPR-CAS13 GUIDE RNAS
#810COMPLEMENT FACTOR B-MODULATING COMPOSITIONS AND METHODS OF USE THEREOF
#811OPTIMIZED TLR7 LIGANDS AND USES THEREOF
#812Oligomers and oligomer conjugates
#813ANTISENSE OLIGOMERS FOR TREATMENT OF NON-SENSE MEDIATED RNA DECAY BASED CONDITIONS AND DISEASES
#814Compositions of matter for detection assays
#815COMPOUNDS AND METHODS FOR MODULATING TMPRSS6 EXPRESSION
#816OLIGONUCLEOTIDES FOR MODULATING TAU EXPRESSION
#817OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF
#818COMPOUNDS AND METHODS FOR MODULATING SCN2A
#819OLIGONUCLEOTIDES USEFUL FOR MODULATION OF SPLICING
#820Stabilized saRNA Compositions and Methods of Use
#821Tuning cascade assay kinetics via molecular design
#822SNCA IRNA COMPOSITIONS AND METHODS OF USE THEREOF FOR TREATING OR PREVENTING SNCA-ASSOCIATED NEURODEGENERATIVE DISEASES
#823MODIFIED OLIGONUCLEOTIDES FOR USE IN TREATMENT OF TAUOPATHIES
#824Compositions and methods for inhibiting transmembrane serine protease 6 (TMPRSS6) expression
#825DOUBLE STRANDED RNA TARGETING 17-BETA HYDROXYSTEROIDDEHYDROGENASE 13 (HSD17B13) AND METHODS OF USE THEREOF
#826NUCLEIC ACID DUPLEXES
#827COMPOUNDS FOR MODULATING CHMP7
#828LINKAGE MODIFIED OLIGOMERIC COMPOUNDS AND USES THEREOF
#829TREATMENT OF FUCHS' ENDOTHELIAL CORNEAL DYSTROPHY
#830COMPOSITIONS AND METHODS FOR THE TREATMENT OF HEMOGLOBINOPATHIES
#831OLIGONUCLEOTIDES CONTAINING 2'-DEOXY-2'FLUORO-BETA-D-ARABINOSE NUCLEIC ACID (2'-FANA) FOR TREATMENT AND DIAGNOSIS OF RETROVIRAL DISEASES
#832MODULATION OF GENE EXPRESSION AND SCREENING FOR DEREGULATED PROTEIN EXPRESSION
#833CHEMICAL MODIFICATIONS FOR INHIBITING EXPRESSION OF ALDH2
#834COMPOSITIONS AND METHODS FOR INHIBITING SNCA EXPRESSION
#835COMPOSITIONS AND METHODS FOR INHIBITING MAPT EXPRESSION
#836MUCIN 5B (MUC5B) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#837OLIGONUCLEOTIDES FOR ATN1 MODULATION
#838UMLILO ANTISENSE TRANSCRIPTION INHIBITORS
#839GUIDE RNA WITH CHEMICAL MODIFICATIONS
#840METHODS AND COMPOSITIONS RELATING TO GENETICALLY ENGINEERED CELLS EXPRESSING CHIMERIC ANTIGEN RECEPTORS
#841METHODS AND COMPOSITIONS FOR INHIBITION OF HAO1 (HYDROXYACID OXIDASE 1 (GLYCOLATE OXIDASE)) GENE EXPRESSION
#842NUCLEIC ACIDS CONTAINING ABASIC NUCLEOTIDES
#843MODIFIED ANTISENSE OLIGONUCLEOTIDES TARGETING SPLICING FACTORS
#844NOVEL EFFICACIOUS MICRORNA-30C ANALOGS REDUCE APOLIPOPROTEIN B SECRETION IN HUMAN LIVER CELLS
#845TREATMENT OF SOS2 RELATED DISEASES AND DISORDERS
#846PROTECTING OLIGONUCLEOTIDES FOR CRISPR GUIDE RNA
#847Compositions of matter for detection assays
#848EXOSOMAL LOADING USING HYDROPHOBICALLY MODIFIED OLIGONUCLEOTIDES
#849OPTIMIZED SIRNA SCAFFOLDS
#850COMPLEMENT COMPONENT C1S INHIBITORS FOR TREATING A NEUROLOGICAL DISEASE, AND RELATED COMPOSITIONS, SYSTEMS AND METHODS OF USING SAME
#851COMPOSITIONS AND METHODS OF TREATING MUSCLE DYSTROPHY
#852COMPOSITIONS AND METHODS FOR CD38 MODIFICATION
#853G PROTEIN-COUPLED RECEPTOR 75 (GPR75) IRNA COMPOSITIONS AND METHODS OF USE THEREOF
#854Huntingtin (HTT) iRNA agent compositions and methods of use thereof
#855OLIGONUCLEOTIDES FOR APP MODULATION
#856MODIFIED GAPMER OLIGOMERS AND METHODS OF USE THEREOF
#857NOVEL RNA COMPOSITIONS AND METHODS FOR INHIBITING ANGPTL3
#858TARGETING XIST AND RNA METHYLATION FOR X REACTIVATION THERAPY
#859COMPOSITIONS AND METHODS FOR TREATING GLYCOGEN STORAGE DISEASE TYPE 1A
#860COMPOSITIONS AND METHODS FOR MODULATING SCAP ACTIVITY
#861COMPOUNDS AND METHODS FOR MODULATING PMP22
#862Human XIST Antisense Oligonucleotides for X Reactivation Therapy
#863COMBINATION
#864Modified short interfering nucleic acid (siNA) molecules and uses thereof
#865SERPINC1 iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#866COMPOSITIONS AND METHODS FOR CD6 MODIFICATION
#867GENE CORRECTION FOR X-CGD IN HEMATOPOIETIC STEM AND PROGENITOR CELLS
#868COMPOUNDS AND METHODS FOR REDUCING IFNAR1 EXPRESSION
#869COMPOSITIONS AND METHODS FOR MODULATING COMPLEMENT FACTOR B EXPRESSION
#870COMPOSITIONS AND METHODS FOR THE TREATMENT OF ANGIOPOIETIN LIKE 7 (ANGPTL7) RELATED DISEASES
#871OLIGONUCLEOTIDE TREATMENT OF HEPATITIS B PATIENTS
#872Nucleic acid, composition and conjugate containing same, preparation method, and use thereof
#873RNAI AGENTS FOR HEPATITIS B VIRUS INFECTION
#874DYSTROPHIN EXON SKIPPING OLIGONUCLEOTIDES
#875SHORT INTERFERING NUCLEIC ACID (siNA) COMPOSITIONS
#876OLIGONUCLEOTIDES
#877Compositions of matter for detection assays
#878COMPOSITIONS AND METHODS FOR INHIBITING MITOCHONDRIA AMIDOXIME REDUCING COMPONENT 1 (MARC1) EXPRESSION
#879COMPOSITIONS AND METHODS FOR THE TREATMENT OF METABOLIC SYNDROME
#880ANAPLASTIC LYMPHOMA KINASE (ALK) iRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
#881MAPT RNA interference agents
#882METHODS FOR INTRACELLULAR DELIVERY AND ENHANCED GENE TARGETING
#883Compounds and compositions including phosphorothioated oligodeoxynucleotide, and methods of use thereof
#884METHODS FOR USING GUIDE RNAS WITH CHEMICAL MODIFICATIONS
#885RNA-editing oligonucleotides and uses thereof
#886Base editing of ANGPTL3 and methods of using same for treatment of disease
#887Modified Short Interfering Nucleic Acid (siNA) Molecules and Uses Thereof
#888IRNA COMPOSITIONS AND METHODS FOR SILENCING GROWTH FACTOR RECEPTOR BOUND PROTEIN 10 (GRB10) OR GROWTH FACTOR RECEPTOR BOUND PROTEIN 14 (GRB14) IN THE LIVER
#889RNA-editing oligonucleotides and uses thereof
#890OLIGONUCLEOTIDES FOR REDUCTION OF PD-L1 EXPRESSION
#891OLIGOMERS HAVING BICYCLIC SCAFFOLD MOIETIES
#892OLIGONUCLEOTIDES TARGETING XBP1
#893NOVEL TLR9 AGONISTS
#894COMPLEMENT COMPONENT C1R INHIBITORS FOR TREATING A NEUROLOGICAL DISEASE, AND RELATED COMPOSITIONS, SYSTEMS AND METHODS OF USING SAME
#895TUMOR NECROSIS FACTOR RECEPTOR ASSOCIATED FACTOR 6 (TRAF6) iRNA COMPOSITIONS AND METHODS OF USE THEREOF
#896ANTIVIRAL SILENCING RNA MOLECULES, CHEMICALLY MODIFIED ANTIVIRAL SILENCING RNA MOLECULES WITH ENHANCED CELL PENETRATING ABILITIES, PHARMACEUTICAL COMPOSITIONS COMPRISING SAME AND USES THEREOF FOR TREATMENT OF VIRAL INFECTIONS
#897Compositions for modulating tau expression
#898RNAi Agents And Compositions for Inhibiting Expression of Apolipoprotein C-III (APOC3)
#899UNA OLIGOMERS FOR THE TREATMENT OF POLYGLUTAMINE DISEASES
#900Modulators of PCSK9 Expression