Patents-Review.com
ClassID:

109048 ⎘

C12N15/113 - page 20 - CPC Classification

Classification description:

Mutation or genetic engineering; DNA or RNA concerning genetic engineering, vectors, e.g. plasmids, or their isolation, preparation or purification; Use of hosts therefor; Recombinant DNA-technology; DNA or RNA fragments; Modified forms thereof Non-coding nucleic acids modulating the expression of genes, e.g. antisense oligonucleotides

Recent Application in this class:
#5701
20200080085
2020-03-12

Serpina1 iRNA compositions and methods of use thereof

 #5702
20200080084
2020-03-12

TLR3 ligands that activate both epithelial and myeloid cells

 #5703
20200080083
2020-03-12

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF

 #5704
20200080082
2020-03-12

Materials and methods for treatment of primary hyperoxaluria type 1 (PH1) and other alanine-glyoxylate aminotransferase (AGXT) gene related conditions or disorders

 #5705
20200080081
2020-03-12

A METHOD FOR REGULATING THE FUNCTION OF A HEART CELL, RELATED NUCLEOTIDES AND COMPOUNDS

 #5706
20200080080
2020-03-12

Therapeutic drug for Alport's syndrome

 #5707
20200080079
2020-03-12

Processes for preparing phosphorodiamidate morpholino oligomers

 #5708
20200080077
2020-03-12

COMPOSITIONS AND METHODS FOR ENHANCING HOMOLOGOUS RECOMBINATION

 #5709
20200078471
2020-03-12

RENAL CLEARABLE DRUG DELIVERING NANOPARTICLES AND METHODS OF USE THEREFOR

 #5710
20200078465
2020-03-12

Exon skipping oligomer conjugates for muscular dystrophy

 #5711
20200078389
2020-03-12

Compositions and methods for modulating MECP2 expression

 #5712
20200077663
2020-03-12

ALTERING MICROBIAL POPULATIONS & MODIFYING MICROBIOTA

 #5713
20200071728
2020-03-05

METHODS AND COMPOSITIONS FOR RNA-DIRECTED TARGET DNA MODIFICATION AND FOR RNA-DIRECTED MODULATION OF TRANSCRIPTION

 #5714
20200071726
2020-03-05

Gene therapies for lysosomal disorders

 #5715
20200071700
2020-03-05

COMPOSITION AND METHOD OF USING MIR-302 PRECURSORS AS DRUGS FOR TREATING ALZHEIMER'S DISEASES

 #5716
20200071699
2020-03-05

TREATMENT OF ALZHEIMERS DISEASE WITH MICRO RNA AND GHRELIN

 #5717
20200071698
2020-03-05

Therapeutic agent for treating cancer comprising anti-miRNA-albumin composite

 #5718
20200071697
2020-03-05

MicroRNA inhibitor

 #5719
20200071696
2020-03-05

Compositions of asymmetric interfering RNA and uses thereof

 #5720
20200071695
2020-03-05

Method and pharmaceutical composition for treating cancer

 #5721
20200071684
2020-03-05

Engineered nucleic-acid targeting nucleic acids

 #5722
20200071369
2020-03-05

Targeted DNA demethylation and methylation

 #5723
20200069723
2020-03-05

COMPLEMENT COMPONENT C5 iRNA COMPOSITIONS AND METHODS OF USE THEREOF

 #5724
20200069721
2020-03-05

Staufen1 agents and associated methods

 #5725
20200069720
2020-03-05

MicroRNA (miRNA) and Downstream Targets for Diagnostic and Therapeutic Purposes

 #5726
20200068901
2020-03-05

ALTERING MICROBIAL POPULATIONS & MODIFYING MICROBIOTA

 #5727
20200063162
2020-02-27

Vector-free intracellular delivery by reversible permeabilization

 #5728
20200063161
2020-02-27

Methods and compositions for the activation of gamma-delta T-cells

 #5729
20200063151
2020-02-27

U6 polymerase III promoter and methods of use

 #5730
20200063147
2020-02-27

CRISPR-CAS COMPONENT SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION

 #5731
20200063140
2020-02-27

Methods of treating cancer harboring hemizygous loss of TP53

 #5732
20200063136
2020-02-27

Anti-connexin compounds targeted to connexins and methods of use thereof

 #5733
20200063135
2020-02-27

METHODS, SYSTEMS, AND COMPOSITIONS FOR NEURONAL DIFFERENTIATION OF MULTIPOTENT STROMAL CELLS

 #5734
20200063134
2020-02-27

Oligonucleotide therapy for Leber Congenital Amaurosis

 #5735
20200063133
2020-02-27

Products and compositions

 #5736
20200063132
2020-02-27

Regulation of MIR-143 using nucleic acid molecules

 #5737
20200063131
2020-02-27

System and method for cell type-specific translation of RNA molecules in eukaryotes

 #5738
20200063130
2020-02-27

CHIMERIC RNA OLIGONUCLEOTIDES AND USES THEREOF

 #5739
20200063129
2020-02-27

Therapeutic alteration of transplantable tissues through in situ or ex vivo exposure to RNA interference molecules

 #5740
20200063128
2020-02-27

Compositions of asymmetric interfering RNA and uses thereof

 #5741
20200062719
2020-02-27

Application of Imidazopyridine Derivatives in Regenerative Medicine

 #5742
20200061207
2020-02-27

Method of delivering genes and drugs to a posterior segment of an eye

 #5743
20200060980
2020-02-27

Compositions for facilitating membrane fusion and uses thereof

 #5744
20200057052
2020-02-20

Oligonucleotides for inducing paternal UBE3A expression

 #5745
20200056248
2020-02-20

METHOD FOR SORTING TISSUE CELLS

 #5746
20200056236
2020-02-20

Methods for detection of RNase activity

 #5747
20200056208
2020-02-20

Systems and methods for one-shot guide RNA (ogRNA) targeting of endogenous and source DNA

 #5748
20200056206
2020-02-20

CRISPR-BASED TREATMENT OF FRIEDREICH ATAXIA

 #5749
20200056187
2020-02-20

SELECTIVE ANTISENSE COMPOUNDS AND USES THEREOF

 #5750
20200056184
2020-02-20

Treatment of tumors with miRNA targeting CDK4/CDK6

 #5751
20200056180
2020-02-20

Rotationally sequestered translators

 #5752
20200056179
2020-02-20

Compounds and methods for reducing ATXN2 expression

 #5753
20200056178
2020-02-20

Antisense oligonucleic acid

 #5754
20200056177
2020-02-20

LONG NON-CODING RNA USED FOR ANTICANCER THERAPY

 #5755
20200056176
2020-02-20

MODULATION OF APOLIPOPROTEIN CIII (APOCIII) EXPRESSION

 #5756
20200056175
2020-02-20

COMPOSITIONS AND METHODS FOR INHIBITIION OF EXPRESSION OF PROTEIN C (PROC) GENES

 #5757
20200056174
2020-02-20

COMPOSITIONS AND METHODS OF TREATING CANCER

 #5758
20200056173
2020-02-20

Oligonucleotide compositions and methods thereof

 #5759
20200056167
2020-02-20

Modified nucleic acids, hybrid guide RNAs, and uses thereof

 #5760
20200055948
2020-02-20

CELLS EXPRESSING A BCMA-TARGETING CHIMERIC ANTIGEN RECEPTOR, AND COMBINATION THERAPY WITH A GAMMA SECRETASE INHIBITOR

 #5761
20200055890
2020-02-20

Nucleic acid compound and oligonucleotide

 #5762
20200054689
2020-02-20

Compositions comprising bacterially derived minicells and methods of using the same

 #5763
20200054558
2020-02-20

AEROSOL DELIVERY SYSTEMS, COMPOSITIONS AND METHODS

 #5764
20200048718
2020-02-13

COMPOSITIONS AND METHODS FOR ANALYZING HETEROGENEOUS SAMPLES

 #5765
20200048638
2020-02-13

COMPOSITIONS AND METHODS FOR MODULATING COMPLEMENT FACTOR B EXPRESSION

 #5766
20200048637
2020-02-13

RNAi-MEDIATED INHIBITION OF HIF1A FOR TREATMENT OF OCULAR ANGIOGENESIS

 #5767
20200048635
2020-02-13

Methods to detect motor neuron disease comprising micro-RNAs

 #5768
20200048634
2020-02-13

METHODS TO MODULATE PROTEIN TRANSLATION EFFICIENCY

 #5769
20200048633
2020-02-13

Novel Structurally Designed shRNAs

 #5770
20200048632
2020-02-13

Antisense Oligonucleotides for Treatment of Spinal Muscular Atrophy

 #5771
20200048622
2020-02-13

Engineered cascade components and cascade complexes

 #5772
20200048615
2020-02-13

Inhibition of serotonin expression in gut enteroendocrine cells results in conversion to insulin-positive cells

 #5773
20200048335
2020-02-13

NOVEL USE OF REGULATORY T CELL-SPECIFIC SURFACE PROTEIN LRIG-1

 #5774
20200046851
2020-02-13

Gene therapy for retinitis pigmentosa

 #5775
20200046753
2020-02-13

Modified pT7/T7 Polymerase System for Sustained shRNA Expression in Cytoplasm and Liposome Transporter Comprising the Same

 #5776
20200040401
2020-02-06

METHOD FOR DETERMINING, PREDICTING AND TREATING CANCER

 #5777
20200040399
2020-02-06

Mutant calreticulin for the diagnosis of myeloid malignancies

 #5778
20200040340
2020-02-06

ANTISENSE POLYNUCLEOTIDES TO INDUCE EXON SKIPPING AND METHOD OF TREATING DYSTROPHIES

 #5779
20200040339
2020-02-06

P-ethoxy nucleic acids for STAT3 inhibition

 #5780
20200040338
2020-02-06

RNA-based regulatory technologies for miRNA sensors

 #5781
20200040337
2020-02-06

COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

 #5782
20200040336
2020-02-06

EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

 #5783
20200040335
2020-02-06

Gene silencing

 #5784
20200040334
2020-02-06

COMPOSITIONS AND METHODS FOR GENE EDITING

 #5785
20200040333
2020-02-06

Compositions and methods for modulating SMN gene family expression

 #5786
20200040332
2020-02-06

Methods and pharmaceutical compositions for the treatment of cystic fibrosis

 #5787
20200040331
2020-02-06

Morpholino oligonucleotide manufacturing method

 #5788
20200040100
2020-02-06

Multimodal cancer therapy comprising chimeric viral/nonviral nanoparticles and anticancer agents

 #5789
20200038426
2020-02-06

Synergistic combination of oligonucleotides and chemotherapeutic for treating cancer

 #5790
20200038336
2020-02-06

Particles and compositions comprising the same for transfection

 #5791
20200033348
2020-01-30

Method for diagnosis, prognosis and determination of treatment for cutaneous t-cell lymphoma

 #5792
20200032341
2020-01-30

Diagnosis and treatment of psoriatic arthritis

 #5793
20200032302
2020-01-30

Structuring fats and methods of producing structuring fats

 #5794
20200032278
2020-01-30

CRISPR-CAS COMPONENT SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION

 #5795
20200032277
2020-01-30

CRISPR-CAS COMPONENT SYSTEMS, METHODS AND COMPOSITIONS FOR SEQUENCE MANIPULATION

 #5796
20200032264
2020-01-30

METHODS FOR DOSING AND MONITORING SMAD7 ANTISENSE OLIGONUCLEOTIDE TREATMENT USING BIOMARKER LEVELS

 #5797
20200032263
2020-01-30

Treatment of down syndrome gene related diseases by inhibition of natural antisense transcript to a down syndrome gene

 #5798
20200032262
2020-01-30

Technique for treating cancer using structurally-reinforced S-TuD

 #5799
20200032261
2020-01-30

Methods and compositions for controlling efficacy of RNA silencing

 #5800
20200032260
2020-01-30

Compositions and methods for modulation of IKBKAP splicing

 #5801
20200032259
2020-01-30

Complement component C5 iRNA compositions and methods of use thereof

 #5802
20200032258
2020-01-30

COMPLEMENT COMPONENT C5 IRNA COMPOSITIONS AND METHODS OF USE THEREOF

 #5803
20200032257
2020-01-30

Methods for treating Alzheimer's disease

 #5804
20200032256
2020-01-30

RAAV-based compositions and methods for treating amyotrophic lateral sclerosis

 #5805
20200032255
2020-01-30

Methods and compositions for the treatment of cancer or other diseases

 #5806
20200032254
2020-01-30

Antisense antibacterial compounds and methods

 #5807
20200031884
2020-01-30

MICROPEPTIDES AND USE OF SAME FOR MODULATING GENE EXPRESSION

 #5808
20200031862
2020-01-30

LIGAND-MODIFIED DOUBLE-STRANDED NUCLEIC ACIDS

 #5809
20200030459
2020-01-30

TARGETED DISRUPTION OF A CSF1-DAP12 PATHWAY MEMBER GENE FOR THE TREATMENT OF NEUROPATHIC PAIN

 #5810
20200030359
2020-01-30

Inhibition of stress granule formation through manipulation of UBAP2L

 #5811
20200030323
2020-01-30

Treating cognitive decline and other neurodegenerative conditions by selectively removing senescent cells from neurological tissue

 #5812
20200030292
2020-01-30

GFI1 inhibitors for the treatment of hyperglycemia

 #5813
20200024652
2020-01-23

Method for blocking miRNA

 #5814
20200024625
2020-01-23

constitutive expression vector promoter screened on the basis of transcriptome sequencing, screening method thereof, and applications thereof

 #5815
20200024618
2020-01-23

RNA-guided transcriptional regulation

 #5816
20200024617
2020-01-23

Recombinant AAV variants and uses thereof

 #5817
20200024615
2020-01-23

Method for Precise Identification, Targeting and Delivery of Directed Therapies for Destruction of Cancerous Cells

 #5818
20200024606
2020-01-23

Antisense oligomers for treatment of conditions and diseases

 #5819
20200024604
2020-01-23

Exosomes and micro-ribonucleic acids for tissue regeneration

 #5820
20200024603
2020-01-23

Antisense oligomers for treatment of conditions and diseases

 #5821
20200024602
2020-01-23

METHODS AND COMPOSITIONS FOR ENHANCING THE EFFICACY AND SPECIFICITY OF SINGLE AND DOUBLE BLUNT-ENDED siRNA

 #5822
20200024601
2020-01-23

Antisense oligonucleotides to treat dystrophic epidermolysis bullosa

 #5823
20200024600
2020-01-23

Oligonucleotides for modulating ATXN2 expression

 #5824
20200024599
2020-01-23

RNA interference for the treatment of gain-of-function disorders

 #5825
20200024598
2020-01-23

ISOLATED POLYNUCLEOTIDE COMPRISING PROMOTER REGION, HOST CELL COMPRISING THE SAME, AND METHOD OF EXPRESSING TARGET GENE IN THE HOST CELL

 #5826
20200024593
2020-01-23

Methods and compositions for treating Leber congenital amaurosis

 #5827
20200023060
2020-01-23

COMPOSITIONS AND METHODS FOR INCREASING THE SERUM HALF-LIFE OF A THERAPEUTIC AGENT TARGETING COMPLEMENT C5

 #5828
20200022957
2020-01-23

KINASE AND UBIQUITIN LIGASE INHIBITORS AND USES THEREOF

 #5829
20200022913
2020-01-23

Liposomal particles, methods of making same and uses thereof

 #5830
20200017884
2020-01-16

Integration sites and uses thereof

 #5831
20200017883
2020-01-16

COMPOSITIONS AND METHODS FOR STUDYING THE TAT GENE

 #5832
20200017879
2020-01-16

RNA-guided nucleic acid modifying enzymes and methods of use thereof

 #5833
20200017858
2020-01-16

Regulation of gene expression through aptamer-modulated polyadenylation

 #5834
20200017857
2020-01-16

Methods of treating porphyria

 #5835
20200017856
2020-01-16

Targeting human satellite II (HSATII)

 #5836
20200017855
2020-01-16

Compositions comprising alternating 2′-modified nucleosides for use in gene modulation

 #5837
20200017854
2020-01-16

MODULATION OF APOLIPOPROTEIN C-III (APOCIII) EXPRESSION IN LIPOPROTEIN LIPASE DEFICIENT (LPLD) POPULATIONS

 #5838
20200017853
2020-01-16

COMPOSITIONS AND METHODS FOR PAIN AMELIORATION VIA MODIFICATION OF GENE EXPRESSION

 #5839
20200017849
2020-01-16

CRISPR/CAS-related methods and compositions for treating Leber's Congenital Amaurosis 10 (LCA10)

 #5840
20200017828
2020-01-16

Human neural precursor cells with inducible STIM1 knockdown

 #5841
20200016280
2020-01-16

Compositions for enhancing transport of molecules into cells

 #5842
20200016189
2020-01-16

METHOD FOR TREATING SCHIZOPHRENIA

 #5843
20200010840
2020-01-09

Targeted control of pests and pathogens by plant delivery of 2'F-ANA-oligonucleotides

 #5844
20200010832
2020-01-09

NEUROPROTECTIVE MOLECULES AND METHODS OF TREATING NEUROLOGICAL DISORDERS AND INDUCING STRESS GRANULES

 #5845
20200010831
2020-01-09

Oligonucleotides for modulating Tau expression

 #5846
20200010830
2020-01-09

Engineered cells with decreased gene expression resulting in increased viral production

 #5847
20200010576
2020-01-09

Capped cyclodextrin-hydrophobic moiety conjugate, cyclodextrin supramolecular polymer, and cyclodextrin-siRNA complex and method of synthesis thereof

 #5848
20200009181
2020-01-09

Antisense oligonucleotides for inhibition of PD-L1 expression and treating cancer

 #5849
20200009177
2020-01-09

METHODS OF INHIBITING CANCER STEM CELLS WITH HMGA1 INHIBITORS

 #5850
20200009149
2020-01-09

Methods of treating autism spectrum disorders

 #5851
20200002758
2020-01-02

Sensor and sensing system

 #5852
20200002708
2020-01-02

Tobacco plant and production method thereof

 #5853
20200002702
2020-01-02

HIPPO AND DYSTROPHIN COMPLEX SIGNALING IN CARDIOMYOCYTE RENEWAL

 #5854
20200002701
2020-01-02

Reduced size self-delivering RNAI compounds

 #5855
20200002419
2020-01-02

Costimulatory B7-H1 in renal cell carcinoma patients: indicator of tumor aggressiveness and potential therapeutic target

 #5856
20200001120
2020-01-02

APPARATUS, METHOD, AND USE FOR ULTRASOUND MEDIATED MICROBUBBLE DELIVERY OF PHARMACEUTICAL COMPOSITIONS

 #5857
20200000936
2020-01-02

BLOCK COPOLYMERS AND USES THEREOF

 #5858
20200000851
2020-01-02

Targeted replacement of endogenous T cell receptors

 #5859
20190390201
2019-12-26

Interfering RNA molecules

 #5860
20190390198
2019-12-26

Methods and compositions for the specific inhibition of alpha-1 antitrypsin by double-stranded RNA

 #5861
20190390197
2019-12-26

OLIGONUCLEOTIDE COMPOSITIONS AND METHODS THEREOF

 #5862
20190388551
2019-12-26

Nucleic acid constructs and methods of using the same

 #5863
20190388523
2019-12-26

Factor IX gene therapy

 #5864
20190388475
2019-12-26

STEM CELL MICROPARTICLES

 #5865
20190388454
2019-12-26

Methods for treating NLRP3 inflammasome-associated diseases, and methods of identifying agents useful therefor

 #5866
20190388413
2019-12-26

Compositions and methods for treating endometriosis

 #5867
20190383797
2019-12-19

Methods of selecting therapeutic molecules

 #5868
20190382837
2019-12-19

Methods and control compositions for sequencing

 #5869
20190382801
2019-12-19

NOVEL CRISPR ENZYMES AND SYSTEMS

 #5870
20190382800
2019-12-19

NOVEL CRISPR ENZYMES AND SYSTEMS

 #5871
20190382797
2019-12-19

Methods and systems for guide RNA design and use

 #5872
20190382763
2019-12-19

Compositions and Methods for Inhibition of Factor XII Gene Expression

 #5873
20190382762
2019-12-19

Chemically-modified siRNA

 #5874
20190382761
2019-12-19

Use of MIR-92A or MIR-145 in the treatment of Angelman syndrome

 #5875
20190382760
2019-12-19

ANTISENSE COMPOUNDS TARGETING GENES ASSOCIATED WITH FIBRONECTIN

 #5876
20190382758
2019-12-19

Artificial single guide RNA and use thereof

 #5877
20190382757
2019-12-19

Control compositions and methods for sequencing

 #5878
20190382752
2019-12-19

Method for re-expression of different hypermethylated genes involved in fibrosis, like hypermethylated RASAL1 and use thereof in treatment of fibrosis as well as kit of parts for re-expression of hypermethylated genes including RASAL1 in a subject

 #5879
20190382746
2019-12-19

Artificial ribosomes for fully programmable synthesis of nonribosomal peptides

 #5880
20190381132
2019-12-19

METHODS AND COMPOSITIONS FOR TREATMENT OF IONIZING RADIATION RESISTANT TUMORS

 #5881
20190381105
2019-12-19

STEM CELL MICROPARTICLES AND miRNA

 #5882
20190381089
2019-12-19

Oligonucleotides to treat eye disease

 #5883
20190381086
2019-12-19

INHIBITION OF NEDDYLATION USING GLYCYL-tRNA SYNTHETASE INHIBITORS

 #5884
20190376091
2019-12-12

Primary cell gene editing

 #5885
20190376086
2019-12-12

Primary cell gene editing

 #5886
20190376074
2019-12-12

U6 polymerase III promoter and methods of use

 #5887
20190376065
2019-12-12

RNAi therapy for treatment and/or prevention of glaucoma

 #5888
20190376062
2019-12-12

siRNA sequence-independent modification formats for reducing off-target phenotypic effects in RNAI, and stabilized forms thereof

 #5889
20190376061
2019-12-12

IncRNAS for therapy and diagnosis of angiogenesis

 #5890
20190374655
2019-12-12

Materials and methods for treatment of Duchenne Muscular Dystrophy

 #5891
20190374567
2019-12-12

Reverse Transcriptase Dependent Conversion of RNA Templates Into DNA

 #5892
20190374472
2019-12-12

Antisense Compositions and Methods of Making and Using Same

 #5893
20190367948
2019-12-05

Orthogonal Cas9 proteins for RNA-guided gene regulation and editing

 #5894
20190367943
2019-12-05

Compositions and related methods for modulating endosymbionts

 #5895
20190367935
2019-12-05

Transgenic plants with enhanced traits

 #5896
20190367930
2019-12-05

METHODS FOR DECOUPLING CELL GROWTH FROM PRODUCTION OF BIOCHEMICALS AND RECOMBINANT POLYPEPTIDES

 #5897
20190367926
2019-12-05

Methods and compositions for treating malignant tumors associated with KRAS mutation

 #5898
20190367920
2019-12-05

ANTISENSE OLIGONUCLEOTIDES FOR MODULATING NFKB1 EXPRESSION

 #5899
20190367919
2019-12-05

Antisense oligonucleotides for the treatment of Stargardt disease

 #5900
20190367918
2019-12-05

COMPOSITIONS AND METHODS FOR DELIVERING MICRORNA

 #5901
20190367917
2019-12-05

Diagnosing COL6-related disorders and methods for treating same

 #5902
20190367916
2019-12-05

Compositions for modulating C9ORF72 expression

 #5903
20190367915
2019-12-05

Method for assaying MicroRNA, cancer therapeutic agent, and medical composition containing same for cancer therapy

 #5904
20190367914
2019-12-05

Conjugated antisense compounds and their use

 #5905
20190367913
2019-12-05

Ribozyme with tRNA synthetase activity and methods of manufacturing and using the same

 #5906
20190367912
2019-12-05

Nucleotide sequence and method for controlling insect infestation

 #5907
20190367891
2019-12-05

Programmable CAS9-recombinase fusion proteins and uses thereof

 #5908
20190367566
2019-12-05

Recombinant polypepties for membrane fusion and uses thereof

 #5909
20190365929
2019-12-05

MATERIALS AND METHODS FOR TREATMENT OF DYSTROPHIC EPIDERMOLYSIS BULLOSA (DEB) AND OTHER COLLAGEN TYPE VII ALPHA 1 CHAIN (COL7A1) GENE RELATED CONDITIONS OR DISORDERS

 #5910
20190365924
2019-12-05

Delivery of target specific nucleases

 #5911
20190365919
2019-12-05

Exon skipping oligomer conjugates for muscular dystrophy

 #5912
20190365918
2019-12-05

Exon skipping oligomer conjugates for muscular dystrophy

 #5913
20190365810
2019-12-05

Coordinating gene expression using RNA destabilizing elements

 #5914
20190365806
2019-12-05

IMMUNOLOGICALLY DISCERNIBLE CELL SURFACE VARIANTS FOR USE IN CELL THERAPY

 #5915
20190365795
2019-12-05

OLIGONUCLEOTIDES FOR MODULATING ATXN2 EXPRESSION

 #5916
20190365716
2019-12-05

Method for treating neurodegenerative diseases

 #5917
20190364862
2019-12-05

DMD REPORTER MODELS CONTAINING HUMANIZED DUCHENNE MUSCULAR DYSTROPHY MUTATIONS

 #5918
20190360056
2019-11-28

Fusion genes associated with progressive prostate cancer

 #5919
20190360002
2019-11-28

Thermostable Cas9 nucleases

 #5920
20190360001
2019-11-28

Nucleic acid-guided nucleases

 #5921
20190359994
2019-11-28

BIOLOGICAL CONTROLS OF COLEOPTERAN PESTS

 #5922
20190359984
2019-11-28

Compositions and methods for inhibiting gene expression of factor XII

 #5923
20190359982
2019-11-28

COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

 #5924
20190359981
2019-11-28

Modulators of APOL1 expression

 #5925
20190359980
2019-11-28

OLIGONUCLEOTIDE COMPOSITIONS AND USES THEREOF

 #5926
20190359979
2019-11-28

Oligomeric compounds comprising α-β-constrained nucleic acid

 #5927
20190359978
2019-11-28

Protecting RNAs from degradation using engineered viral RNAs

 #5928
20190359976
2019-11-28

NOVEL ENGINEERED AND CHIMERIC NUCLEASES

 #5929
20190359971
2019-11-28

Type VI CRISPR orthologs and systems

 #5930
20190359718
2019-11-28

Compositions and methods for treating and preventing inflammation

 #5931
20190359556
2019-11-28

Lipids and lipid nanoparticle formulations for delivery of nucleic acids

 #5932
20190358264
2019-11-28

METHODS OF TREATING DISEASES ASSOCIATED WITH ILC2 CELLS

 #5933
20190354055
2019-11-21

Serpina1 siRNAs: compositions of matter and methods of treatment

 #5934
20190353642
2019-11-21

CD2-associated protein (CD2AP) and its interactive proteins

 #5935
20190352722
2019-11-21

Treatment of angiogenesis disorders

 #5936
20190352718
2019-11-21

Exonic splicing enhancers and exonic splicing silencers

 #5937
20190352701
2019-11-21

METHOD FOR EVALUATING THE STATUS OF LATENT TUBERCULOSIS INFECTION, METHOD FOR EVALUATING THE EFFECT OF THE METHOD FOR TREATING THE SAME, AND TREATMENT METHOD THEREOF

 #5938
20190352648
2019-11-21

Methods of altering gene expression by perturbing transcription factor multimers that structure regulatory loops

 #5939
20190352645
2019-11-21

Angiopoietin-like 3 (ANGPTL3) iRNA compositions and methods of use thereof

 #5940
20190352643
2019-11-21

Transgenic mouse expressing amyloid precursor protein that has olfactory neuron degeneration

 #5941
20190352634
2019-11-21

CRISPR RNA

 #5942
20190352604
2019-11-21

NERVE CELL PRODUCTION METHOD

 #5943
20190352316
2019-11-21

Polycationic methyl phospholipids for improved delivery of nucleic acids to eukaryotic cells

 #5944
20190351074
2019-11-21

Gene therapy for haploinsufficiency

 #5945
20190351071
2019-11-21

STRUCTURES AND METHODS FOR GENE THERAPY

 #5946
20190351067
2019-11-21

Multifunctional RNA nanoparticles and methods for treating cancer and therapeutic resistant cancer

 #5947
20190351056
2019-11-21

COMBINATION THERAPY FOR THE TREATMENT OF AUTOIMMUNE DISEASES

 #5948
20190350977
2019-11-21

Coordinating gene expression using RNA destabilizing elements

 #5949
20190350963
2019-11-21

Sterile formulation comprising a stable phosphorothioate oligonucleotide

 #5950
20190350962
2019-11-21

METHODS FOR TREATING OR PREVENTING TTR-ASSOCIATED DISEASES USING TRANSTHYRETIN (TTR) iRNA COMPOSITIONS

 #5951
20190345573
2019-11-14

Methods and Compositions for Selecting siRNA of Improved Functionality

 #5952
20190345518
2019-11-14

NOVEL CRISPR ENZYMES AND SYSTEMS

 #5953
20190345517
2019-11-14

GENOME EDITING KIT

 #5954
20190345498
2019-11-14

Modified iRNA agents

 #5955
20190345497
2019-11-14

Nucleic acid simultaneously inhibiting expression of mTOR gene and STAT3 gene

 #5956
20190345496
2019-11-14

ANTISENSE OLIGONUCLEOTIDES FOR MODULATING RELB EXPRESSION

 #5957
20190345495
2019-11-14

ANTISENSE OLIGONUCLEOTIDES FOR MODULATING NFKB2 EXPRESSION

 #5958
20190345494
2019-11-14

METHODS FOR TREATMENT OF POLYCYSTIC KIDNEY DISEASE

 #5959
20190345493
2019-11-14

Anti-ARID3a treatments for inflammatory disorders

 #5960
20190345492
2019-11-14

Transthyretin (TTR) iRNA compositions and methods of use thereof for treating or preventing TTR-associated diseases

 #5961
20190345479
2019-11-14

Compositions and methods for improved gene editing

 #5962
20190345188
2019-11-14

Bicyclic nucleosides and oligomers prepared therefrom

 #5963
20190343868
2019-11-14

Benzimidazoles that enhance the activity of oligonucleotides

 #5964
20190343865
2019-11-14

Therapeutic targets for facioscapulohumeral muscular dystrophy

 #5965
20190343863
2019-11-14

Modulation of Lnc05 expression

 #5966
20190343767
2019-11-14

Artificial exosome composition and related methods

 #5967
20190338311
2019-11-07

OPTIMIZED STRATEGY FOR EXON SKIPPING MODIFICATIONS USING CRISPR/CAS9 WITH TRIPLE GUIDE SEQUENCES

 #5968
20190338292
2019-11-07

SCN9A antisense pain killer

 #5969
20190338287
2019-11-07

RNAi-MEDIATED INHIBITION OF HIF1A FOR TREATMENT OF OCULAR ANGIOGENESIS

 #5970
20190338283
2019-11-07

METHODS AND COMPOSITIONS FOR TREATING A SUBJECT WITH A SMAD7 ANTISENSE OLIGONUCLEOTIDE

 #5971
20190338282
2019-11-07

Method for modifying amino acid attenuator and use of same in production

 #5972
20190338281
2019-11-07

SELECTIVE ANTISENSE COMPOUNDS AND USES THEREOF

 #5973
20190338280
2019-11-07

IMMUNOMODULATION BY CONTROLLING ELR+ PROINFLAMMATORY CHEMOKINE LEVELS WITH THE LONG NON-CODING RNA UMLILO

 #5974
20190337987
2019-11-07

EXON SKIPPING BY PEPTIDE NUCLEIC ACID DERIVATIVES

 #5975
20190330662
2019-10-31

Methods and compositions for RNA-directed target DNA modification and for RNA-directed modulation of transcription

 #5976
20190330661
2019-10-31

Efficient genetic screening method

 #5977
20190330659
2019-10-31

SCARLESS DNA ASSEMBLY AND GENOME EDITING USING CRISPR/CPF1 AND DNA LIGASE

 #5978
20190330658
2019-10-31

Targeted gene editing platform independent of DNA double strand break and uses thereof

 #5979
20190330647
2019-10-31

Methods and compositions for multiplex RNA guided genome editing and other RNA technologies

 #5980
20190330639
2019-10-31

RNA INTERFERENCE MEDIATED INHIBITION OF CATENIN (CADHERIN-ASSOCIATED PROTEIN), BETA 1 (CTNNB1) GENE EXPRESSION USING SHORT INTERFERING NUCLEIC ACID (SINA)

 #5981
20190330632
2019-10-31

Compositions and methods used in diagnosing and treating colorectal cancer

 #5982
20190330631
2019-10-31

Non-invasive method and kit for capturing and isolating fetal cells from mother

 #5983
20190330630
2019-10-31

Endosomal cleavable linkers

 #5984
20190330629
2019-10-31

Reagents for treatment of oculopharyngeal muscular dystrophy (OPMD) and use thereof

 #5985
20190330628
2019-10-31

Methods for intracellular delivery and enhanced gene targeting

 #5986
20190330627
2019-10-31

Inducer of muscle differentiation

 #5987
20190330626
2019-10-31

COMPOUNDS AND METHODS FOR USE IN DYSTROPHIN TRANSCRIPT

 #5988
20190330625
2019-10-31

Consequences of a defective switch in cutaneous squamous cell carcinoma

 #5989
20190330624
2019-10-31

EXON SKIPPING COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

 #5990
20190330623
2019-10-31

MICRORNAS DIFFERENTIALLY EXPRESSED IN PANCREATIC DISEASES AND USES THEREOF

 #5991
20190330620
2019-10-31

RNA COMPOSITIONS FOR GENOME EDITING

 #5992
20190330604
2019-10-31

Materials and methods for treatment of Amyotrophic Lateral Sclerosis (ALS) and other related disorders

 #5993
20190330591
2019-10-31

AMPLIFIABLE RNAS FOR THERAPEUTIC CELL SYSTEMS

 #5994
20190330280
2019-10-31

Transcriptional regulatory fusion polypeptide

 #5995
20190328905
2019-10-31

Methods for treating Parkinson's disease

 #5996
20190328791
2019-10-31

ENHANCED HETATOPOIETIC STEM CELL TRANSPLANTATION

 #5997
20190328770
2019-10-31

COMPOSITIONS OF SMAD7 ANTISENSE OLIGONUCLEOTIDE AND METHODS OF TREATING OR PREVENTING PSORIASIS

 #5998
20190328763
2019-10-31

A LIPID NANOPARTICLE FOR CARRYING ANTISENSE OLIGONUCLEOTIDES INHIBITING BCL-2 AND METHOD FOR PREPARING THE SAME

 #5999
20190323013
2019-10-24

ANTISENSE OLIGONUCLEOTIDES DIRECTED AGAINST CONNECTIVE TISSUE GROWTH FACTOR AND USES THEREOF

 #6000
20190323011
2019-10-24

Compositions and methods for treating cancer by inhibiting PIWIL4