108937 ⎘
Enzymes; Proenzymes; Compositions thereof ; Processes for preparing, activating, inhibiting, separating or purifying enzymes; Hydrolases (3) acting on ester bonds (3.1) Ribonucleases RNAses, DNAses
ENGINEERING OF SYSTEMS, METHODS AND OPTIMIZED GUIDE COMPOSITIONS FOR SEQUENCE MANIPULATION
#302Compositions and Methods for Immunotherapy
#303SEQUENCE SPECIFIC ANTIMICROBIALS
#304PHARMACEUTICAL COMPOSITION FOR TOPICAL WOUND TREATMENT
#305Dual Cut Retron Editors for Genomic Insertions and Deletions
#306NUCLEASES AND COMPOSITIONS, SYSTEMS, AND METHODS THEREOF
#307COMPOSITIONS, METHODS, AND SYSTEMS FOR DNA MODIFICATION
#308TYPE I-D CRISPR-GUIDED TRANSPOSON WITH ENHANCED GENOME EDITING
#309SERINE RECOMBINASE SYSTEMS FOR SITE-SPECIFIC GENE EDITING
#310CRISPR-ASSOCIATED TRANSPOSON SYSTEMS AND METHODS OF USING SAME
#311MODIFIED IMMUNE CELLS HAVING ENHANCED FUNCTION AND METHODS FOR SCREENING THE SAME
#312MAMMALIAN CELL LINE FOR PROTEIN PRODUCTION AND LIBRARY GENERATION
#313GENOME EDITING COMPOSITIONS AND METHODS FOR TREATMENT OF CHRONIC GRANULOMATOUS DISEASE
#314FUSION OF SITE-SPECIFIC RECOMBINASES FOR EFFICIENT AND SPECIFIC GENOME EDITING
#315METHODS FOR FACILITATING THE DIFFERENTIATION OF INDUCED PLURIPOTENT STEM CELLS INTO RETINAL GANGLION CELLS
#316Materials and Methods for Treatment of Hemoglobinopathies
#317METHODS AND COMPOSITIONS FOR USING PLASMA CELL DEPLETING AGENTS AND/OR B CELL DEPLETING AGENTS TO SUPPRESS HOST ANTI-AAV ANTIBODY RESPONSE AND ENABLE AAV TRANSDUCTION AND RE-DOSING
#318NOVEL CRISPR/CAS13 SYSTEMS AND USES THEREOF
#319Method for Producing Double-Stranded DNA Molecules Having Reduced Sequence Errors
#320Inhibition of NHEJ, MMEJ, and 53BP1 Promotes High Levels of HDR
#321OPTIMIZED RETRON EDITORS FOR EFFICIENT GENOME ENGINEERING AND DELIVERY TO MAMMALIAN CELLS
#322NON-LTR RETROTRANSPOSON SYSTEM AND USE THEREOF
#323TARGETED TRANS-SPLICING USING CRISPR/CAS13
#324PERMANENT EPIGENETIC GENE SILENCING
#325COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH SIRNAS TARGETING CIDEB
#326ENGINEERING AND OPTIMIZATION OF IMPROVED SYSTEMS, METHODS AND ENZYME COMPOSITIONS FOR SEQUENCE MANIPULATION
#327CAS VARIANTS FOR GENE EDITING
#328CRISPR/CAS9-BASED FUSION PROTEINS FOR MODULATING GENE EXPRESSION AND METHODS OF USE
#329COMPOSITIONS AND METHODS FOR EPIGENETIC REGULATION OF HBV GENE EXPRESSION
#330E. COLI NISSLE STRAIN WITH IMPROVED TRANSFORMATION EFFICIENCY
#331METHODS FOR INTRATUMORAL DELIVERY OF CRISPR/CAS SYSTEMS
#332INTEIN TECHNOLOGY TO DELIVER ABCA3 LIPID TRANSPORTER FOR ABCA3 DEFICIENCY
#333GENETICALLY ENGINEERED MESENCHYMAL STEM CELLS AND USES THEREOF
#334METHOD FOR TARGETED GENE INSERTION INTO IMMUNE CELLS
#335GENETICALLY MODIFIED NON-HUMAN MAMMALS, PREPARATION METHODS THEREFOR, AND APPLICATIONS THEREOF
#336METHODS AND COMPOSITIONS FOR MODIFYING FLOWERING TIME GENES IN PLANTS
#337METHODS AND SYSTEMS FOR IDENTIFYING AND VALIDATING A GENE COMBINATION ASSOCIATED WITH A TRAIT AND USES THEREOF
#338Counter-Selection by Inhibition of Conditionally Essential Genes
#339ENGINEERING DISEASE RESISTANCE BY EDITING THE EPIGENOME
#340TARGETED DONOR DNA INSERTION AND INDEL EDITING OF PLANT GENES
#341PLANT GENOME EDITING METHODS
#342COMPOSITION COMPRISING GENE EDITING PROTEIN FOR CANNABIS SATIVA GENE EDITING, AND GENE EDITING METHOD USING SAME
#343EXPRESSION SYSTEM FOR PRODUCT MANUFACTURING
#344METHODS AND COMPOSITIONS FOR THE MAKING AND USING OF GUIDE NUCLEIC ACIDS
#345Continuous Multiplexed Phage Genome Engineering Using a Retron Editing Template
#346MODIFIED CASCADE RIBONUCLEOPROTEINS AND USES THEREOF
#347METHODS OF PURIFYING AN ENVELOPED VIRUS
#348BASE EDITING METHODS AND COMPOSITIONS FOR TREATING TRIPLET REPEAT DISORDERS
#349GENE THERAPY FOR HAPLOINSUFFICIENCY
#350METHODS AND COMPOSITIONS FOR TREATING LIPOPROTEIN-RELATED DISEASES
#351GENE EDITING METHODS FOR TREATING ALPHA-1 ANTITRYPSIN (AAT) DEFICIENCY
#352GENE EDITING TO IMPROVE JOINT FUNCTION
#353LIPID NANOPARTICLE FORMULATIONS AND COMPOSITIONS
#354CELLS HAVING SOLID TUMOR TARGETING BACKBONE AND USE THEREOF
#355ENHANCED IMMUNE CELL THERAPY
#356COMPOSITIONS AND METHODS FOR TREATING LIVER DISEASES WITH SIRNAS TARGETING GPAM
#357METHODS OF TREATING, AMELIORATING AND/OR PREVENTING FIBRODYSPLASIA OSSIFICANS PROGRESSIVA AND HETEROTOPIC OSSIFICATION, AND KITS FOR THE SAME
#358COMPOSITIONS AND METHODS FOR ORGAN SPECIFIC DELIVERY OF NUCLEIC ACIDS
#359NOVEL REGULATOR VIPR IN BACILLUS STRAINS
#360SYNTHETIC POLYPEPTIDES AND USES THEREOF
#361GENOME-MODIFIED SILKWORM PRODUCING CHIMERIC SILK THREAD
#362COMPOSITIONS AND METHODS FOR EFFICIENT IN VIVO DELIVERY
#363PROGRAMMABLE NUCLEASE-PEPTIDASE COMPOSITIONS
#364NOVEL CRISPR ENZYMES AND SYSTEMS
#365MODIFIED CASCADE RIBONUCLEOPROTEINS AND USES THEREOF
#366HYBRID CRISPR-CAS SYSTEMS AND METHODS OF USE THEREOF
#367OPTIMIZED CAS PROTEIN AND USE THEREOF
#368HYPOIMMUNE BETA CELLS DIFFERENTIATED FROM PLURIPOTENT STEM CELLS AND RELATED USES AND METHODS
#369GENOME EDITING METHODS AND CONSTRUCTS
#370SITE-SPECIFIC IN VIVO T CELL ENGINEERING, SYSTEMS, COMPOSITIONS AND METHODS THEREOF
#371GENE EDITING SYSTEM FOR TREATING USHER SYNDROME
#372IMMUNE CELLS WITH COMBINATION GENE PERTURBATIONS
#373UNIVERSAL CELL AND METHOD FOR PREPARING SAME
#374METHOD FOR PREDICTING OFF-TARGET WHICH CAN OCCUR IN PROCESS OF EDITING GENOME BY USING PRIME EDITING SYSTEM
#375Production of reverse transcribed DNA (RT-DNA) using a retron reverse transcriptase from exogenous RNA
#376TARGET SYSTEM FOR HOMOLOGY-DIRECTED REPAIR AND GENE EDITING METHOD USING SAME
#377NOVEL CRISPR ENZYMES AND SYSTEMS
#378ONE VECTOR SYSTEM FOR IDENTIFICATION OF GENOME MODIFYING ENZYMES
#379RT-DNA Fidelity and Retron Genome Editing
#380MULTIPLEXABLE CRISPR EDITORS UTILIZING INTRACELLULAR EVOLVED APTAMERS FOR ENDOGENOUS EFFECTOR RECRUITMENT
#381METHODS AND COMPOSITIONS FOR SIMULTANEOUS EDITING OF BOTH STRANDS OF A TARGET DOUBLE-STRANDED NUCLEOTIDE SEQUENCE
#382SYSTEMS METHODS, AND COMPOSITIONS FOR TARGETED NUCLEIC ACID EDITING
#383IMPROVED MACROMOLECULES AND METHODS FOR DESIGNING SAME
#384COMPOSITIONS INCLUDING IFNE AND USES THEREOF
#385COMPOSITIONS AND METHODS FOR ENGINEERING TREG CELLS FOR TREATMENT OF DIABETES
#386COMPOSITIONS AND METHODS FOR TREATING A REFRACTORY OR RELAPSED CANCER OR A CHRONIC INFECTIOUS DISEASE
#387GENETICALLY MODIFIED MOUSE, METHODS FOR PRODUCING THE SAME, AND USES THEREOF
#388PATHOGEN-RESISTANT ANIMALS HAVING MODIFIED CD163 GENES
#389DOUBLE STRANDED CIRCULAR DNA VECTOR, METHOD FOR PRODUCING LINEAR COVALENTLY CLOSED DNA, AND FUSION POLYPEPTIDE CONTAINING PROTELOMERASE AND ENDONUCLEASE
#390COMPOSITIONS AND METHODS FOR RNA-ENCODED DNA-REPLACEMENT OF ALLELES
#391INTEGRATION OF LARGE NUCLEIC ACIDS INTO GENOMES
#392CASZ COMPOSITIONS AND METHODS OF USE
#393Compositions and Methods for TTR Gene Editing and Treating ATTR Amyloidosis
#394METHODS FOR THE TREATMENT OF NEURODEGENERATIVE DISORDERS
#395VITRO TRANSCRIPTION OF SPATIALLY CAPTURED NUCLEIC ACIDS
#396ENGINEERED CRISPR-CAS13F SYSTEM AND USES THEREOF
#397DEVELOPMENT OF RNA-TARGETED GENE EDITING TOOL
#398MOBILE GENETIC ELEMENTS FROM EPTESICUS FUSCUS
#399POLYNUCLEOTIDES ENCODING APOA-1 FUSION POLYPEPTIDES
#400COMPOSITIONS COMPRISING A MUSCLE ACTIVE PROMOTER AND METHODS OF USING THE SAME
#401GUIDE NUCLEIC ACID TARGETING MECP2 AND USES THEREOF
#402FUNCTIONAL AAV CAPSIDS FOR SYSTEMIC ADMINISTRATION
#403LIPID NANOPARTICLES
#404TARGETED DELIVERY OF ARMMS
#405TARGETING E COLI CELLS
#406THERAPEUTIC VESICLES AND METHODS OF PROCESSING THE SAME
#407EFFICIENT SYNTHESIS AND ASSEMBLY METHOD FOR LARGE FRAGMENT DNA BASED ON PROGRAMMABLE NUCLEASE ARGONAUTE
#408SYSTEMS AND METHODS FOR TRANSPOSING CARGO NUCLEOTIDE SEQUENCES
#409MORPHOREGULATORS FOR REGENERATION OF MAIZE SOMATIC EMBRYOS
#410TYPE II CAS PROTEINS AND APPLICATIONS THEREOF
#411S. PYOGENES CAS9 MUTANT GENES AND POLYPEPTIDES ENCODED BY SAME
#412COMPOSITIONS AND METHODS FOR NUCLEIC ACID PROCESSING USING BLOCKING AGENTS
#413Compositions and Methods for Kallikrein (KLKB1) Gene Editing
#414NOVEL CAS EFFECTOR PROTEINS, GENE EDITING SYSTEMS, AND USES THEREOF
#415GENETICALLY ENGINEERED T CELL FOR CELL THERAPY
#416CAS PROTEIN HAVING IMPROVED ACTIVITY AND USE THEREOF
#417RNA TARGETING COMPOSITIONS AND METHODS OF USE THEREOF
#418COMPOSITIONS AND METHODS FOR EPIGENOME EDITING TO ENHANCE T CELL THERAPY
#419NOVEL OMNI-59, 61, 67, 76, 79, 80, 81 AND 82 CRISPR NUCLEASES
#420COMPOSITIONS AND METHODS FOR EPIGENETIC EDITING
#421COMPOSITIONS AND METHODS FOR GENERATING CELLS WITH REDUCED IMMUNOGENICITY
#422ADAPTATIONS FOR HIGH EFFICIENCY I-F3-CRISPR-CAS SYSTEMS FOR GUIDE RNA-DIRECTED TRANSPOSITION IN HUMAN CELLS
#423METHODS AND COMPOSITIONS FOR ENHANCING EFFICACY OF THERAPEUTIC IMMUNE CELLS
#424CXCL-MODULATING COMPOSITIONS AND METHODS
#425GENE-REGULATING COMPOSITIONS AND METHODS FOR IMPROVED IMMUNOTHERAPY
#426COMPOSITIONS AND METHODS FOR ANALYZING DNA USING PARTITIONING AND BASE CONVERSION
#427A METHOD OF CELL ELECTROPORATION
#428METHODS AND COMPOSITIONS FOR PRODUCING TOBACCO PLANTS WITH REDUCED NICOTINIC ALKALOID LEVELS
#429METHODS FOR NON-TRANSGENIC GENOME EDITING IN PLANTS
#430SYSTEMS AND METHODS FOR GENETIC MODULATION TO TREAT OCULAR DISEASES
#431C2C9 NUCLEASE-BASED NOVEL GENOME EDITING SYSTEM AND USE THEREOF
#432MODIFIED BACTERIAL RETROELEMENT WITH ENHANCED DNA PRODUCTION
#433REVERSAL OF EXHAUSTION OF HIV-1 SPECIFIC CTLS BY CRISPR-MEDIATED DISRUPTION OF PD-1 GENE
#434ENGINEERED NUCLEASE AND USE THEREOF
#435RECOMBINOGENIC NUCLEIC ACID STRANDS IN SITU
#436Molecular Systems and Therapies Using the Same
#437Induction of IL-15/IL-15RA Expression in Immune Cells
#438COMPACT DRUG RESPONSIVE DOMAINS FOR REGULATION OF FUNCTION/ABUNDANCE AND DELIVERY OF POLYPEPTIDE PAYLOADS
#439ARTIFICIAL ANTIGEN-SPECIFIC IMMUNOREGULATORY T (AIRT) CELLS
#440Novel CRISPR-Cas sigma enzyme and system
#441RETROVIRAL-LIKE PARTICLE-REDUCED CHINESE HAMSTER OVARY PRODUCTION CELL LINES
#442COMPOSITIONS AND METHODS FOR HOMOLOGY-DIRECTED REPAIR GENE MODIFICATION
#443FUSION PROTEINS
#444RNA-GUIDED NUCLEASES AND ACTIVE FRAGMENTS AND VARIANTS THEREOF AND METHODS OF USE
#445CRISPR-AID USING CATALYTICALLY INACTIVE RNA-GUIDED ENDONUCLEASE
#446METHODS AND MEANS FOR GENOME EDITING USING GUIDE RNAS EXPRESSED UNDER CONTROL OF DIFFERENT PROMOTERS
#447NATIVE DELIVERY OF BIOMOLECULES INTO PLANT CELLS USING IONIC COMPLEXES WITH CELL-PENETRATING PEPTIDES
#448EFFICIENT TCR GENE EDITING IN T LYMPHOCYTES
#449FUSION PROTEINS
#450GENOME EDITING COMPOSITIONS AND METHODS FOR TREATMENT OF GLYCOGEN STORAGE DISEASE TYPE 1B
#451CFTR-MODULATING COMPOSITIONS AND METHODS
#452COMPOSITIONS AND METHODS FOR TARGETING, EDITING, OR MODIFYING GENES
#453CREATION AND USE OF GUIDE NUCLEIC ACIDS
#454CBLB ENDONUCLEASE VARIANTS, COMPOSITIONS, AND METHODS OF USE
#455DIRECT REPLACEMENT GENOME EDITING
#456METHODS AND COMPOSITIONS FOR EDITING SBDS GENE
#457LACHNOSPIRACEAE BACTERIUM ND2006 CAS12A MUTANT GENES AND POLYPEPTIDES ENCODED BY SAME
#458COMPOSITIONS AND METHODS FOR NUCLEIC ACID MODIFICATIONS
#459COMPOSITIONS AND METHODS FOR NUCLEIC ACID MODIFICATIONS
#460FUSION PROTEINS AND USES THEREOF FOR PRECISION EDITING
#461CRISPR ENZYME MUTATIONS REDUCING OFF-TARGET EFFECTS
#462SYSTEMS AND METHODS FOR TRANSPOSING CARGO NUCLEOTIDE SEQUENCES
#463DNASE ENZYMES ENGINEERED FOR IMPROVED STABILITY
#464CRISPR/SpCas9 VARIANT AND METHODS FOR ENHANCED CORRECTION OF DUCHENNE MUSCULAR DYSTROPHY MUTATIONS
#465DNase Variants and Compositions
#466ENGINEERED MICROORGANISMS AND METHODS OF MAKING AND USING SAME
#467GENETICALLY ENGINEERED T CELLS WITH REGNASE-1 AND/OR TGFBRII DISRUPTION HAVE IMPROVED FUNCTIONALITY AND PERSISTENCE
#468Materials & Methods for Treatment of Macular Degeneration
#469MULTIPLEXED REPRESSION OF IMMUNOSUPPRESSIVE GENES
#470COMPOSITIONS FOR THE MODIFICATION OF THE HUMAN NRAS AND KRAS GENES
#471COMPOSITIONS AND METHODS FOR MODULATING ALPHA-SYNUCLEIN EXPRESSION
#472MODIFIED CRISPR-BASED GENE EDITING SYSTEM AND METHODS OF USE
#473USE OF CHEMICAL EPIGENETIC MODIFIERS TO MODULATE GENE EXPRESSION
#474METHODS AND MATERIALS FOR INHIBITING/PREVENTING THE TRAFFICKING OF MONOCYTES TO THE CENTRAL NERVOUS SYSTEM
#475RECOMBINANT ADENOVIRUS VACCINE FOR AFRICAN SWINE FEVER AND METHOD FOR CONSTRUCTING SAME
#476G ALPHA Q/11 INHIBITORS FOR USE AS AN ANALGESIC
#477CULTURE OF TUMOR INFILTRATING LYMPHOCYTES FROM TUMOR DIGEST
#478METHOD FOR PRODUCING PROLIFERATIVE MACROPHAGE-LIKE CELLS (pMAC)
#479COMPOSITIONS AND METHODS FOR THE TREATMENT OF EXPANDED REPEAT-ASSOCIATED DISORDERS
#480TARGETING PTCHD1 AND NEURONAL CHOLESTEROL TO ENHANCE SAFETY OF OPIOID ANALGESICS
#481SYSTEMS AND METHODS OF ASSISTED REPRODUCTION AND PREVENTION OF GENETIC DEFECTS IN OFFSPRING USING INDUCED PLURIPOTENT STEM CELLS
#482TYPE I-B CRISPR-ASSOCIATED TRANSPOSASE SYSTEMS
#483COMPOSITIONS, SYSTEMS, AND METHODS FOR PRIME EDITING
#484GENETICALLY MODIFIED CELLS AND METHODS OF USE THEREOF
#485Nuclease-Independent Targeted Gene Editing Platform and Uses Thereof
#486Materials and Methods for Treatment of Hemoglobinopathies
#487COMPOSITIONS AND METHODS FOR INCREASING PERIDERM IN PLANT ROOTS
#488Compositions for Inducing Modifications of Target Endogenous Nucleic Acid Sequences in Nucleuses of Eukaryotic Cells
#489COMPOSITIONS, SYSTEMS, AND METHODS FOR REGULATION OF HEPATITIS B VIRUS THROUGH TARGETED GENE REPRESSION
#490REGULATION OF TRANSCRIPTION THROUGH CTCF LOOP ANCHORS
#491OPTIMIZED ENGINEERED MEGANUCLEASES HAVING SPECIFICITY FOR A RECOGNITION SEQUENCE IN THE HEPATITIS B VIRUS GENOME
#492NOVEL TYPE VI CRISPR ENZYMES AND SYSTEMS
#493VARIANT ALICYCLOBACILLUS CAS12b PROTEINS WITH IMPROVED DNA CLEAVAGE SELECTIVITY AND METHODS OF USE
#494CRISPR-CAS9 COMPOSITIONS AND METHODS WITH A NOVEL CAS9 PROTEIN FOR GENOME EDITING AND GENE REGULATION
#495GENETICALLY MODIFIED ORGANISMS FOR PRODUCING PSYCHOTROPIC ALKALOIDS
#496METHODS AND SYSTEMS FOR DIFFERENTIATION OF CELLS USING OPTOGENETICS
#497METHOD FOR THE SITE-SPECIFIC ENZYMATIC LABELLING OF NUCLEIC ACIDS IN VITRO BY INCORPORATION OF UNNATURAL NUCLEOTIDES
#498EPITOPE ENGINEERING OF CELL-SURFACE RECEPTORS
#499SPINACH PLANT RESISTANT TO DOWNY MILDEW AND NOVEL RESISTANCE GENE
#500METHODS FOR IMMUNOREGULATION BY MODULATING PLASMINOGEN-APPLE-NEMATODE (PAN) DOMAIN-CONTAINING PROTEINS
#501METHODS AND COMPOSITIONS RELATED TO NUCLEIC ACID-BASED FLUORESCENT NANOCLUSTER PROBES
#502QUANTIFICATION OF ON-TARGET AND OFF-TARGET GENE EDITING ACTIVITY
#503ENZYMATIC SYNTHESIS OF POLYNUCLEOTIDE
#504SYSTEMS AND METHODS FOR CELL MODIFICATION
#505SYSTEMS, METHODS, AND COMPOSITIONS FOR TARGETED GENE MANIPULATION AND USES THEREOF
#506TARGETED GENE EDITING PLATFORM INDEPENDENT OF DNA DOUBLE STRAND BREAK AND USES THEREOF
#507Carrier for functional nucleic acid and protein introduction
#508IMPROVED CELL LINES AND METHODS FOR THE PRODUCTION OF ADENO-ASSOCIATED VECTORS
#509IRON MAN (IMA) OVEREXPRESSION INCREASES DISEASE RESISTANCE
#510Compositions and Methods for Suppression of Flowering in Sugarcane and Energycane
#511DOMESTICATION OF A LEGUME PLANT
#512COMPOSITIONS AND METHODS FOR IMPROVED RHIZOBIUM-MEDIATED PLANT TRANSFORMATION
#513ACTIVATION OF NONCODING HOST GENE LOCI
#514Tandem Guide RNAs (TG-RNAs) and Their Use in Genome Editing
#515CRISPR-TRANSPOSON SYSTEMS FOR DNA MODIFICATION
#516METHOD OF INTRODUCING A PLURALITY OF GENE DRIVES INTO A POPULATION
#517SYSTEMS AND METHODS OF NOVEL CRISPR-CAS PROTEINS FOR IN-VITRO APPLICATIONS
#518Mutant Cpf1 Endonucleases
#519METHODS AND COMPOSITIONS FOR ADVANCED BREEDING THROUGH TARGETED CHROMOSOME ENGINEERING
#520NUCLEIC ACID-GUIDED NICKASE FUSION PROTEINS
#521METHODS OF GENERATING A POPULATION OF NEURONS FROM HUMAN GLIAL PROGENITOR CELLS AND GENETIC CONSTRUCTS FOR CARRYING OUT SUCH METHODS
#522TRANSMEMBRANE RECEPTOR GENE EDITING
#523COMPOSITIONS AND METHODS FOR IN VIVO NUCLEASE-MEDIATED TREATMENT OF ORNITHINE TRANSCARBAMYLASE (OTC) DEFICIENCY
#524BASE EDITING APPROACHES FOR THE TREATMENT OF BETA-THALASSEMIA
#525SUPPLEMENTATION OF LIVER ENZYME EXPRESSION
#526MEDICINE FOR DISEASE CAUSED BY FRAME-SHIFT MUTATION
#527GENE EDITING TO IMPROVE JOINT FUNCTION
#528MODIFIED IMMUNE CELLS FOR TREATING AND/OR PREVENTING METASTASIS
#529MODIFIED IMMUNE EFFECTOR CELLS AND USES THEREOF
#530NUCLEIC ACID CONSTRUCT BASED ON CRE-LOXP AND CRISPR AND USE THEREOF
#531METHODS FOR VARIANT DETECTION
#532ENGINEERED RETRONS AND METHODS OF USE
#533METHODS FOR IMPROVED HOMOLOGOUS RECOMBINATION AND COMPOSITIONS THEREOF
#534PLANT VIRUS MOVEMENT PROTEINS AND METHODS OF USING SAME
#535TOMATOES CONTAINING HIGH LEVELS OF 7-DEHYDROCHOLESTEROL AND PREPARATION METHOD THEREFOR
#536USE OF CAS12F NUCLEASES IN PRODUCTION OF EXPRESSION MODULATED PLANT MATERIALS
#537Applications of Streptococcus-derived Cas9 nucleases on minimal Adenine-rich PAM targets
#538EFFECTOR PROTEINS AND METHODS OF USE
#539COMPOSITIONS, SYSTEMS, AND METHODS FOR PROGRAMMING T CELL PHENOTYPES THROUGH TARGETED GENE REPRESSION
#540MUTANT CYTIDINE DEAMINASES WITH IMPROVED EDITING PRECISION
#541ENGINEERED MEGANUCLEASES SPECIFIC FOR RECOGNITION SEQUENCES IN THE HEPATITIS B VIRUS GENOME
#542RATIONALLY-DESIGNED SINGLE-CHAIN MEGANUCLEASES WITH NON-PALINDROMIC RECOGNITION SEQUENCES
#543RNASE-PON1 FUSION POLYPEPTIDES AND RELATED COMPOSITIONS AND METHODS
#544NOVEL CRISPR DNA AND RNA TARGETING ENZYMES AND SYSTEMS
#545SYSTEMS AND METHODS FOR NUCLEIC ACID DETECTION
#546ENGINEERED MEGANUCLEASES SPECIFIC FOR RECOGNITION SEQUENCES IN THE PCSK9 GENE
#547TREATMENT FOR NUCLEOTIDE REPEAT EXPANSION DISEASE
#548STREPTOCOCCUS PYOGENES-DERIVED CAS9 VARIANT
#549COMBINATION BCL11A ENHANCER EDITING
#550NUCLEOSIDE TRIPHOSPHATE TRANSPORTER AND USES THEREOF
#551BASE EDITING OF ANGPTL3 AND METHODS OF USING SAME FOR TREATMENT OF DISEASE
#552DYSTROPHIN GENE EXON DELETION USING ENGINEERED NUCLEASES
#553TRANS-SPLICING METHODS AND COMPOSITIONS FOR GENERATION OF SINGLE SEX OFFSPRING
#554ABERRANT VIRAL RNA DETECTION USING CAS13
#555Method and Reagent Kit for Targeted Genomic Enrichment
#556Methods and Compositions for RNA-Directed Target DNA Modification and For RNA-Directed Modulation of Transcription
#557CRISPR-CAS SYSTEMS AND USES THEREOF
#558COMPOSITIONS AND METHODS FOR IMPEDING TRANSCRIPTION OF EXPANDED MICROSATELLITE REPEATS
#559PLANT GRAIN SIZE REGULATION GENE AND USE THEREOF
#560METHODS AND COMPOSITIONS FOR TRICHOME REMOVAL
#561Compositions for Inducing Modifications of Target Endogenous Nucleic Acid Sequences in Nucleuses of Eukaryotic Cells
#562Compositions for Inducing Modifications of Target Endogenous Nucleic Acid Sequences in Nucleuses of Eukaryotic Cells
#563Compositions and Methods for Enhancing AAV Therapy and Decreasing Tropism of AAV to the Liver
#564COMPOSITIONS AND METHODS FOR GENE EDITING BY TARGETING TRANSFERRIN
#565METHODS FOR TREATING RHEUMATOID ARTHRITIS USING CTLA4-PON1 FUSION PROTEINS
#566MESSENGER RNA ENCODING CAS9 FOR USE IN GENOME-EDITING SYSTEMS
#567METHODS FOR IN VIVO DELIVERY AND DETECTION OF CLUSTERED REGULARLY INTERSPACED SHORT PALINDROMIC REPEAT SYSTEMS UTILIZING BACULOVIRUS VECTOR-MAGNETIC NANOPARTICLE COMPLEXES
#568ENGINEERED CAS-PHI PROTEINS AND USES THEREOF
#569GENETIC ENGINEERING OF BACTERIOPHAGES USING CRISPR-CAS13A
#570ENHANCED IMMUNE EFFECTOR CELLS AND USE THEREOF
#571COMPOSITIONS AND METHODS FOR PRODUCING SMOOTH MUSCLE CELLS
#572T CELLS WITH IMPROVED FUNCTIONALITY
#573COMPOSITIONS AND METHODS FOR MODIFYING A HUMAN DYSTROPHIN GENE
#574DISRUPTION OF THE SECRETION OF INSULIN-LIKE GROWTH FACTOR 2 FOR CANCER TREATMENT
#575METHODS OF TARGETING REPETITIVE RNA IN HUNTINGTON'S DISEASE
#576METHODS AND COMPOSITIONS FOR TREATING LIPOPROTEIN-RELATED DISEASES
#577Transdifferentiation of Pancreatic Duct Cells Into Beta-Like Cells
#578ADENOSINE DEAMINASE BASE EDITORS AND METHODS FOR USE THEREOF
#579BASE EDITING AND CRISPR/CAS9 GENE EDITING STRATEGIES TO CORRECT CD3 SEVERE COMBINED IMMUNODEFICIENCY IN HEMATOPOIETIC STEM CELLS
#580METHOD FOR PRODUCING STERILIZED MALE INDIVIDUALS OF MARINE FISH, METHOD FOR PREVENTING REPRODUCTION OF MARINE FISH, AND STERILIZED MALE INDIVIDUALS OF MARINE FISH
#581MEANS AND METHOD FOR FLUORESCENT IN SITU HYBRIDIZATION USING CRISPR-CAS9 VARIANTS AND A NUCLEASE
#582METHODS FOR VARIANT DETECTION
#583METHODS FOR RECOMBINANT PROTEIN EXPRESSION IN EUKARYOTIC CELLS
#584NOVEL TRANSCRIPTIONAL REGULATOR 30S RIBOSOMAL PROTEIN REGULATES PHYSIOLOGICAL RESPONSES IN PLANT CELLS
#585ORGANELLE GENOME MODIFICATION USING POLYNUCLEOTIDE GUIDED ENDONUCLEASE
#586COMPOSITIONS, SYSTEMS, AND METHODS FOR REGULATION OF HEPATITIS B VIRUS THROUGH TARGETED GENE REPRESSION
#587COMPOSITIONS
#588CATALYTICALLY DEAD ENGINEERED PROTEINS
#589ISOLATED NUCLEASE AND USE THEREOF
#590CELL DATA RECORDERS AND USES THEREOF
#591TRANSCRIPTION REGULATION SYSTEM BASED ON CRISPRI AND CRISPRA, AND ESTABLISHMENT METHOD THEREFOR AND USE THEREOF
#592METHODS TO ACCELERATE STEM CELL DIFFERENTIATION TO CARDIOMYOCYTES
#593COMPOSITIONS AND METHODS FOR PRODUCING PRIMORDIAL GERM CELL-LIKE CELLS
#594INHIBITOR-RESISTANT MGMT MODIFICATIONS AND MODIFICATION OF MGMT-ENCODING NUCLEIC ACIDS
#595MRNA REGULON THERAPY FOR THE TREATMENT OF HAPLOINSUFFICIENCY DISORDERS
#596CRISPR-MEDIATED MANIPULATION OF APP EXPRESSION AS A THERAPEUTIC APPROACH FOR AMYLOID PATHOLOGIES
#597DEPLETION OF CELLS BY CRISPR NUCLEASES
#598COMPOSITIONS AND METHODS FOR CELLULAR IMMUNOLOGY
#599COMPOSITIONS, SYSTEMS, AND METHODS FOR PROGRAMMING T CELL PHENOTYPES THROUGH TARGETED GENE ACTIVATION
#600REGULATION OF CELLS AND ORGANISMS